MedPath

Study to Evaluate the Safety and Efficacy of Lenacapavir (GS-6207) in Combination With an Optimized Background Regimen (OBR) in Heavily Treatment Experienced Participants Living With HIV-1 Infection With Multidrug Resistance

Phase 2
Active, not recruiting
Conditions
HIV-1-infection
Interventions
Drug: Failing ARV Regimen
Drug: Optimized Background Regimen (OBR)
Registration Number
NCT04150068
Lead Sponsor
Gilead Sciences
Brief Summary

The primary objective of this study is to evaluate the antiviral activity of lenacapavir (formerly GS-6207) administered as an add-on to a failing regimen (functional monotherapy) in people with human immunodeficiency virus (HIV) (PWH) with multi-drug resistance (MDR).

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
72
Inclusion Criteria
  • Adult aged ≥ 18 years (at all sites) or adolescent aged ≥ 12 and weighing ≥ 35 kg (at sites in North America and Dominican Republic)
  • Currently receiving a stable failing ARV regimen for > 8 weeks
  • Have HIV-1 RNA ≥ 400 copies/mL at screening
  • Have multidrug resistance (resistance to ≥2 agents from ≥3 of the 4 main classes of ARV)
  • Have no more than 2 fully active ARV remaining from the 4 main classes that can be effectively combined to form a viable regimen
  • Able and willing to receive an OBR together with lenacapavir
  • No Hepatitis C virus (HCV) ongoing infection

Note: Other protocol defined Inclusion/Exclusion criteria may apply.

