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A Study of Molidustat for Treatment of Renal Anemia in Peritoneal Dialysis Subjects

Phase 3
Completed
Conditions
Anemia
Renal Insufficiency, Chronic
Interventions
Registration Number
NCT03418168
Lead Sponsor
Bayer
Brief Summary

The purpose of this study is to evaluate the efficacy and safety of molidustat in peritoneal dialysis subjects with renal anemia

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
51
Inclusion Criteria
  • Subject with end-stage kidney disease (ESKD) on peritoneal dialysis prior to assignment and not expected to start maintenance dialysis (e.g., hemodialysis, hemodiafiltration) other than peritoneal dialysis during the study period

  • Body weight > 40 and ≤ 160 kg at screening

  • Male or female subject ≥ 20 years of age at screening

  • At least one kidney

  • Subjects who meet one of the 1 or 2 following criteria

    • Subjects untreated with ESA at assignment: Mean of the last 2 Hb level (central laboratory measurement) during the screening period must be ≥ 8.0 and < 11.0 g/dL (2 measurements must be taken ≥ 2 days apart and the difference between the 2 measurements must be < 1.2 g/dL) with the last screening Hb measurement within 14 days prior to study drug assignment
    • Subjects pre treated with ESA at assignment: Mean of the last 2 Hb level (central laboratory measurement) during the screening period must be ≥ 10.0 and < 13.0 g/dL (2 measurements must be taken ≥ 2 days apart and the difference between the 2 measurements must be < 1.2 g/dL) with the last screening Hb measurement within 14 days prior to study drug assignment
  • Subjects who meet one of the 1 or 2 following criteria

    • Subjects untreated with ESA at assignment: Subject with ESKD on peritoneal dialysis for at least 2 weeks prior to assignment. AND. Subject not received ESA for 8 weeks prior to assignment. OR. In case of the patient washed out from ESAs, when mean of the last 2 Hb level (at least 2 central laboratory measurements must be taken ≥ 2 days apart) has decrease to ≥ 0.5g/dL from the Hb level (central laboratory measurement) after the last ESA administration, AND the interval from the last ESA administration to the study drug assignment should be over 2 week for epoetin-alpha/beta, 4 weeks for darbepoetin alpha or epoetin beta pegol

    • Subjects pre treated with ESA at assignment:

      • Subject with ESKD on peritoneal dialysis for at least 12 weeks prior to assignment
      • Subject treated with ESA by IV or SC within 8 weeks prior to assignment
      • Treated with 2 or 4 weekly dose of darbepoetin alfa, 4 weekly dose of epoetin beta pegol, OR 3 times per week, twice per week, weekly or bi-weekly dose of epoetin alfa/beta, and having had no more than one dose change within 8 weeks prior to assignment
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Exclusion Criteria
  • New York Heart Association (NYHA) Class III or IV congestive heart failure
  • History of cardio- (cerebro-) vascular events (e.g., unstable angina, myocardial infarction, stroke, pulmonary thromboembolism, and acute limb ischemia) within 6 months prior to randomization
  • Sustained and poorly controlled arterial hypertension (defined as systolic BP≥ 180mmHg or diastolic BP ≥ 110mmHg) or hypotension (defined as systolic BP < 90mmHg) at randomization
  • Proliferative choroidal or retinal disease, such as neovascular age-related macular degeneration or proliferative diabetic retinopathy requiring invasive treatment (e.g., intraocular injections or laser photocoagulation)
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Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Molidustat (BAY85-3934)Molidustat (BAY85-3934)Molidustat group
Primary Outcome Measures
NameTimeMethod
Responder rate: proportion of responders among the subjectsWeek 30 to 36

Responder is defined as meeting all of the following criteria:

(i) Mean of the Hb levels in the target range (ii) ≥ 50% of the Hb levels in the target range (iii) No rescue treatment

Secondary Outcome Measures
NameTimeMethod
Change in mean Hb levelBaseline and Week 30 to 36
Proportion of subjects with mean hemoglobin levels are in the target rangeWeek 30 to 36
Proportion of subjects with hemoglobin levels in the target rangeUp to 36 weeks
Percentage of days in the target Hb range during the evaluation periodWeek 30 to 36
Mean Hb (Hemoglobin) levelWeek 30 to 36
Rate of rise in Hb (Hemoglobin) level (g/dL/week)Up to 4 weeks
Change in Hb levelBaseline and Up to Week 36
Proportion of subjects who meet each component of the responseWeek 30 to 36

