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Comparison of Pixantrone + Rituximab With Gemcitabine + Rituximab in Patients With Aggressive B-cell Non-Hodgkin Lymphoma or Follicular Grade 3 Lymphoma Who Have Relapsed After Therapy and Are Not Eligible for Stem Cell Transplant

Phase 3
Completed
Conditions
Diffuse Large B-cell Lymphoma
de Novo DLBCL
DLBCL Transformed From Indolent Lymphoma
Follicular Grade 3 Lymphoma
Interventions
Registration Number
NCT01321541
Lead Sponsor
CTI BioPharma
Brief Summary

The purpose of this study is to evaluate the efficacy of Pixantrone + Rituximab compared to Gemcitabine + Rituximab in patients with relapsed or refractory diffuse large B-cell lymphoma (DLBCL), or follicular grade 3 lymphoma.

Detailed Description

Eligible patients will be randomized to treatment with pixantrone plus rituximab or gemcitabine plus rituximab in up to six 28-day cycles. At the time patients experience progressive disease during study treatment, early follow- up, or intermediate follow-up, they enter the survival follow up period. Patients who complete study treatment or discontinue study treatment for any other reason will participate in the follow-up periods.

Early Follow-Up: After treatment completion or discontinuation, patient will enter a 24-week follow-up period.

Intermediate Follow-Up: After completing the 24-week early follow-up period, patient will enter an additional 72-week follow-up period.

Survival Follow-Up: All patients will be monitored for survival.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
312
Inclusion Criteria
  1. Diagnosis of DLBCL (de novo DLBCL, or transformed from indolent lymphoma) or follicular grade 3 lymphoma on the basis of tissue biopsy.
  2. Patients with de novo DLBCL must have received 1-3 treatment regimens for DLBCL. Patients with follicular grade 3 lymphoma must have received 1-3 treatment regimens for follicular lymphoma (any grade). Patients with DLBCL transformed from indolent lymphoma must have received at least 1-4 treatment regimens for NHL.
  3. Received rituximab containing a multi-agent therapy for the treatment of NHL.
  4. Not eligible for high-dose chemotherapy and stem cell transplant.
  5. Patients with DLBCL transformed from indolent lymphoma must have had a complete or partial response to a therapy for NHL lasting at least 12 weeks.
Exclusion Criteria
  1. Primary refractory de novo DLBCL or primary refractory follicular grade 3 lymphoma, defined as documented progression within 12 weeks of the last cycle of the first-line multi-agent regimen.
  2. Prior treatment with cumulative dose of doxorubicin or equivalent exceeding 450 mg/m2
  3. Any experimental therapy ≤ 28 days prior to randomization
  4. Other malignancy within last 5 years except for the following: curatively treated basal cell/squamous cell skin cancer, carcinoma in situ of the cervix, superficial transitional cell bladder carcinoma, or in situ ductal carcinoma of the breast after complete resection
  5. Any contraindication or known allergy or hypersensitivity to any study drugs
  6. Concomitant therapy with any anticancer agents, immunosuppressive agents, other investigational anticancer therapies. Low-dose corticosteroids for the treatment of non cancer-related illnesses are permitted.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Gemcitabine + RituximabGemcitabine + RituximabGemcitabine and Rituximab
Pixantrone + RituximabPixantrone + RituximabPixantrone and Rituximab
Primary Outcome Measures
NameTimeMethod
Progression Free Survival (PFS)From the date of randomization to the date of progressive disease or death due to any cause (whichever is first reported) (Up to 100 weeks)

PFS is defined as the time of randomization to the date of disease progression or death due to any cause (whichever occurs first)

Secondary Outcome Measures
NameTimeMethod
Overall Response RateFrom date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

ORR is defined as the proportion of patients who achieve a CR or PR without additional therapy.

Overall SurvivalFrom date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

Overall survival is from randomization to death due to any cause

Number of Treatment Emergent Adverse Events (TEAE) Related to Study DrugFrom date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

The number of Participants with Treatment Emergent Adverse Events (TEAE) related to study drug (pixantrone or gemcitabine)

Complete Response RateFrom date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

CRR is defined as the proportion of patients who achieve a Complete Response (CR) without additional therapy. CR is defined as the disappearance of all target lesions.