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Cohort 1A: LenacapavirOral LenacapavirParticipants with HIV-1 ribonucleic acid (RNA) ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at Cohort Selection visit compared with screening visit will receive oral lenacapavir (LEN) 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive subcutaneous (SC) LEN 927 mg and will initiate an optimized background regimen (OBR) at Day 1 SC Visit (14 days after the first dose of oral LEN). Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 1A: LenacapavirSubcutaneous LenacapavirParticipants with HIV-1 ribonucleic acid (RNA) ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at Cohort Selection visit compared with screening visit will receive oral lenacapavir (LEN) 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive subcutaneous (SC) LEN 927 mg and will initiate an optimized background regimen (OBR) at Day 1 SC Visit (14 days after the first dose of oral LEN). Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 1A: LenacapavirFailing ARV RegimenParticipants with HIV-1 ribonucleic acid (RNA) ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at Cohort Selection visit compared with screening visit will receive oral lenacapavir (LEN) 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive subcutaneous (SC) LEN 927 mg and will initiate an optimized background regimen (OBR) at Day 1 SC Visit (14 days after the first dose of oral LEN). Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 1A: LenacapavirOptimized Background Regimen (OBR)Participants with HIV-1 ribonucleic acid (RNA) ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at Cohort Selection visit compared with screening visit will receive oral lenacapavir (LEN) 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive subcutaneous (SC) LEN 927 mg and will initiate an optimized background regimen (OBR) at Day 1 SC Visit (14 days after the first dose of oral LEN). Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 1B: Placebo to LenacapavirFailing ARV RegimenParticipants with HIV-1 RNA ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at the Cohort Selection visit compared with screening visit will receive oral LEN placebo on Days 1, 2, and 8 while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive oral LEN 600 mg on Days 15 and 16 and 300 mg on Day 22, and will initiate an OBR on Day 15. At Day 1 SC (14 days after the first dose of oral LEN), participants will receive SC LEN 927 mg while continuing OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue study in the country.
Cohort 1B: Placebo to LenacapavirOptimized Background Regimen (OBR)Participants with HIV-1 RNA ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at the Cohort Selection visit compared with screening visit will receive oral LEN placebo on Days 1, 2, and 8 while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive oral LEN 600 mg on Days 15 and 16 and 300 mg on Day 22, and will initiate an OBR on Day 15. At Day 1 SC (14 days after the first dose of oral LEN), participants will receive SC LEN 927 mg while continuing OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue study in the country.
Cohort 2: LenacapavirOral LenacapavirParticipants with a ≥ 0.5 log10 copies/mL HIV-1 RNA decline at the Cohort Selection Visit compared with the screening visit or with HIV-1 RNA \< 400 copies/mL or if Cohort 1 is fully enrolled will receive oral LEN 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, and will initiate an OBR on Day 1 in Oral Lead-in Period (Baseline to Day 14); followed by Maintenance Period where participants will receive SC LEN 927 mg at Day 1 SC Visit (14 days after the first dose of oral LEN) while continuing their OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 2: LenacapavirOptimized Background Regimen (OBR)Participants with a ≥ 0.5 log10 copies/mL HIV-1 RNA decline at the Cohort Selection Visit compared with the screening visit or with HIV-1 RNA \< 400 copies/mL or if Cohort 1 is fully enrolled will receive oral LEN 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, and will initiate an OBR on Day 1 in Oral Lead-in Period (Baseline to Day 14); followed by Maintenance Period where participants will receive SC LEN 927 mg at Day 1 SC Visit (14 days after the first dose of oral LEN) while continuing their OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Cohort 1B: Placebo to LenacapavirOral LenacapavirParticipants with HIV-1 RNA ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at the Cohort Selection visit compared with screening visit will receive oral LEN placebo on Days 1, 2, and 8 while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive oral LEN 600 mg on Days 15 and 16 and 300 mg on Day 22, and will initiate an OBR on Day 15. At Day 1 SC (14 days after the first dose of oral LEN), participants will receive SC LEN 927 mg while continuing OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue study in the country.
Cohort 1B: Placebo to LenacapavirOral Lenacapavir PlaceboParticipants with HIV-1 RNA ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at the Cohort Selection visit compared with screening visit will receive oral LEN placebo on Days 1, 2, and 8 while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive oral LEN 600 mg on Days 15 and 16 and 300 mg on Day 22, and will initiate an OBR on Day 15. At Day 1 SC (14 days after the first dose of oral LEN), participants will receive SC LEN 927 mg while continuing OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue study in the country.
Cohort 1B: Placebo to LenacapavirSubcutaneous LenacapavirParticipants with HIV-1 RNA ≥ 400 copies/mL and with a \<0.5 log10 HIV-1 RNA decline at the Cohort Selection visit compared with screening visit will receive oral LEN placebo on Days 1, 2, and 8 while continuing their failing regimen in blinded Functional Monotherapy Period (Baseline to Day 14); followed by unblinded Maintenance Period where participants will receive oral LEN 600 mg on Days 15 and 16 and 300 mg on Day 22, and will initiate an OBR on Day 15. At Day 1 SC (14 days after the first dose of oral LEN), participants will receive SC LEN 927 mg while continuing OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue study in the country.
Cohort 2: LenacapavirSubcutaneous LenacapavirParticipants with a ≥ 0.5 log10 copies/mL HIV-1 RNA decline at the Cohort Selection Visit compared with the screening visit or with HIV-1 RNA \< 400 copies/mL or if Cohort 1 is fully enrolled will receive oral LEN 600 mg tablet on Days 1 and 2 and 300 mg tablet on Day 8, and will initiate an OBR on Day 1 in Oral Lead-in Period (Baseline to Day 14); followed by Maintenance Period where participants will receive SC LEN 927 mg at Day 1 SC Visit (14 days after the first dose of oral LEN) while continuing their OBR. Participants will receive their subsequent SC LEN injection at Week 26 Visit (relative to Day 1 SC). Participants will be given an option to receive SC LEN injection at Weeks 52 and 156, while continuing their OBR, until the product becomes accessible to participants through an access program or until Gilead elects to discontinue the study in the country.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants in Cohort 1 Achieving a Reduction of ≥ 0.5 log10 Copies/mL in Human Immunodeficiency Virus-1 Ribonucleic Acid (HIV-1 RNA) From Baseline to the End of Functional Monotherapy PeriodBaseline up to Day 1 SC Visit (14 days after the first dose of oral lencapavir) or Day 15
Secondary Outcome Measures
NameTimeMethod
Percentage of Participants in Cohort 1 With Plasma HIV-1 RNA < 50 Copies/mL at Week 52 Based on the US FDA-defined Snapshot AlgorithmWeek 52
Percentage of Participants in Cohort 1 With Plasma HIV-1 RNA < 200 Copies/mL at Week 52 Based on the US FDA-defined Snapshot AlgorithmWeek 52
Percentage of Participants in Cohort 1 With Plasma HIV-1 RNA < 50 Copies/mL at Week 26 Based on the US FDA-defined Snapshot AlgorithmWeek 26 (26 weeks after first dose of subcutaneous lenacapavir)

The percentage of participants in cohort 1 with plasma HIV-1 RNA \< 50 copies/mL at Week 26 was analyzed using the United States Food and Drug Administration (US FDA)-defined snapshot algorithm, which defines a participant's virologic response status using only the viral load at the predefined time point within an allowed window of time, along with study drug discontinuation status.