Response:

(i) Mean of the Hb levels in the target range (ii) ≥ 50% of the Hb levels in the target range (iii) No rescue treatment

Proportion of subjects with mean hemoglobin levels are below the target rangeWeek 30 to 36
Proportion of subjects whose maximum rise in Hb between each consecutive visits is above 0.5 g/dL/weekUp to 36 weeks

Defined as change in Hb level / duration between two visits (weeks)

Proportion of subjects whose Hb level was ≥ 13.0 g/dL or < 8.0 g/dLUp to 36 weeks
Proportion of subjects with hemoglobin levels above the target rangeUp to 36 weeks
Proportion of subjects with mean hemoglobin levels are above the target rangeWeek 30 to 36
Percentage of Hb levels in target range during the evaluation periodWeek 30 to 36

Defined as the number of measurements in the target range / number of measurements x 100 \[%\])

Percentage of days in the target Hb range during the treatment periodUp to 36 weeks
Number of participants with serious adverse eventsUp to 36 weeks
Percentage of Hb levels in target range during the treatment periodUp to 36 weeks

Defined as the number of measurements in the target range / number of measurements x 100 \[%\])

Proportion of subjects who received at least one rescue treatmentUp to 36 weeks
EPO (Erythropoietin) serum concentration of MolidustatBaseline, Week 8, Wee16 and Week 36
Rate of rise in Hb level (g/dL/week) between each consecutive visitsUp to 36 weeks
Maximum concentration (Cmax) of MolidustatBaseline, Week 8, Wee16 and Week 36
Area under the concentration-time curve (AUC) of MolidustatBaseline, Week 8, Wee16 and Week 36
Proportion of subjects with hemoglobin levels below the target rangeUp to 36 weeks
Hb levelBaseline and Up to Week 36

Trial Locations

Locations (27)

Japanese Red Cross Fukuoka Hospital

🇯🇵

Fukuoka, Japan

Fukushima Medical University Hospital

🇯🇵

Fukushima, Japan

Asahi University Hospital

🇯🇵

Gifu, Japan

JCHO Kyushu Hospital

🇯🇵

Kitakyushu, Fukuoka, Japan

Kurume University Hospital

🇯🇵

Kurume, Fukuoka, Japan

Elm Grove Clinic

🇯🇵

Sapporo, Hokkaido, Japan

National Hospital Organization Beppu Medical Center

🇯🇵

Beppu, Oita, Japan

Fuchu Hospital

🇯🇵

Izumi, Osaka, Japan

Kyushu University Hospital

🇯🇵

Fukuoka, Japan

Nara Prefecture General Medical Center

🇯🇵

Nara, Japan

National Hospital Organization Kyoto Medical Center

🇯🇵

Kyoto, Japan

Japanese Red Cross Oita Hospital

🇯🇵

Oita, Japan

Ehime Prefectural Central Hospital

🇯🇵

Matsuyama, Ehime, Japan

Fukui-ken Saiseikai Hospital

🇯🇵

Fukui, Japan

Showa University Fujigaoka Hospital

🇯🇵

Yokohama, Kanagawa, Japan

Osaka General Medical Center

🇯🇵

Osaka, Japan

Kokura Memorial Hospital

🇯🇵

Kitakyushu, Fukuoka, Japan

Fujisawa City Hospital

🇯🇵

Fujisawa, Kanagawa, Japan

Toranomon Hospital Kajigaya

🇯🇵

Kawasaki, Kanagawa, Japan

Tohoku Medical and Pharmaceutical University Hospital

🇯🇵

Sendai, Miyagi, Japan

Kainan Hospital

🇯🇵

Yatomi, Aichi, Japan

Kobe City Medical Center General Hospital

🇯🇵

Kobe, Hyogo, Japan

Shonan Kamakura General Hospital

🇯🇵

Kamakura, Kanagawa, Japan

Okinawa prefectural Chubu Hospital

🇯🇵

Uruma, Okinawa, Japan

Niigata City General Hospital

🇯🇵

Niigata, Japan

Niigata Prefectural Shibata Hospital

🇯🇵

Shibata, Niigata, Japan

Fukuoka University Hospital

🇯🇵

Fukuoka, Japan

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