Trial Locations

Locations (119)

Cancer Care Centers of South Texas-HOAST

🇺🇸

San Antonio, Texas, United States

Hospital Elisabethinen Linz, Internal Department 1 - Hemato-Oncology

🇦🇹

Linz, Austria

National Cancer Institute, Department of Hematology and Transfusiology

🇸🇰

Bratislava, Slovakia

Hanusch Hospital, Department of Internal Medicine III

🇦🇹

Vienna, Austria

State Budget Healthcare Institution of Sverdlovsk region: Sverdlovsk Regional Clinical Hospital #1

🇷🇺

Ekaterinburg, Russian Federation

Moscow State Budget Medical Institution: City Clinical Hospital n.a. S.P.Botkin

🇷🇺

Moscow, Russian Federation

Marine Hospital of Polish Red Cross, Department of Chemotheraphy

🇵🇱

Gdynia, Poland

Saint Luc University Hospital, Department of Hematology

🇧🇪

Brussels, Belgium

UMHAT "Sveti Georgi", Plovdiv, Department of Medical Oncology

🇧🇬

Plovdiv, Bulgaria

Rocky Mountain Cancer Centers

🇺🇸

Denver, Colorado, United States

Arizona Clinical Research Center

🇺🇸

Tucson, Arizona, United States

Integrated Community Oncology Network

🇺🇸

Orange Park, Florida, United States

Crossroads Cancer Center

🇺🇸

Effingham, Illinois, United States

Harry and Jeanette Weinberg Cancer Institute at Franklin Square

🇺🇸

Baltimore, Maryland, United States

Cancer Center of Kansas

🇺🇸

Wichita, Kansas, United States

Carle Foundation Physician Services

🇺🇸

Mattoon, Illinois, United States

Center for Cancer and Blood Disorders, PC

🇺🇸

Bethesda, Maryland, United States

Metro Minnesota Community Clinical Oncology Program

🇺🇸

Saint Louis Park, Minnesota, United States

Metro Minnesota CCOP-St. Johns

🇺🇸

Maplewood, Minnesota, United States

Hematology-Oncology Associates of Northern New Jersey

🇺🇸

Morristown, New Jersey, United States

Northwest Cancer Specialists, PC

🇺🇸

Vancouver, Washington, United States

Fox Chase Cancer Center

🇺🇸

Philadelphia, Pennsylvania, United States

Joe Arrington Cancer Research and Treatment Center

🇺🇸

Lubbock, Texas, United States

University Hospital Hradec Kralove, 4th Department of Internal Medicne, Clinical Hematology

