MedPath

A Study in Participants With Asthma Initiating Treatment With Omalizumab (Xolair)

Phase 4
Completed
Conditions
Asthma
Interventions
Registration Number
NCT01922037
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This multicenter, prospective study will evaluate the baseline participant characteristics (including biomarkers) associated with a variety of individual and composite clinical outcomes in participants with moderate to severe asthma initiating treatment with omalizumab.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
806
Inclusion Criteria
  • Participants identified by the investigator as a candidate for treatment for asthma with omalizumab
  • Confirmation of access to omalizumab through insurance or other source of funding
Exclusion Criteria
  • Enrollment in any other concurrent clinical trial or observational study
  • Participants for whom omalizumab treatment is contraindicated
  • Participants who had a prior allergic reaction to omalizumab or its excipients
  • Participants treated with omalizumab within the previous year
  • Participants who received an experimental drug as part of another study within 3 months of enrollment

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Participants With Allergic AsthmaOmalizumabParticipants with allergic asthma, who have decided to initiate treatment with omalizumab will be observed until a maximum follow-up of 12 months, death, withdrawal of consent, loss to follow-up, or study closure, whichever occurs first.
Primary Outcome Measures
NameTimeMethod
Total Number of Asthma Exacerbations During Months 1-12Months 1-12

An asthma exacerbation was defined as new or increased asthma symptoms which resulted in either hospitalization and/or treatment with systemic corticosteroids (or increase of stable maintenance dose) for \>/= 3 days.

Secondary Outcome Measures
NameTimeMethod
Total Number of Asthma-Related Emergency Room (ER) Visits During Months 1-6Months 1-6
Total Number of Asthma-Related ER Visits During Months 7-12Months 7-12
Total Number of Asthma Exacerbations During Months 1-6Months 1-6

An asthma exacerbation was defined as new or increased asthma symptoms which resulted in either hospitalization and/or treatment with systemic corticosteroids (or increase of stable maintenance dose) for \>/=3 days.

Total Number of Asthma-Related ER Visits During Months 1-12Months 1-12
Total Number of Asthma-Related Unscheduled Physician's Office Visits During Months 1-12Months 1-12
Total Number of Asthma-Related Unscheduled Physician's Office Visits During Months 1-6Months 1-6
Total Number of Asthma-Related Unscheduled Physician's Office Visits During Months 7-12Months 7-12
Percentage of Participants by Number of Asthma ExacerbationsMonths 1-12

Percentage of participants by number of asthma exacerbations (0, 1, 2, 3, \>/=4) was reported. An asthma exacerbation was defined as new or increased asthma symptoms which resulted in either hospitalization and/or treatment with systemic corticosteroids (or increase of stable maintenance dose) for \>/= 3 days.

Percentage of Participants by Number of Asthma Exacerbations Requiring Treatment With Systemic SteroidsMonths 1-12

Percentage of participants by number of asthma exacerbations (0, 1, 2, 3, \>/=4) requiring treatment with systemic steroids was reported. An asthma exacerbation was defined as new or increased asthma symptoms which resulted in either hospitalization and/or treatment with systemic corticosteroids (or increase of stable maintenance dose) for \>/= 3 days.

Change From Baseline in Raw Forced Expiratory Volume in One Second (FEV1)Baseline, Month 6, end of study (EOS)/early termination (ET) (up to Month 12)

FEV1 was defined as the volume of air that can be forced out in one second after taking a deep breath. Pre-bronchodilator FEV1 and post-bronchodilator FEV1 are reported for each timepoint. FEV1 was measured using spirometry.

Total Number of Asthma Exacerbations During Months 7-12Months 7-12

An asthma exacerbation was defined as new or increased asthma symptoms which resulted in either hospitalization and/or treatment with systemic corticosteroids (or increase of stable maintenance dose) for \>/= 3 days.

