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ESCORT-HU Extension: European Sickle Cell Disease Cohort - Hydroxyurea - Extension Study

Active, not recruiting
Conditions
Sickle Cell Disease
Interventions
Registration Number
NCT04707235
Lead Sponsor
Theravia
Brief Summary

As safety information pertaining to the long-term use of HU remains incomplete in spite of the first safety study (ESCORT-HU), an extension of the latter is proposed. ESCORT-HU Extension study aims at evaluating the long-term safety of Siklos® focusing on some questions regarding its safety when used in current practice in adults and paediatric patients treated with Siklos® and followed for up to 5 years. The study will focus on the following concerns : occurrence and incidence of malignancies, leg ulcers, male fertility impairment and serious unexpected AEs causally related to Siklos®.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
2093
Inclusion Criteria
  • Male or female patients with symptomatic SCD,
  • ≥ 2 years old,
  • Treated with Siklos®,
  • Having been informed of the study by the investigator and consenting to participate, or whose parents or legal guardians are consenting for their child to participate.

To allow risk evaluation, participants must belong at least to one of the subpopulations defined below:

  • Participants previously enrolled in ESCORT-HU who agree to participate in ESCORT-HU Extension study,

  • New participants with any of the following criteria:

    • history of HU treatment for more than 5 years or
    • prepubescent over 10 years of age for girls and 13 years of age for boys at enrolment, or
    • with history of leg ulcer, or
    • pregnant women without interruption of Siklos® 3 months before the beginning of the pregnancy or,
    • males treated with Siklos® whose partner is pregnant and without discontinuation of Siklos® 3 months before the beginning of the pregnancy.
Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Sickle cell disease patients treated with SiklosHydroxycarbamide-
Primary Outcome Measures
NameTimeMethod
Occurrence and incidence of the number of malignancies, leg ulcers, male fertility impairment and serious unexpected AEs causally related to Siklos®5 years
Occurrence and incidence of the number of leg ulcers5 years
Occurrence and incidence of male fertility impairment5 years
Occurrence and incidence of serious unexpected AEs causally related to Siklos®5 years
Secondary Outcome Measures
NameTimeMethod
Measure of quality of life with SF12 questionnaire5 years

Quality of life for adults SCD patients

Mean age of puberty5 years

Document changes in fertility status in males and females

Mean number of patients with the use of a contraception, incidence of the use of semen cryopreservation and of semen analysis performed5 years

Document changes in fertility status in males and females

Number of switch and combination with alternative treatment5 years
Frequency and reason for temporary or permanent discontinuations of Siklos®5 years

Potential barriers to the compliance to the prescription of Siklos

Incidence of the use of semen cryopreservation and of semen analysis performed5 years

Document changes in fertility status in males and females

Incidence of semen analysis performed5 years

Document changes in fertility status in males and females

Management of Siklos® during pregnancy and outcome of pregnancy following exposure at the time of conception or at any time during the pregnancy5 years

Outcome of pregnancies Following exposure to Siklos® at the time of conception (in participant and participant's partner) or at any time during the pregnancy

Trial Locations

Locations (87)