🇨🇿

Hradec Kralove, Czechia

Aalborg University Hospital, Department of Hematology

🇩🇰

Aalborg, Denmark

University Hospital Kralovske Vinohrady, Department of Clinical Hematology

🇨🇿

Prague, Czechia

Polyclinique de Bordeaux nord Acquitaine

🇫🇷

Bordeaux, France

Centre hospitalier du Mans

🇫🇷

Le Mans Cedex 03, France

Hospital Universitario Vall Hebrón

🇪🇸

Barcelona, Spain

Klinik für Innere Medizin III

🇩🇪

Frankfurt (a.M.), Germany

St. Marien Hospital Hamm

🇩🇪

Hamm, Germany

Siena University Hospital Authority Santa Maria alle Scotte Polyclinic

🇮🇹

Siena, Italy

Romagna Local Health Authority (AUSL Romagna) - "Infermi" Hospital

🇮🇹

Rimini, Italy

Santa Maria Hospital

🇮🇹

Terni, Italy

A.O.U. Città della Salute e della Scienza di Torino

🇮🇹

Torino, Italy

Oncology Center of Lublin Land, Department of Clinical Oncology

🇵🇱

Lublin, Poland

Hospital Iniversitario Puerta del Mar

🇪🇸

Cadiz, Spain

Arizona Oncology Associates

🇺🇸

Tucson, Arizona, United States

Highlands Oncology Group

🇺🇸

Fayetteville, Arkansas, United States

Integrated Community Oncology Network-Southside

🇺🇸

Jacksonville, Florida, United States

Carle Physician Group

🇺🇸

Danville, Illinois, United States

Integrated Community Oncology Network-St. Vincent's

🇺🇸

Jacksonville, Florida, United States

Cancer Care Specialists of Central Illinois

🇺🇸

Decatur, Illinois, United States

Carle Cancer Center

🇺🇸

Urbana, Illinois, United States

Baptist Hospital East

🇺🇸

Louisville, Kentucky, United States

Cancer & Hematology Center of Western Michigan

🇺🇸

Grand Rapids, Michigan, United States

Metro Minnesota CCOP-Unity Hospital

🇺🇸

Fridley, Minnesota, United States

Missouri Cancer Associates

🇺🇸

Columbia, Missouri, United States

Metro Minnesota CCOP-Regions Hospital

🇺🇸

Saint Paul, Minnesota, United States

North Shore Hematology/Oncology Associates

🇺🇸

East Setauket, New York, United States

Gabrail Cancer Center

🇺🇸

Dover, Ohio, United States

Mercy Cancer Center at St. Anne's

🇺🇸

Toledo, Ohio, United States

Toledo Clinic Cancer Center-Toledo

🇺🇸

Toledo, Ohio, United States

Upstate Oncology Associates

🇺🇸

Greenville, South Carolina, United States

South Carolina Cancer Specialists

🇺🇸

Hilton Head Island, South Carolina, United States

Blue Ridge Cancer Care

🇺🇸

Roanoke, Virginia, United States

Green Bay Oncology-St. Mary's Hospital MC

🇺🇸

Green Bay, Wisconsin, United States

Saint Vincent Hospital Green Bay Oncology

🇺🇸

Green Bay, Wisconsin, United States

Medical University Innsbruck, Department of Internal Medicine V (Hematology and Oncology)

🇦🇹

Innsbruck, Austria

General Hospital Delta, Hematology Department

🇧🇪

Roeselare, Belgium

General Hospital Turnhout, Hematology Department

🇧🇪

Turnhout, Belgium

UMHAT "Sveti Georgi", Plovdiv, Clinical Hematology Clinic

🇧🇬

Plovdiv, Bulgaria

MHAT "Tokuda Hospital Sofia", Hematology Clinic

🇧🇬

Sofia, Bulgaria

University Multiprofile Hospital for Active Treatment "Sveti Ivan Rilski", Department of Clinical Hematology

🇧🇬

Sofia, Bulgaria

Specialized Hospital For Active Treatment Of Hematological Diseases, Sofia, Clinical Hematology Clinic

🇧🇬

Sofia, Bulgaria

MHAT Hristo Botev, Vratsa, First Department of Internal Medicine

🇧🇬

Vratsa, Bulgaria

University Hospital Brno, Clinic of Internal Medicine - Hematology and Oncology

🇨🇿

Brno, Czechia

General University Hospital in Prague, 1st Department of Internal Medicine - Department of Hematology

🇨🇿

Prague, Czechia

Service d'hématologie clinique, Avenue Laennec Salouel

🇫🇷

Amiens, Cedex 1, France

Centre hospitalier Lyon Sud

🇫🇷

Pierre Benite Cedex, France

Centre hopitalier de la cote basque

🇫🇷

Bayonne, France

Centre hospitalier de Beziers

🇫🇷

Beziers, France

Saint Quentin Hospital Center, Department of Oncology-Hematology

🇫🇷

Saint-Quentin, France

Hautepierre Hospital, Department of Hematology and Oncology

🇫🇷

Strasbourg Cedex, France

Gemeinschaftspraxis Drs. Klausmann

🇩🇪

Aschaffenburg, Germany

Klinikum Chemnitz gGmbH

🇩🇪

Chemnitz, Germany

Universitaetsklinikum Halle

🇩🇪

Halle (Saale), Germany

Klinikum Nürnberg Nord

🇩🇪

Nürnberg, Germany

Universitätsklinik Köln

🇩🇪

Köln, Germany

Klinikum Mutterhaus der Borromäerinnen

🇩🇪

Trier, Germany

St. Istvan and St. Laszlo Hospital of Budapest

🇭🇺

Budapest, Hungary

University of Debrecen

🇭🇺

Debrecen, Hungary

Bologna University Hospital Authority St. Orsola-Malpighi Polyclinic

🇮🇹

Bologna, Italy

Moritz Kaposi General Hospital

🇭🇺

Kaposvár, Hungary

Scientific Institute of Romagna for the Study and Treatment of Cancer (I.R.S.T.) S.R.L.