Total Number of Asthma-Related Hospital Admissions During Months 7-12Months 7-12
Total Number of Asthma-Related Telephone Calls to Healthcare Providers During Months 1-12Months 1-12
Total Number of Asthma-Related Telephone Calls to Healthcare Providers During Months 1-6Months 1-6
Total Number of Asthma-Related Telephone Calls to Healthcare Providers During Months 7-12Months 7-12
Total Number of Asthma-Related Hospital Admissions During Months 1-12Months 1-12
Total Number of Asthma-Related Hospital Admissions During Months 1-6Months 1-6
Change From Baseline in Work Productivity and Activity Impairment (WPAI) Asthma Questionnaire ScoreBaseline, Month 6, EOS/ET (up to Month 12)

WPAI-asthma is a self-administered instrument to measure asthma-specific performance impairment of work and regular daily activity within the last 7 days and yields 4 types of scores: work time missed (absenteeism), impairment while working (presenteeism or reduced on-the-job effectiveness), overall work impairment (WI) (work productivity loss or absenteeism plus presenteeism) and activity impairment (daily activity impairment). Total score and each score ranged from 0 (not affected/no impairment) to 100 (completely affected/impaired). Higher scores indicated greater impairment and less productivity. A negative change in score indicated improvement and a positive change indicated impairment.

Change From Baseline in Raw Forced Vital Capacity (FVC)Baseline, Month 6, EOS/ET (up to Month 12)

FVC was defined as the amount of air which can be forcibly exhaled from the lungs after taking the deepest breath possible. Pre-bronchodilator FVC and post-bronchodilator FVC are reported for each timepoint. FVC was measured using spirometry.

Change From Baseline in Raw Forced Expiratory Flow at 25-75 Percent (%) of Pulmonary Volume (FEF25%-75%)Baseline, Month 6, EOS/ET (up to Month 12)

FEF25%-75% was defined as the flow (or speed) of air coming out of the lung during the middle portion of a forced expiration. Pre-bronchodilator FEF25%-75% and post-bronchodilator FEF25%-75% are reported for each timepoint. FEF25%-75% was measured using spirometry.

Change From Baseline in Percentage Predicted FEV1 (ppFEV1)Baseline, Month 6, EOS/ET (up to Month 12)

FEV1 is the volume of air that can be forced out in one second after taking a deep breath, as measured using spirometry. Hankinson and Wang standards were used to calculate ppFEV1 (for age, gender, race, and height). The Hankinson standard was used for male participants 18 years and older and female participants 16 years and older. The Wang standard was used for male participants aged 12 to 17 years and for female participants aged 12 to 15 years. ppFEV1= 100 multiplied by (\*) FEV1 (in liters \[L\]) divided by (/) predicted FEV1 (in L). Pre-bronchodilator ppFEV1 and post-bronchodilator ppFEV1 are reported for each timepoint.

Percentage of Participants With Prior Asthma Medications by Category or Class of MedicationsBaseline

Prior asthma medications were defined as all medications used for asthma prior to the study (initiated within 90 days of baseline) and were assessed retrospectively at baseline. Participants received prior asthma medications of following categories or classes: short acting beta agonist (SABA), combination inhaled corticosteroids/long acting beta agonist (ICS/LABA), leukotriene receptor antagonist (LTRA), inhaled corticosteroids (ICS), oral/parenteral (systemic) corticosteroids, anticholinergic, long acting beta agonist (LABA), and other medication.

Percentage of Participants With Concomitant and Ongoing Asthma Medications by Category or Class of MedicationsBaseline until EOS/ET (up to Month 12)

Concomitant and ongoing asthma medications were defined as all medications used for asthma which began on or after the participant's study start, as well as those ongoing at the beginning of the study. Participants received following categories or classes of concomitant and ongoing asthma medications: SABA, combination ICS/LABA, LTRA, oral/parenteral (systemic) corticosteroids, ICS, anticholinergic, LABA, and other medication.

Change From Baseline in Asthma Quality of Life Questionnaire for 12 Years and Older (AQLQ +12) Overall ScoreBaseline, Month 6, EOS/ET (up to Month 12)

AQLQ +12 is a 32-item disease specific questionnaire designed to assess the participants' asthma-specific health-related quality of life (QOL). The questionnaire contains four domains: activity limitations (11 items), symptoms (12 items), emotional function (5 items), and environmental stimuli (4 items). All items are scored on a 7-point likert scale. All item scores are averaged to produce one overall QOL score. Overall score ranges from 1 (total impairment) to 7 (no impairment), with higher scores indicating better QOL. A positive change from baseline indicated improved QOL.

