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Assessing Withdrawal of Disease-Modifying Antirheumatic Drugs in Rheumatoid Arthritis

Phase 4
Completed
Conditions
Rheumatoid Arthritis
Interventions
Drug: Synthetic DMARD(s)
Registration Number
NCT01881308
Lead Sponsor
Diakonhjemmet Hospital
Brief Summary

The purpose of this study is to assess the effect of disease-modifying anti-rheumatic drugs (DMARDs) dose reduction in patients with rheumatoid arthritis (RA).

Remission is the treatment target in RA, but knowledge about the best way to treat RA patients who achieve sustained remission is limited. DMARDs have potential serious adverse events, and biologic DMARDs are costly to the society. The objectives for ARCTIC REWIND are to assess the effect of tapering and withdrawal of DMARDs on disease activity in RA patients in sustained remission, to study predictors for successful tapering and withdrawal of DMARDs in this patient group, and to study cost-effectiveness of different treatment options in RA remission.

ARCTIC REWIND is a randomized, open, controlled, parallel-group, multicenter, phase IV, non-inferiority strategy study. Patients with less than five years of disease duration and stable remission for at least 12 months are randomized to either continued stable treatment or tapering and withdrawal of DMARDs, including tumor necrosis factor (TNF) inhibitors and synthetic DMARDs. Patients are assessed by clinical examination, patient reported outcome measures, ultrasonography, MRI and X-ray, and monitored for adverse events. The primary endpoint of the study is the proportion of patients who are non-failures (have not experienced a flare) at 12 months. Secondary endpoints include composite disease activity scores and remission criteria, joint damage and inflammation assessed by various imaging modalities, work participation, health care resource use and health related quality of life.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
320
Inclusion Criteria
  • Rheumatoid arthritis according to the 2010 American College of Rheumatology (ACR)/European League Against Rheumatism (EULAR) classification criteria
  • Male or non-pregnant, non-nursing female
  • >18 years of age and <80 years of age
  • Patient in the TNF-inhibitor group: Any disease duration. Patient in the synthetic DMARD group: RA diagnosis after 01.01.2010.
  • Sustained remission for ≥12 months according to DAS or Disease Activity Score based on 28 joints (DAS28), with documented remission status at a minimum of 2 consecutive visits during the last 18 months OR participation in the first ARCTIC trial
  • DAS <1.6 and no swollen joints at inclusion OR participation in the first ARCTIC trial
  • Unchanged treatment with TNF inhibitors and/or synthetic DMARDs during the previous 12 months, with a stable or reduced dose of glucocorticosteroids OR participation in the first ARCTIC trial
  • Subject capable of understanding and signing an informed consent form
  • Provision of written informed consent
Exclusion Criteria
  • Abnormal renal function, defined as serum creatinine >142 μmol/L in female and >168 μmol/L in male, or a glomerular filtration rate (GFR) <40 mL/min/1.73 m2
  • Abnormal liver function (defined as aspartate transaminase (ASAT)/alanine aminotransferase (ALAT) >3x upper normal limit), active or recent hepatitis, cirrhosis
  • Major co-morbidities, such as severe malignancies, severe diabetic mellitus, severe infections, uncontrollable hypertension, severe cardiovascular disease (NYHA class 3 or 4) and/or severe respiratory diseases
  • Leukopenia and/or thrombocytopenia
  • Inadequate birth control, pregnancy, and/or breastfeeding
  • Indications of active tuberculosis
  • Psychiatric or mental disorders, alcohol abuse or other substance abuse, language barriers or other factors which makes adherence to the study protocol impossible.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Stable dose synthetic DMARDSynthetic DMARD(s)Stable dose of synthetic DMARDs, either monotherapy or combination therapy.
Synthetic DMARD dose reductionSynthetic DMARD(s)Half-dose synthetic DMARDs (monotherapy or combination therapy) for the first 12 months of the study. Patients classified as non-failures are re-randomized at 12 months to either continue half-dose synthetic DMARD(s) or withdraw all DMARD(s).
ARCTIC follow-upTNF inhibitorsPatients are treated according to the ARCTIC treatment schedule based on disease activity.
ARCTIC follow-upSynthetic DMARD(s)Patients are treated according to the ARCTIC treatment schedule based on disease activity.
Stable dose TNF inhibitorTNF inhibitorsStable dose TNF inhibitor. Any co-medication with synthetic DMARDs kept stable.
Stepdown and withdrawal of TNF inhibitorTNF inhibitorsHalf-dose of TNF inhibitor for the first four months, thereafter withdrawal of TNF inhibitor. Any co-medication with synthetic DMARDs kept stable.
Primary Outcome Measures
NameTimeMethod
Proportion of patients who are non-failures (have not experienced a flare)12 months