🇮🇹

Meldola, Italy

University Hospital "Ospedali Riuniti Umberto I - G.M. Lancisi - G. Salesi"

🇮🇹

Ancona, Italy

Romagna Local Health Authority (AUSL Romagna) - "Santa Maria delle Croci"

🇮🇹

Ravenna, Italy

"Ospedali Riuniti Villa Sofia-Cervello" Hospital

🇮🇹

Palermo, Italy

Independent Public Healthcare Facility Municipal Hospital Group

🇵🇱

Chorzów, Poland

Silesia Medical University, Department of Hematology and Bone Marrow Transplantation

🇵🇱

Katowice, Poland

Malopolskie Medical Center S.C. , Department of Hematology

🇵🇱

Krakow, Poland

Institute of Hematology and Transfusion Medicine, Clinic of Hematology

🇵🇱

Warsaw, Poland

Nicolaus Copernicus Memorial Provincial Specialist Hospital in Lodz

🇵🇱

Lodz, Poland

Rapid Diagnosis Polyclinic SA

🇷🇴

Brasov, Romania

Bucharest University Emergency Hospital, Hematology Clinic

🇷🇴

Bucharest, Romania

Wroclaw Medical University, Department and Clinic of Hematology, Blood Neoplasms and Bone Marrow Transplantation

🇵🇱

Wroclaw, Poland

Fundeni Clinical Institute Center for Hematology and Bone Marrow Transplantation

🇷🇴

Bucharest, Romania

Federal State Public Institution: Main Military Clinical Hospital n.a. N.N. Burdenko of the Russian Ministry of Defense

🇷🇺

Moscow, Russian Federation

State Medical Institution: Republican Hospital named after V.A. Baranov

🇷🇺

Petrozavodsk, Russian Federation

State Healthcare Institution: Republican Clinical Oncology Center

🇷🇺

Ufa, Russian Federation

St. Petersburg Clinical Research and Practical Center for Specialized Types of Medical Care

🇷🇺

St. Petersburg, Russian Federation

University Hospital with Outpatient Clinic F.D. Roosevelt Banska Bystrica, Department of Hematology

🇸🇰

Banska Bystrica, Slovakia

University Hospital Martin, Department of Hematology and Transfusiology

🇸🇰

Martin, Slovakia

A Coruña University Hospital

🇪🇸

A Coruña, Spain

J. A. Reiman University Hospital with Polyclinic in Presov

🇸🇰

Presov, Slovakia

Institut Català de Oncologia (ICO), Hospital Dr Trueta

🇪🇸

Girona, Spain

Hospital Universitario Araba

🇪🇸

Vitoria, Spain

National Institute of Cancer

🇺🇦

Kyiv, Ukraine

Kharkiv Regional Clinical Oncology Center

🇺🇦

Kharkiv, Ukraine

Cherkasy Regional Oncology Center, Regional Treatment and Diagnostic Hematology Center

🇺🇦

Cherkasy, Ukraine

Beatson West of Scotland Cancer Center

🇬🇧

Glasgow, United Kingdom

St. George's Healthcare NHS Trust

🇬🇧

London, United Kingdom

State Institution: Institute of Blood Pathology and Transfusion Medicine

🇺🇦

Lviv, Ukraine

Christie Hospital, Department of Medical Oncology

🇬🇧

Manchester, United Kingdom

Nebraska Hematology-Oncology, PC

🇺🇸

Lincoln, Nebraska, United States

University Hospital Ostrava, Institute of Clinical Hematology

🇨🇿

Ostrava, Czechia

George Washington University Department of Medicine

🇺🇸

Washington, District of Columbia, United States

Toledo Clinical Cancer Center

🇺🇸

Toledo, Ohio, United States

Hospital Iniversitario La Paz

🇪🇸

Madrid, Spain

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