Percentage of Participants in Combined Cohorts 1 and 2 With Plasma HIV-1 RNA < 200 Copies/mL From the First SC Dose of Lenacapavir Based on the US FDA-defined Snapshot AlgorithmWeek 156
Percentage of Participants in Cohort 1 With Plasma HIV-1 RNA < 200 Copies/mL at Week 26 Based on the US FDA-defined Snapshot AlgorithmWeek 26 (26 weeks after first dose of subcutaneous lenacapavir)

The percentage of participants in cohort 1 with plasma HIV-1 RNA \< 200 copies/mL at Week 26 was analyzed using the US FDA-defined snapshot algorithm, which defines a participant's virologic response status using only the viral load at the predefined time point within an allowed window of time, along with study drug discontinuation status.

Percentage of Participants in Combined Cohorts 1 and 2 With Plasma HIV-1 RNA < 50 Copies/mL From the First SC Dose of Lenacapavir Based on the US FDA-defined Snapshot AlgorithmWeek 156
Percentage of Participants in Combined Cohorts 1 and 2 With Plasma HIV-1 RNA < 50 Copies/mL From the First Subcutaneous (SC) Dose of Lenacapavir Based on the US FDA-defined Snapshot AlgorithmWeek 104

Trial Locations

Locations (75)

Mills Clinical Research

🇺🇸

Los Angeles, California, United States

Emory Hospital Midtown Infectious Disease Clinic

🇺🇸

Atlanta, Georgia, United States

North Texas Infectious Diseases Consultants, P.A.

🇺🇸

Dallas, Texas, United States

Maple Leaf Research/Maple Leaf Medical Clinic

🇨🇦

Toronto, Ontario, Canada

AIDS Healthcare Foundation - South Beach

🇺🇸

Miami Beach, Florida, United States

Gary J. Richmond, M.D., P.A.

🇺🇸

Fort Lauderdale, Florida, United States

Floridian Clinical Research

🇺🇸

Hialeah, Florida, United States

Perelman Center for Advanced Medicine at the Hospital of the University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

Vancouver ID Research and Care Centre Society

🇨🇦

Vancouver, British Columbia, Canada

Hospital Clinic de Barcelona

🇪🇸

Barcelona, Spain

Helen Joseph Hospital

🇿🇦

Johannesburg, South Africa

The Ottawa Hospital

🇨🇦

Ottawa, Canada

Midland Florida Clinical Research Center, LLC

🇺🇸

DeLand, Florida, United States

Durban International Clinical Research Site, Enhancing Care Foundation

🇿🇦

Durban, South Africa

Eisenhower Health Center at Rimrock

🇺🇸

Palm Springs, California, United States

Triple O Research Institute, P.A.

🇺🇸

West Palm Beach, Florida, United States

Southampton Healthcare, Inc.

🇺🇸

Saint Louis, Missouri, United States

The Miriam Hospital

🇺🇸

Providence, Rhode Island, United States

Midway Immunology and Research Center

🇺🇸

Fort Pierce, Florida, United States

Hospital Universitario La Paz

🇪🇸

Madrid, Spain

Washington Health Institute

🇺🇸

Washington, District of Columbia, United States

Hôpital Bichat-Claude Bernard

🇫🇷

Paris, France

Howard Brown Health Center

🇺🇸

Chicago, Illinois, United States

University of Naples Federico II

🇮🇹

Bergamo, Italy

UOC Malattie Infettive - ASST Spedali Civili Di Brescia - Piazzale Spedali Civili 1

🇮🇹

Brescia, Italy

Clinique de médecine urbaine du Quartier Latin

🇨🇦

Montreal, Quebec, Canada

Clinical Alliance for Research and Education - Infectious Diseases, LLC (CARE-ID)