Flare is defined as composite measure: (1) An increase in disease activity score (DAS) to \>1.6 AND (2) a change in DAS of at least 0.6 AND (3) \> 1 swollen joint. If a patient does not fulfill this formal definition, but experiences a clinically significant flare according to the investigator and patient, this is treated as a flare.

Secondary Outcome Measures
NameTimeMethod
Disease Activity Score in 28 joints (DAS28)12 months, with subsequent long-term analyses after 24 months and 36 months

The 28-joint Disease Activity Score (DAS28) includes the 28- tender joint counts (TJC28), 28-swollen joint counts (SJC28), Erythrocyte Sedimentation Rate (ESR) and Patient Global Assessment (PGA) on a VAS.

Disease Activity Score (DAS)12 months, with subsequent long-term analyses after 24 months and 36 months

The DAS is a composite score that includes the Ritchie articular index (RAI), the 44- swollen joint counts (SJC-44), the Erythrocyte Sedimentation Rate (ESR) and a general health (GH) assessment on a Visual Analogue Scale (VAS).

The DAS is calculated as follows:

DAS = 0.54\*sqrt(RAI) + 0.065\*(SJC-44) + 0.33\*Ln(ESR) + 0.0072\*GH

EuroQol-5 Dimension (EQ-5D)12 months, with subsequent long-term analyses after 24 months and 36 months

EQ-5D is a standardised instrument for use as a measure of health outcome.

DAS-remission12 months, with subsequent long-term analyses after 24 months and 36 months

Remission is defined as a DAS-score \<1.6

C-reactive protein (CRP)12 months, with subsequent long-term analyses after 24 months and 36 months

Assessment of CRP in mg/L

Patient's assessment of disease activity (PGA)12 months, with subsequent long-term analyses after 24 months and 36 months

PGA is the patient's assessment of disease activity on a VAS 0-100 mm.

Health Assessment Questionnaire (HAQ-PROMIS)12 months, with subsequent long-term analyses after 24 months and 36 months

The HAQ-PROMIS is a questionnaire evaluating the physical function in patients with RA.

Simplified Disease Activity Index (SDAI)12 months, with subsequent long-term analyses after 24 months and 36 months

SDAI includes TCJ28, SJC28, PGA, physician's global assessment of disease activity on a VAS 0-100 mm (PhGA) and C-reactive protein (CRP).

Physician's global assessment of disease avtivity (PHGA)12 months, with subsequent long-term analyses after 24 months and 36 months

PHGA is the investigator's assessment of disease activity on a VAS 0-100 mm.

Medical Outcomes Study Short-Form 36-item (SF-36) Physical and Mental Component Summary Score12 months, with subsequent long-term analyses after 24 months and 36 months

The SF-36 is a multi-purpose, short-form health survey with only 36 questions. It yields an 8-scale profile of functional health and well-being scores as well as psychometrically-based physical and mental health summary measures and a preference-based health utility index.

Work performance12 months, with subsequent long-term analyses after 24 months and 36 months

1. Absenteeism (work time missed)

2. Presenteeism (impairment at work / reduced on-the-job effectiveness)

3. Work productivity loss (overall work impairment / absenteeism plus presenteeism)

4. Activity Impairment

SDAI-remission12 months, with subsequent long-term analyses after 24 months and 36 months

Remission is defined as a SDAI score ≤ 3.3

Clinical Disease Activity Index (CDAI)12 months, with subsequent long-term analyses after 24 months and 36 months

CDAI includes TCJ28, SJC28, PGA and PhGA.

