MedPath

Cord Blood Transplantation for Patients With Cancer

Phase 2
Terminated
Conditions
Hematological Disease
Interventions
Drug: Antithymocyte Globulin (ATG)
Drug: Total Body Irradiation (TBI)
Registration Number
NCT01359254
Lead Sponsor
University of Chicago
Brief Summary

The primary objective of this study is to assess the rate of engraftment with combined haploidentical-cord blood transplantation in patients with pre-existing donor specific antibodies and in those with active disease.

Detailed Description

Primary Objective

- To assess the rate of engraftment with combined haploidentical-cord blood transplantation in patients with pre-existing donor specific anti-HLA antibodies and in those with active disease

Secondary Objectives

* To determine the long term fate of the haplo transplant and the cord blood transplant in this setting.

* To describe the incidence and severity of acute and chronic GVHD.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
1
Inclusion Criteria
  • Relapsed or refractory acute leukemia (myeloid or lymphoid)
  • Acute leukemia in first remission at high-risk for recurrence
  • Chronic myelogenous leukemia in accelerated phase or blast-crisis
  • Chronic myelogenous leukemia in chronic phase
  • Recurrent or refractory malignant lymphoma or Hodgkin lymphoma
  • Chronic lymphocytic leukemia, relapsed or with poor prognostic features
  • Multiple myeloma
  • Myelodysplastic syndrome
  • Chronic myeloproliferative disease
  • Hemoglobinopathies
  • Aplastic anemia
Exclusion Criteria
  • Zubrod performance status > 2
  • Life expectancy is severely limited by concomitant illness
  • Patients with severely decreased LVEF or impaired pulmonary function tests
  • Estimated Creatinine Clearance <50 ml/min
  • Serum bilirubin> 2.0 mg/dl or SGPT >3 x upper limit of normal
  • Evidence of chronic active hepatitis or cirrhosis
  • HIV-positive
  • Patient is pregnant
  • Patient or guardian not able to sign informed consent

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Conditioning Regimen IIAntithymocyte Globulin (ATG)Arm II contains fludarabine, busulfan, antithymocyte globulin (ATG), and total body irradiation (TBI).
Conditioning Regimen IITotal Body Irradiation (TBI)Arm II contains fludarabine, busulfan, antithymocyte globulin (ATG), and total body irradiation (TBI).
Conditioning Regimen IAntithymocyte Globulin (ATG)Arm I contains fludarabine, melphalan, and antithymocyte globulin (ATG)
Conditioning Regimen IMelphalanArm I contains fludarabine, melphalan, and antithymocyte globulin (ATG)
Conditioning Regimen IFludarabineArm I contains fludarabine, melphalan, and antithymocyte globulin (ATG)
Conditioning Regimen IIFludarabineArm II contains fludarabine, busulfan, antithymocyte globulin (ATG), and total body irradiation (TBI).
Conditioning Regimen IIBusulfanArm II contains fludarabine, busulfan, antithymocyte globulin (ATG), and total body irradiation (TBI).
Primary Outcome Measures
NameTimeMethod
Cord Blood Engraftment by Day 100100 days

Percent of subjects with cord blood engraftment on or before day 100. Detectable cord blood engraftment should be present by day 100 in at least 50% of patients.

As of 44 days post-transplant, only haploidentical donor chimerism achieved in the one patient enrolled in the Fludarabine, melphalan, and ATG arm. There were no cord cells detected for this patient.

Secondary Outcome Measures
NameTimeMethod
Survival at Day 100100 days

Percent of subjects who are alive 100 days after the stem cell infusion

Trial Locations

Locations (1)

University of Chicago

🇺🇸

Chicago, Illinois, United States

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