Change From Baseline in Mini Rhinoconjunctivitis Quality of Life Questionnaire (MiniRQLQ) Overall Quality of Life ScoreBaseline, EOS/ET (up to Month 12)

The MiniRQLQ is a shorter version of the Rhinoconjunctivitis Quality of Life Questionnaire (RQLQ) instrument. The MiniRQLQ is a validated quality of life questionnaire to measure the functional impairments that are most troublesome to adult participants with either seasonal or perennial rhinoconjunctivitis of either allergic or non-allergic origin. The miniRQLQ contains 14 items; each item scored on a 7-point scale ranging from 0 \[not impaired at all\] to 6 \[severely impaired\]). The overall quality of life score is the average of the all item scores and ranges from 0 (not impaired at all) to 6 (severely impaired), with higher scores indicating more impairment. A negative change in score indicated improvement and a positive change indicated impairment.

Change From Baseline in Asthma Control Test (ACT) Overall ScoreBaseline, Months 3, 6, 9, 12

Multidimensional factors associated with asthma control from the participant's perspective were assessed using the ACT questionnaire. The ACT is a validated, five-item patient-reported outcome (PRO) questionnaire that measures the impact of asthma on home and work activities, shortness of breath, symptoms, rescue medication usage, and overall asthma control. All items are scored on a 5-point likert scale (1 to 5). All item scores are added together to calculate a total score. Total score ranges from 5 (poor control of asthma) to 25 (complete control of asthma), with higher scores reflecting greater asthma control. A positive change from baseline indicated improvement.

Percentage of Participants Who Showed an Improvement in Asthma Symptoms Due to the Medication, Assessed Using Global Evaluation of Treatment Effectiveness (GETE) by InversigatorEOS/ET (up to Month 12)

Response to treatment was assessed using the GETE. The GETE is a validated instrument that measures the overall impression of the effect of the study medication on typical asthma symptoms. The evaluation was performed using the 5-point scale. The GETE scale ranges were as follows: 1=excellent, 2=good, 3=moderate, 4=poor, 5= worsening. A good or excellent response on the 5 point scale indicated that a participant had responded to treatment. Percentage of participants who showed an improvement (GETE scale score of 1 or 2) in asthma symptoms, as assessed by investigator, is reported.

Percentage of Participants Who Showed an Improvement in Asthma Symptoms Due to the Medication, Assessed Using GETE by ParticipantEOS/ET (up to Month 12)

Response to treatment was assessed using the GETE. The GETE is a validated instrument that measures the overall impression of the effect of the study medication on typical asthma symptoms. The evaluation was performed using the 5-point scale. The GETE scale ranges were as follows: 1=excellent, 2=good, 3=moderate, 4=poor, 5= worsening. A good or excellent response on the 5 point scale indicated that a participant had responded to treatment. Percentage of participants who showed an improvement (GETE scale score of 1 or 2) in asthma symptoms, as assessed by participant, is reported.

Trial Locations

Locations (143)

University of Rochester

🇺🇸

Rochester, New York, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Chest Medicine Consultants