Swollen joint count12 months, with subsequent long-term analyses after 24 months and 36 months

Swollen joint counts are performed on 44 joints, with total joint count ranging from 0 to 44.

CDAI-remission12 months, with subsequent long-term analyses after 24 months and 36 months

Remission is defined as a CDAI score ≤ 2.8

Erythrocyte Sedimentation Rate (ESR)12 months, with subsequent long-term analyses after 24 months and 36 months

Assessment of ESR in mm/h

Tender joint count12 months, with subsequent long-term analyses after 24 months and 36 months

Tender joints is assessed by Ritchie Articular Index which assesses tenderness of 26 joint regions, based on summation of joint responses after applying firm digital pressure. The index ranges from 0 to 3 for individual measures and the sum 0 to 78 overall.

Radiographic joint damage12 months, with subsequent long-term analyses after 24 months and 36 months

Radiographs of hands (posterior/anterior) and foot (anterior/posterior) will be taken at baseline, 12, 24 and 36 months. The modified Sharp van der Heijde Score (vdHSS) will be calculated, including an erosion score and a joint space narrowing score.

Ultrasonography (subclinical synovitis)12 months, with subsequent long-term analyses after 24 months and 36 months

36 joints and 2 tendons will be scored for both grey scale and power doppler synovitis on a 0-3 scale.

DAS28-remission12 months, with subsequent long-term analyses after 24 months and 36 months

Remission is defined as a DAS28 score \< 2.6

ACR/EULAR Boolean remission12 months, with subsequent long-term analyses after 24 months and 36 months

The patient must satisfy all of the following in order to achieve ACR/EULAR remission:

* RAI ≤ 1

* SJC44 ≤ 1

* CRP ≤ 1

* PGA ≤ 1 (on a scale 0-10, in this study ≤ 14 on a scale 0-100)

No swollen joint12 months, with subsequent long-term analyses after 24 months and 36 months

The percentage of patients with no swollen joints will be assessed

Radiographic outcome12 months, with subsequent long-term analyses after 24 months and 36 months

No radiographic progression

Ultrasound outcome12 months, with subsequent long-term analyses after 24 months and 36 months

No ultrasound power Doppler signal in any joint.

American College of Rheumatology (ACR) response12 months, with subsequent long-term analyses after 24 months and 36 months

If a patient has experienced a flare, and treatment has been escalated, the ACR 2050/70/90 response will be calculated.

The European League Against Rheumatism (EULAR) response12 months, with subsequent long-term analyses after 24 months and 36 months

If a patient has experienced a flare, and treatment has been escalated, the EULAR response will be calculated.

The Food and Drug Administration (FDA) major clinical response12 months, with subsequent long-term analyses after 24 months and 36 months

If a patient has experienced a flare, and treatment has been escalated, the FDA major clinical response will be calculated.

Medication12 months, with subsequent long-term analyses after 24 months and 36 months

The number of patients on different conventional synthetic disease-modifying antirheumatic drugs (csDMARDs) and biologic therapy. Dose of DMARDs in users will be recorded, prednisolone usages and number of intraarticular injections.

Trial Locations

Locations (10)

Department of Rheumatology, Helse Møre og Romsdal HF

🇳🇴

Ålesund, Norway

Department of Rheumatology, Sykehuset Østfold HF

🇳🇴

Fredrikstad, Norway

Martina Hansens Hospital AS

🇳🇴

Sandvika, Norway

Universitetssykehuset Nord-Norge HF

🇳🇴

Tromsø, Norway

Helgelandssykehuset, Mo i Rana

🇳🇴

Mo i Rana, Norway

Department of Rheumatology, Haukeland University Hospital, Helse Bergen HF

🇳🇴

Bergen, Norway

Revmatismesykehuset AS

🇳🇴

Lillehammer, Norway

Department of Rheumatology, Drammen Hospital, Vestre Viken HF

🇳🇴

Drammen, Norway

Department of Rheumatology, Sørlandet Sykehus HF

🇳🇴

Kristiansand, Norway

Department of Rheumatology, Diakonhjemmet Hospital

🇳🇴

Oslo, Norway

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