MedPath

Safety and Efficacy of Propranolol Eye Drops in Treating Retinopathy of Premature

Phase 2
Completed
Conditions
Retinopathy of Prematurity
Interventions
Registration Number
NCT02014454
Lead Sponsor
Azienda Ospedaliero, Universitaria Meyer
Brief Summary

The aim of the present study is to evaluate the safety and efficacy of propranolol eye drops in preterm newborns with a precocious stage of retinopathy of prematurity (ROP). Preterm newborns (gestational age 23-32 weeks) with a stage 2 ROP (zone II without plus) will receive propranolol eye drops treatment until retinal vascularization will be completed.

Propranolol concentrations will be measured on dried blood spots during the first 3 days of treatment and at the steady state. Cardiovascular and respiratory parameters will be continuously monitored. Blood samplings checking metabolic, renal and liver functions will be performed periodically, as well as cardiac function, in order to verify the treatment safety. Serial ophthalmological evaluations will be planned to monitor the efficacy of the treatment, the ROP progression and the possible complications.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
23
Inclusion Criteria
  • Preterm newborns (gestational age 23-32 weeks) with stage 2 ROP, zone II without plus.
  • A signed parental informed consent.
Exclusion Criteria
  • Newborns with heart failure;
  • Newborns with congenital cardiovascular anomalies, except for persistent ductus arteriosus, patent foramen ovale and small ventricular septal defects;
  • Newborns with recurrent bradycardia (heart rate < 90 beat per minute);
  • Newborns with second or third degree atrioventricular block;
  • Newborns with hypotension;
  • Newborns with renal failure;
  • Newborns with actual cerebral haemorrhage;
  • Newborns with other diseases which contraindicate the use of beta-adrenoreceptor blockers.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Propranolol eye dropsPropranolol eye dropsAll the enrolled preterm newborns will receive propranolol as ophthalmic solution (0,1%): 3 microdrops of 6 microliters (μL) propranolol solution (= 6 μg propranolol/microdrop) will be topically applied with a calibrated pipette, in each eye, three times daily (every 8 hours).The treatment will continue until the complete development of retinal vascularization, but no more than 60 days. The propranolol treatment will be always associated to the conventional approach adopted by the Early Treatment for Retinopathy of Prematurity Study (ETROP Cooperative Group.
Primary Outcome Measures
NameTimeMethod
Incidence rate of progression from stage 2 ROP to more severe stage ROP (stage 2 or 3 with plus, stage 4 and stage 5)participants will be followed for the duration of hospital stay, an expected average of 2 months

Eye drop propranolol is considered to be effective in counteracting the progression of ROP if the treatment decreases the incidence rate of progression from stage 2 ROP to more severe stage ROP (stage 2 or 3 with plus) from actual 38% to 19% or less.

Plasma concentrations of propranolol at the steady state10th day of treatment

To evaluate the safety of eye drop propranolol we consider the plasma propranolol concentrations at the steady state. In particular it should be always less than 20 ng/ml, which is the plasma concentration, at the steady state, reported after oral administration of propranolol in the PROP-ROP study

Secondary Outcome Measures
NameTimeMethod
Number of newborns who progress to Stage 4 or 5 ROP with total or partial retinal detachmentparticipants will be followed for the duration of hospital stay, an expected average of 2 months
Collection of adverse events due to eye drop propranolol treatmentparticipants will be followed for the duration of hospital stay, an expected average of 2 months
Number of newborns who progress to Stage 3 without plus ROPparticipants will be followed for the duration of hospital stay, an expected average of 2 months
Number of newborns who need vitrectomyparticipants will be followed for the duration of hospital stay, an expected average of 2 months
Number of newborns who need laser treatmentparticipants will be followed for the duration of hospital stay, an expected average of 2 months
Number of newborns who need rescue treatment with bevacizumabparticipants will be followed for the duration of hospital stay, an expected average of 2 months

Trial Locations

Locations (2)

Neonatal Intensive Care Unit, A. Meyer University Childrens' Hospital

🇮🇹

Florence, Italy

Institute of Pediatrics and Neonatology, Fondazione IRCCS Ospedale Maggiore Policlinico, Mangiagalli e Regina Elena, University of Milan

🇮🇹

Milan, Italy

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