🇺🇸

Chicago, Illinois, United States

Allergy & Clinical Immun Assoc

🇺🇸

Pittsburgh, Pennsylvania, United States

ASTHMA, Inc

🇺🇸

Seattle, Washington, United States

San Tan Allergy & Asthma

🇺🇸

Gilbert, Arizona, United States

Dedicated Clinical Research

🇺🇸

Goodyear, Arizona, United States

West Coast Clinical Trials Global, LLC

🇺🇸

Costa Mesa, California, United States

Allergy & Asth Phys of Cent KY

🇺🇸

Lexington, Kentucky, United States

Abraham Research PLLC

🇺🇸

Florence, Kentucky, United States

Chesapeake Clinical Research Inc - CRN

🇺🇸

Baltimore, Maryland, United States

North Bay Allergy & Asthma; Medical Assoc

🇺🇸

Napa, California, United States

Waterbury Pulmonary Associates

🇺🇸

Waterbury, Connecticut, United States

Dr. Paul Shapero

🇺🇸

Bangor, Maine, United States

Family Allergy & Asthma

🇺🇸

Gaithersburg, Maryland, United States

Gettysburg Medical Clinic

🇺🇸

Fresno, California, United States

Allergy Asthma & Sinus Center

🇺🇸

Greenfield, Wisconsin, United States

Georgia Pollens

🇺🇸

Albany, Georgia, United States

Brookstone Clinical Res Ctr

🇺🇸

Columbus, Georgia, United States

Asthma & Allergy of Idaho

🇺🇸

Twin Falls, Idaho, United States

Allergy Asthma Care

🇺🇸

Crown Point, Indiana, United States

VA Loma Linda Healthcare System

🇺🇸

Loma Linda, California, United States

Allergy & Asthma Inst Valley

🇺🇸

Granada Hills, California, United States

FL Ctr Allergy & Asthma Res

🇺🇸

Miami, Florida, United States

Allergy & Asthma Care Center

🇺🇸

Gainesville, Georgia, United States

Clinical Research Center of Indiana

🇺🇸

Indianapolis, Indiana, United States

University of Kansas Med Ctr; Int med/Allgy/Immun/Rheum

🇺🇸

Kansas City, Kansas, United States

William Ebbeling MD - PP

🇺🇸

Fresno, California, United States

Allergy & Asthma Care LTD

🇺🇸

Glen Carbon, Illinois, United States

Florida Ctr-Allergy & Asthma

🇺🇸

Miami, Florida, United States

Aeroallergy Research Labs

🇺🇸

Savannah, Georgia, United States

The Allergy and Asthma Center

🇺🇸

Fort Wayne, Indiana, United States

Allergy Asthma & Immun Center

🇺🇸

Leesburg, Florida, United States

Washington Univ. School of Med

🇺🇸

Saint Louis, Missouri, United States

Brigham and Women's Hospital

🇺🇸

Boston, Massachusetts, United States

Asthma Allergy Ctr of SW MI

🇺🇸

Portage, Michigan, United States

Bend Memorial Clinic

🇺🇸

Bend, Oregon, United States

LeBonheur Children's Hospital

🇺🇸

Memphis, Tennessee, United States

Allergy Asthma & Immun Assoc

🇺🇸

Garland, Texas, United States

Clinical Research Partners, LLC

🇺🇸

Henrico, Virginia, United States

Santiago Reyes MD-Private Prac

🇺🇸

Oklahoma City, Oklahoma, United States

Live Oak Allergy & Asthma Clinic

🇺🇸

San Antonio, Texas, United States

Allergy & Asthma Res Ctr PA

🇺🇸

San Antonio, Texas, United States

Allergy Assoc Medical Group

🇺🇸

San Diego, California, United States

Kaiser Permanente - San Diego

🇺🇸

San Diego, California, United States

Clinical Research Inst

🇺🇸

Minneapolis, Minnesota, United States

Impact Clinical Trials

🇺🇸

Las Vegas, Nevada, United States

University of California at San Francisco

🇺🇸

San Francisco, California, United States

Asthma & Allergy Clinic

🇺🇸

San Francisco, California, United States

Huntsville Lung Associates PC

🇺🇸

Huntsville, Alabama, United States

Achieve Clinical Research, LLC

🇺🇸

Birmingham, Alabama, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Allergy Associates of Tucson

🇺🇸

Tucson, Arizona, United States

Allergy & Asthma Care of FL; Clinical Research

🇺🇸

Ocala, Florida, United States

Sneeze Wheeze and Itch Associates LLC

🇺🇸

Normal, Illinois, United States

University of Arizona

🇺🇸

Tucson, Arizona, United States

Alabama Allergy & Asthma

🇺🇸

Birmingham, Alabama, United States

Stuart Epstein MD - PP

🇺🇸

Beverly Hills, California, United States

Peninsula Allergy Associates

🇺🇸

Daly City, California, United States

Allianz Medical and Research Center

🇺🇸

Fountain Valley, California, United States

Allergy Asthma Care Ctr, Inc.

