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Trial of EP0057, a Nanoparticle Camptothecin With Olaparib in People With Relapsed/Refractory Small Cell Lung Cancer

Phase 1
Active, not recruiting
Conditions
Small Cell Lung Cancer
Prostate Cancer
Lung Neoplasms
Urothelial Carcinoma
Urothelial Cancer
Interventions
Registration Number
NCT02769962
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

Background: EP0057 consists of a sugar molecule cyclodextrin linked to a chemotherapy drug called camptothecin. The combined molecule or "nanoparticle drug conjugate" travels through the blood. Once inside cancer cells, the chemotherapy drug is released from the molecule. Olaparib is a drug that may stop cancer cells from repairing the DNA damage caused by chemotherapy. Researchers want to see how safe it is to give EP0057 and olaparib together and to see how well the combination treats a specific type of lung cancer called small cell lung cancer (SCLC).

Objectives:

To test the safety and maximum dose of EP0057 and olaparib together. To test how well they treat small cell lung cancer.

Eligibility:

Adults 18 and older with small cell lung cancer.

Design:

Participants will be screened with standard cancer care tests.

Participants will get the 2 study drugs in 28-day cycles. EP0057 will be given every 2 weeks, through a small plastic tube in an arm vein. Olaparib will be taken by mouth twice a day most days. Participants will keep a pill diary.

For Cycle 1, participants will have 3 visits. All other cycles will have 2 visits.

At study visits, participants may have:

* Blood and hair samples taken

* History and Physical exam

* Questions about health and side effects

* Pregnancy test

* Optional tumor biopsy where a piece of tumor is removed by needle after numbing the skin.

* CT scan

* Injection of EP0057 (twice per cycle)

* Olaparib prescription \<TAB\>

Participants will have a follow-up visit 4 weeks after finish taking the drugs. They will have a physical exam and blood tests. They may have a tumor biopsy. The study team will call the patient every 3 months for follow up after completing the study treatment.

Detailed Description

Background:

* Small cell lung cancer (SCLC) is an aggressive cancer with a poor prognosis.

* Although highly responsive to chemotherapy initially, SCLC relapses quickly and becomes refractory to treatment within a few months.

* Urothelial Carcinoma (UC) of the Bladder is the fourth most common malignancy in men and the ninth most common in women.

* Prostate cancer is the most common cancer among men in the United States. While prostate cancer is initially responsive to androgen deprivation therapy (ADT), the median duration of sensitivity is 24-36 months. Moreover, patients develop resistance to current treatment options.

* The use of PARP inhibitors in combination with chemotherapy builds upon pre-clinical data in lung cancer and other cancers supporting the notion that PARP inhibitors potentiate the effect of DNA damaging therapies.

* Despite their highly synergistic activity in preclinical models, human studies combining PARP inhibitors and camptothecins have not translated into clinical benefit due to enhanced toxicity with the combination.

* One approach to improve ability to combine camptothecins with agents that sensitize their activity like PARP inhibitors is to use alternative formulations that minimize toxicity to the normal tissues.

* EP0057 is a nanoparticle drug conjugate composed of 20 (S)-camptothecin (a potent and highly selective topoisomerase I inhibitor) conjugated to a linear, cyclodextrinpolyethylene glycol-based polymer.

* Olaparib is a PARP inhibitor indicated as monotherapy in patients with deleterious or suspected deleterious germline BRCA mutated advanced ovarian cancer who have been treated with three or more prior lines of chemotherapy. Olaparib has an established safety profile and it is under investigation in a number of different cancers.

Objectives:

* Phase I: To determine the MTD/recommended Phase 2 dose (RP2D) of EP0057 in combination with olaparib in patients with refractory cancers.

* Phase II: To determine the antitumor activity of olaparib plus EP0057 with respect to progression free survival at 16 weeks in SCLC patients with resistant or sensitive relapse.

* Expansion Cohorts: To determine overall response rate of EP0057 plus olaparib in patients with mCRPC and urothelial carcinoma.

Eligibility:

Phase I

* Adult patients \>=18 years of age

* Histologically or cytologically confirmed, advanced solid tumor that is refractory to standard therapy and/or for whom no further standard therapy is available

* ECOG Performance Status of 0, 1 or 2

Phase II

* Adult patients \>= 18 years old

* Have a pathologically (histology or cytology) confirmed diagnosis of SCLC

* Disease progression on or after at least one platinum-based standard chemotherapy regimen and/or an immune-checkpoint inhibitor for either limited or extensive stage disease.