Bordeaux Hospital Adults

🇫🇷

Bordeaux, France

Bordeaux Hospital Children

🇫🇷

Bordeaux, France

Tours Regional University Hospital Center Adults

🇫🇷

Chambray-lès-Tours, France

Estaing Hospital Children

🇫🇷

Clermont-Ferrand, France

Amiens - Picardie Hospital Adults

🇫🇷

Amiens, France

Clinique de l'Europe Amiens

🇫🇷

Amiens, France

Angers Hospital Adults

🇫🇷

Angers, France

Amiens Picardie Hospital Children

🇫🇷

Amiens, France

Angers Hospital Center Children

🇫🇷

Angers, France

Robert Ballanger Hospital Adults

🇫🇷

Aulnay-sous-Bois, France

Avicenne Hospital Adults

🇫🇷

Bobigny, France

Robert Ballanger Hospital Children

🇫🇷

Aulnay-sous-Bois, France

Jean Verdier Hospital Children

🇫🇷

Bondy, France

Ambroise Paré Hospital Children

🇫🇷

Boulogne-Billancourt, France

Sud Francilien Hospital Center Adults

🇫🇷

Corbeil-Essonnes, France

Centre Hospitalier Sud Francilien

🇫🇷

Corbeil-Essonnes, France

Louis Mourier Hospital Children

🇫🇷

Colombes, France

Sud Oise Public Hospital Group Adults

🇫🇷

Creil, France

Henri Mondor Hospital Adults

🇫🇷

Créteil, France

Intercommunal Hospital Center of Créteil Adults and Children

🇫🇷

Créteil, France

Dreux Hospital Center Children

🇫🇷

Dreux, France

Gonesse Hospital Children

🇫🇷

Gonesse, France

Bicêtre Hospital Adults

🇫🇷

Le Kremlin-Bicêtre, France

Grenoble Hospital Children

🇫🇷

La Tronche, France

Hôpital Bicêtre

🇫🇷

Le Kremlin-Bicêtre, France

CH du Mans

🇫🇷

Le Mans, France

Jeanne De Flandre Hospital Children

🇫🇷

Lille, France

Hôpital Saint-Vincent de Paul

🇫🇷

Lille, France

Hôpital Mère-Enfant - CHU de Limoges

🇫🇷

Limoges, France

Edouard Herriot Hospital Adults

🇫🇷

Lyon, France

Timone Hospital Adults

🇫🇷

Marseille, France

Meaux Hospital Center Children

🇫🇷

Meaux, France

Timone Hospital Children

🇫🇷

Marseille, France

Meaux Hospital Center Adults

🇫🇷

Meaux, France

St Eloi Hospital Adults

🇫🇷

Montpellier, France

Montpellier Hospital Children

🇫🇷

Montpellier, France

Emile Muller Hospital Adults

🇫🇷

Mulhouse, France

Nice Hospital Children

🇫🇷

Nice, France

Nantes Hospital Children

🇫🇷

Nantes, France

Nantes Hospital Adults

🇫🇷

Nantes, France

Orléans Hospital Adults

🇫🇷

Orléans, France

Armand Trousseau Hospital Children

🇫🇷

Paris, France

Saint-Antoine Hospital Adults

🇫🇷

Paris, France

Georges Pompidou European Hospital Adults

🇫🇷

Paris, France

Necker Hospital Adults

🇫🇷

Paris, France

Necker Hospital Children

🇫🇷

Paris, France

Robert Debré Hospital Children

🇫🇷

Paris, France

Centre hospitalier Perpignan

🇫🇷

Perpignan, France

Poitiers Hospital Adults

🇫🇷

Poitiers, France

American Hospital Children

🇫🇷

Reims, France

Reims Hospital Adults

🇫🇷

Reims, France

Charles Nicolle Hospital Adults

🇫🇷

Rouen, France

Pontchaillou Hospital Adults

🇫🇷

Rennes, France

Rouen Hospital Children

🇫🇷

Rouen, France

Yves Le Foll. Hospital Center Children

🇫🇷

Saint-Brieuc, France

Delafontaine Hospital Center Adults

🇫🇷

Saint-Denis, France

Toulouse University Institute of cancer Adults

🇫🇷

Toulouse, France

Hautepierre Hospital Children

🇫🇷

Strasbourg, France

Children Hospital

🇫🇷

Toulouse, France

Saint-Quentin Hospital Center Adults

🇫🇷

Saint-Quentin, France

CH de Cayenne

🇬🇫

Cayenne, French Guiana

Versailles Hospital Center Children

🇫🇷

Versailles, France

Clocheville Regional University Hospital Center Children

🇫🇷

Tours, France

Nancy Hospital Children

🇫🇷

Vandoeuvre les nancy, France

Charité Hospital Children

🇩🇪

Berlin, Germany

Düsseldorf Hospital Children

🇩🇪

Düsseldorf, Germany

Laiko General Hospital Adults

🇬🇷

Athens, Greece

Koblenz Hospital Children

🇩🇪

Koblenz, Germany

Hamburg Hospital Children

🇩🇪

Hamburg, Germany

Freiburg Hospital Children

🇩🇪

Freiburg, Germany

Hôpital RICOU - CHU Pointe-à-Pitre Abymes

🇬🇵

Pointe-à-Pitre, Guadeloupe

CHU Martinique Adults

🇲🇶

Le Lamentin, Martinique

CHU Sud Réunion

🇷🇪

Saint-Pierre, Réunion

Centre hospitalier de Kourou Children

🇬🇫

Kourou, French Guiana

Hôpital RICOU - CHU Pointe-à-Pitre Abymes Children

🇬🇵

Pointe-à-Pitre, Guadeloupe

Centre Hospitalier de l'Ouest Guyanais Franck Joly Adults

🇬🇫

Saint-Laurent-du-Maroni, French Guiana

CHU Fort de France Children

🇲🇶

Fort-de-France, Martinique

Centre Hospitalier de l'Ouest Guyanais Franck Joly Children

🇬🇫

Saint-Laurent-du-Maroni, French Guiana

Padova Hospital Children

🇮🇹

Padova, Italy

Verona Hospital Children

🇮🇹

Verona, Italy

AUO Policlinico di Modena

🇮🇹

Modena, Italy

Napoli Hospital Children

🇮🇹

Napoli, Italy

Louis Mourier Hospital Adults

🇫🇷

Colombes, France

Marne-La-Vallée Hospital Center Children

🇫🇷

Jossigny, France

Grenoble Hospital Adults

🇫🇷

La Tronche, France

Delafontaine Hospital Center Children

🇫🇷

Saint-Denis, France

Hematology and oncology institute Children

🇫🇷

Lyon, France

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