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NICU Antibiotics and Outcomes (NANO) Follow-up Study

Phase 3
Not yet recruiting
Conditions
Antibiotics
Neurodevelopment
Premature Birth
Interventions
Registration Number
NCT05977400
Lead Sponsor
Sharp HealthCare
Brief Summary

The NANO follow-up study is designed to determine whether a simple, cost-effective intervention- withholding antibiotics at birth- reduces clinically relevant outcomes such as behavioral and neurological impairment at 2 years of age. This study will be the largest study evaluating the effects of early antibiotics in children with comprehensive measures of neurodevelopment linked to genomic variants and microbiota interactions.

Detailed Description

The multidisciplinary team launched the NANO (NICU Antibiotics and Outcomes) Trial to study the longstanding clinical practice of empirically administering intravenous antibiotics to very preterm infants. The NANO trial is an 802-patient,13-site randomized blinded controlled trial (R01HD09757801) discerning whether administration of antibiotics within the first three days of life increases the incidence of short-term, life-threatening complications among very preterm infants.

The proposed NANO follow-up study will build upon the parent NANO trial to determine whether avoiding antibiotics in very preterm infants - a simple, cost-effective intervention - improves neurodevelopmental and behavioral outcomes during the toddler years. Evaluation of children enrolled in the proposed NANO follow-up study will include serial comprehensive, standardized assessments of motor, cognitive, behavioral and adaptive outcomes. To support retention and provide an important early assessment, a first virtual visit at 1 year of age will include the Hammersmith Infant Neurologic Exam (HINE) and the Developmental Assessment of Young Children, Second Edition (DAYC-2). A second comprehensive follow-up visit in person at 2 years will include the Bayley Scales of Infant Development 4th ed., Gross Motor Function Classification System, Child Behavior Checklist for ages 1.5-5, and the Modified Checklist for Autism in Toddlers, Revised, with Follow-up.

In the NANO follow-up trial, outcomes will be assessed using the Desirability of outcome ranking (DOOR), an innovative, patient-centered statistical approach used in clinical trials to evaluate the global benefits and risks of an intervention. The ordinal neonatal follow-up endpoint composite scale, to be named neoDOOR, will be developed by both clinicians and families. Stakeholder meetings will develop consensus rankings of individual and composite outcomes of different severities reported by the above developmental assessments. Neonatal biospecimens collected during the parent NANO trial will allow for additional exploratory analyses evaluating interactions among genetics, environment, and microbiota with antibiotic exposure and long-term outcomes. Through these assessments and evaluation, the investigators will provide substantial evidence for the use (or non-use) of early antibiotics for very preterm infants at birth.

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
802
Inclusion Criteria

Families that have agreed to participate and are enrolled in the parent NANO trial will be eligible for the NANO follow-up study. There will be no exclusions for eligible children entering the follow-up study.

Parent NANO trial Criteria:

I. Inclusion criteria: We will enroll newborn infants with gestational age of 23.0-30.6 weeks born to mothers 18 years or older at participating study sites. Only inborn infants at participating study sites will be eligible.

II. Exclusion criteria:

  1. Infants at low risk for early onset sepsis-Infants born for maternal indications via caesarean section with rupture of membranes within 6 hours, without attempts to induce labor, and without concern for maternal infection
  2. Infants at high risk for early onset sepsis- Infants born to mothers with intrapartum fever (> 38ºC) or clinical diagnosis of chorioamnionitis (suspected or definite), infants born to mothers with proven Group B Streptococcus colonization or indication for intrapartum antibiotic prophylaxis that did not receive adequate antibiotic treatment according to specialty specific guidelines, (i.e., penicillin, ampicillin, cefazolin), infant born to mother with previous infant with GBS disease/infection
  3. Infants with respiratory insufficiency requiring invasive mechanical ventilation and fraction of inspired oxygen> 0.40 or non-invasive ventilation and fraction of inspired oxygen > 0.60 at time of randomization
  4. Infants with ongoing hemodynamic instability requiring vasopressors or more than one fluid bolus at time of randomization
  5. Clinician concern for sepsis due to physical exam findings or clinical history of mother or infant
  6. Major congenital anomalies
  7. Infants not anticipated to survive beyond 72 hours
  8. Infants who have received antibiotics prior to randomization.
Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Very preterm infants that do not receive empiric antibiotic treatment in the first 48 hours of lifePlaceboNeonates in this group will have been enrolled and randomized into the NANO trial and received a blinded 48 hour course of placebo.
Very preterm infants that receive empiric antibiotic treatment in the first 48 hours of lifeGentamicinNeonates in this group will have been enrolled and randomized into the NANO trial and received a blinded 48 hour course of empiric antibiotic treatment.
Very preterm infants that receive empiric antibiotic treatment in the first 48 hours of lifeAmpicillinNeonates in this group will have been enrolled and randomized into the NANO trial and received a blinded 48 hour course of empiric antibiotic treatment.
Primary Outcome Measures
NameTimeMethod
Rate of neurodevelopmental impairment or Death24 months corrected gestational age

The first primary outcome will be a composite of newborn or childhood death OR one of following: cognitive or motor composite scores \<80 on the Bayley-4, Gross Motor Function Classification Score score ≥2, bilateral blindness, severe functional hearing impairment. The incidence of the composite outcome will be compared between the placebo and early antibiotic groups.

DOOR probability Distribution24 months corrected gestational age

The second primary outcome will be a comparison of the DOOR probability of more desirable outcomes at 2 years using a novel ordinal endpoint scale developed during the trial. Outcomes to be included in the rank are as follows: death, cognitive/language/motor composite scores\<80 on the Bayley-4, Gross Motor Function Classification Score ≥2, bilateral blindness, severe functional hearing impairment, Child Behavior Checklist (CBCL) scores \>70, autism risk scores (MCHAT R/F) of ≥2, and medical measures, such as need for oxygen support. The distribution of the finalized neoDOOR will be compared between the placebo and empiric antibiotic groups.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (15)

Westchester Medical Center

🇺🇸

Valhalla, New York, United States

Magee-Womens Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Sinai Health System

🇨🇦

Toronto, Canada

Columbia University

🇺🇸

New York, New York, United States

Jefferson Medical College of Thomas Jefferson University

🇺🇸

Philadelphia, Pennsylvania, United States

Sharp Mary Birch Hospital for Women & Newborns

🇺🇸

San Diego, California, United States

State University of New York Downstate

🇺🇸

Brooklyn, New York, United States

University of Rochester

🇺🇸

Rochester, New York, United States

The Pennsylvania State University

🇺🇸

Hershey, Pennsylvania, United States

The Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

The University of Pittsburgh Medical Center

🇺🇸

Pittsburgh, Pennsylvania, United States

University of Texas Health Science Center at San Antonio

🇺🇸

San Antonio, Texas, United States

University of South Florida

🇺🇸

Tampa, Florida, United States

University of Louisville

🇺🇸

Louisville, Kentucky, United States

Yale University

🇺🇸

New Haven, Connecticut, United States

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