* Have measurable disease per RECIST 1.1

* ECOG performance status of 0, 1 or 2

Phase II Expansion Cohorts

* Have a pathologically (histology or cytology) confirmed diagnosis of urothelial carcinoma or metastatic, progressive, castrate resistant prostate cancer (mCRPC)

* Disease progression on or after at least one platinum-based standard chemotherapy regimen and/or an immune-checkpoint inhibitor (except prostate cohort)

* Have measurable disease per RECIST 1.1 (except prostate cohort)

* Prior treatment with enzalutamide and/or abiraterone (prostate cancer cohort only)

* Patients must have castrate levels of testosterone (\<50 ng/dl \[1.74 nmol/l\]) (Prostate cohort only)

Design:

* Patients meeting eligibility criteria will receive EP0057 (IV Q 2weeks) plus olaparib (PO BID days 3-13 and days 17-26 administered in 28-day cycles, until disease progression or development of intolerable side effects. The MTD of the combination will be used in Phase II.

* Patients in Phase II will receive, the RP2D at DL4R EP0057 12 mg/m2 and olaparib 250 mg BID.

* Blood, tumor and hair samples will be collected at multiple time points for PK, PD analyses. Hair sample collection is optional. Tumor biopsies are optional for SCLC and UC patients and mandatory for mCRPC patients (only baseline biopsy is mandatory).

* Toxicity will be graded according to CTCAE version 4.0.

* Tumor assessments will be made using CT scans (chest, abdomen and pelvis) at baseline and after every 2 cycles (3 cycles for mCRPC) according to RECIST version 1.1.

* After discontinuation of study treatment, follow-up for survival will be carried out every 3 months.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
45
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
1/Phase IEP0057EP0057 + olaparib
2/Phase IIolaparibEP0057 + olaparib at MTD/RP2D
1/Phase IolaparibEP0057 + olaparib
2/Phase IIEP0057EP0057 + olaparib at MTD/RP2D
Primary Outcome Measures
NameTimeMethod
Expansion: To determine overall response rate of EP0057 plus olaparib in patients with mCRPC12 weeks

Determine if slightly more than 50% of patients may be identified as being without progression by 12 weeks.

Phase I: Determine the MTD/RP2D of EP0057 plus olaparib in patients with refractory cancers.28 days

Number of DLTs during the first cycle.

Expansion: Determine the PFS rate in the combination of olaparib plus EP0057 at 16 weeks in SCLC patients.16 weeks

Determine if slightly more than 50% of patients may be identified as being without progression by 16 weeks

Expansion: To determine overall response rate of EP0057 plus olaparib in patients with urothelial carcinoma8 weeks

Best response recorded from the start of the treatment until disease progression/recurrence.

Secondary Outcome Measures
NameTimeMethod
To determine progression-free survival (PFS) on expansion cohortsEvery 3 months post-treatment

PFS is defined as the duration of time from start of treatment to time of progression or death, whichever occurs first.

Evaluate the pharmacokinetic profile of EP0057 (both the total drug and released camptothecin) and olaparib in plasmaCycles 1 and 6

Drug levels in blood.

Determine the duration of response (DOR), overall survival (OS), and progression-free survival (PFS) of the combinationEvery 3 months post-treatment

DOR is measured from the time measurement criteria are met for CR or PR (whichever is first recorded) until the first date that recurrent or progressive disease is objectively documented. OS is determined from the start of treatment until death. PFS is defined as the duration of time from start of treatment to time of progression or death, whichever occurs first.

To determine safety in patients on expansion cohorts: table of toxicities including type, severity, time of onset, time of resolution and probable association with study regimenStart of treatment through 30 days post last dose

List of adverse event frequency

Explore further the safety of the combination: table of toxicities including type, severity, time of onset, time of resolution and probable association with study regimenStart of treatment through 30 days post last dose

List of adverse event frequency

Evaluate the pharmacodynamic (PD) activity of EP0057 in blood, surrogate tissue and tumor biopsy specimens.Baseline, Cycle 1, then every 2 cycles, and at progression

Drug levels in blood.

To determine duration of response and PSA on mCRPC expansion cohortEvery 12 weeks until progression

PSA levels in blood.

Trial Locations

Locations (1)

National Institutes of Health Clinical Center

🇺🇸

Bethesda, Maryland, United States

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