🇺🇸

Annandale, Virginia, United States

National Hospital Organization Nagoya Medical Center

🇯🇵

Nagoya, Japan

Vx Pharma

🇿🇦

Pretoria, South Africa

Be Well Medical Center

🇺🇸

Berkley, Michigan, United States

AIDS Arms, Inc. DBA Prism Health North Texas

🇺🇸

Dallas, Texas, United States

Northstar Healthcare

🇺🇸

Chicago, Illinois, United States

Hospital Dr. Salvador Bienvenido Gautier

🇩🇴

Santo Domingo, Dominican Republic

U.O.C. Malattie Infettive - Fondazione Policlinico Universitario A. Gemelli IRCCS

🇮🇹

Rome, Italy

Perinatal HIV Research Unit (PHRU)

🇿🇦

Soweto, South Africa

Hôpital Saint-Louis

🇫🇷

Paris, France

Hôpital Saint-Antoine

🇫🇷

Paris, France

New York-Presbyterian/Queens

🇺🇸

Flushing, New York, United States

North Shore University Hospital/Division of Infectious Diseases

🇺🇸

Manhasset, New York, United States

Divisione di Malattie Infettive, IRCCS Ospedale San Raffaele

🇮🇹

Milano, Italy

Hospital Universitari Germans Trías i Pujol

🇪🇸

Badalona, Spain

Faculty of Medicine Ramathibodi Hospital, Mahidol University

🇹🇭

Bangkok, Thailand

Universitätsklinikum Frankfurt, Medizinische Klinik II

🇩🇪

Frankfurt, Hesse, Germany

Bamrasnaradura Infectious Diseases Institute

🇹🇭

Nonthaburi, Thailand

Thai Red Cross AIDS Research Center

🇹🇭

Bangkok, Thailand

Faculty of Medicine Siriraj Hospital, Mahidol University

🇹🇭

Bangkok, Thailand

National Taiwan University Hospital

🇨🇳

Taipei, Taiwan

Faculty of Medicine, Khon Kaen University

🇹🇭

Khon Kaen, Thailand

Kaohsiung Medical University Chung-Ho Memorial Hospital

🇨🇳

Kaohsiung, Taiwan

Kaohsiung Veterans General Hospital

🇨🇳

Kaohsiung, Taiwan

Far Eastern Memorial Hospital

🇨🇳

New Taipei City, Taiwan

Taoyuan General Hospital, Ministry of Health and Welfare

🇨🇳

Taoyuan City, Taiwan

U.O.C. IMMUNODEFICIENZE VIRALI - Istituto Nazionale Malattie Infettive Lazzaro Spallanzani IRCCS

🇮🇹

Roma, Italy

Universitätsklinikum Essen, Klinik für Dermatologie und Venerologie

🇩🇪

Essen, Germany

Ruane Clinical Research Group Inc

🇺🇸

Los Angeles, California, United States

Atlanta ID Group, PC

🇺🇸

Atlanta, Georgia, United States

Atrium Health- Infectious Disease Consultants

🇺🇸

Charlotte, North Carolina, United States

1265 Union Avenue, 8 East

🇺🇸

Memphis, Tennessee, United States

St Hope Foundation

🇺🇸

Bellaire, Texas, United States

DCOL Center for Clinical Research

🇺🇸

Longview, Texas, United States

Hôpital Sainte-Marguerite

🇫🇷

Marseille, France

Instituto Dominicano de Estudios Virologicos (IDEV)

🇩🇴

Santo Domingo, Dominican Republic

ICH Study Center GmbH & Co. KG

🇩🇪

Hamburg, Germany

Tokyo Medical University Hospital

🇯🇵

Tokyo, Japan

National Hospital Organization Osaka National Hospital

🇯🇵

Osaka, Japan

Center Hospital of the National Center for Global Health and Medicine

🇯🇵

Tokyo, Japan

Hospital Universitario Virgen del Rocío

🇪🇸

Sevilla, Spain

Chatham County Health Department

🇺🇸

Savannah, Georgia, United States

St. Joseph's Hospital Comprehensive Research Institute

🇺🇸

Tampa, Florida, United States

One Community Health

🇺🇸

Sacramento, California, United States

Yale University; School of Medicine

🇺🇸

New Haven, Connecticut, United States

Orlando Immunology Center

🇺🇸

Orlando, Florida, United States

Jacobi Medical Center

🇺🇸

Bronx, New York, United States

Central Texas Clinical Research

🇺🇸

Austin, Texas, United States

The Crofoot Research Center, INC.

🇺🇸

Houston, Texas, United States

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