🇺🇸

Los Angeles, California, United States

California Allergy & Asthma Medical Group, Inc.

🇺🇸

Palmdale, California, United States

Clinical Trials of Orange County

🇺🇸

Orange, California, United States

Choc Psf, Amc

🇺🇸

Orange, California, United States

Joann Blessing-Moore MD - PP

🇺🇸

Palo Alto, California, United States

Southern California Research Center

🇺🇸

Mission Viejo, California, United States

TPMG - Rancho Cordova

🇺🇸

Rancho Cordova, California, United States

Allergy & Asthma Consultants

🇺🇸

Redwood City, California, United States

Redding Allergy & Asthma Care

🇺🇸

Redding, California, United States

Central Coast Allergy and Asthma

🇺🇸

Salinas, California, United States

The Allergy and Asthma Clinic

🇺🇸

San Mateo, California, United States

Allergy & Asthma Medical Group; Clinical Research Division

🇺🇸

Walnut Creek, California, United States

Danbury Hospital

🇺🇸

Danbury, Connecticut, United States

IMMUNOe International Research Centers

🇺🇸

Centennial, Colorado, United States

Christopher C Randolph MD - PP

🇺🇸

Waterbury, Connecticut, United States

AAADRS; Clinical Research Center

🇺🇸

Coral Gables, Florida, United States

St. Francis Sleep; Allergy & Lung Institute

🇺🇸

Clearwater, Florida, United States

Gulf Coast Allergy Center, P.A.

🇺🇸

Port Charlotte, Florida, United States

Kansas City Allergy And Asthma Assoc.

🇺🇸

Overland Park, Kansas, United States

Glenn M. Silber, M.D., P.A

🇺🇸

Ellicott City, Maryland, United States

Center for Clinical Research.

🇺🇸

Brockton, Massachusetts, United States

Allergy Arth Fam Treatment Ctr

🇺🇸

Gardner, Massachusetts, United States

Infinity Medical Research Inc

🇺🇸

North Dartmouth, Massachusetts, United States

Asthma & Allergy Inst of MI

🇺🇸

Clinton Township, Michigan, United States

McGovern & Baja Allergy Assoc

🇺🇸

Springfield, Massachusetts, United States

Ocean Allergy & Resp Res Ctr

🇺🇸

Brick Township, New Jersey, United States

Adult Ped Aller Central Jersey

🇺🇸

Edison, New Jersey, United States

Center for Asthma and Allergy

🇺🇸

Highland Park, New Jersey, United States

Atlantic Allergy Asthma Immunology Associates

🇺🇸

Ocean City, New Jersey, United States

Allergy Treatment Center of New Jersey

🇺🇸

Piscataway, New Jersey, United States

Pulmonary and Allergy Associates

🇺🇸

Summit, New Jersey, United States

SUNY Downstate Medical Center.

🇺🇸

Brooklyn, New York, United States

Boris Sagalovich MD - PC

🇺🇸

Brooklyn, New York, United States

Allergy Consultants, PA

🇺🇸

Verona, New Jersey, United States

Island Medical Research Pc

🇺🇸

Commack, New York, United States

North Shore Medical Arts, LLP

🇺🇸

Great Neck, New York, United States

Jamaica Hospital Medical Center

🇺🇸

Jamaica, New York, United States

Laura and ISAAC Perlmutter Cancer Center at NYU Langone.

🇺🇸

New York, New York, United States

Winthrop Univ Hospital

🇺🇸

Mineola, New York, United States

Parikh Institute for Research LLC

🇺🇸

New York, New York, United States

Olean Medical Group

🇺🇸

Olean, New York, United States

Albert P Hirdt DO - PP

🇺🇸

Newburgh, New York, United States

Urban Health Plan, Inc.

🇺🇸

The Bronx, New York, United States

Advanced Allergy & Asthma PLLC

🇺🇸

Rockville Center, New York, United States

Alan Kaufman MD - PP

🇺🇸

The Bronx, New York, United States

Allergy & Asthma Centre of Dayton

🇺🇸

Centerville, Ohio, United States

Allergy Partners of Western NC

🇺🇸

Asheville, North Carolina, United States

The Cleveland Clinic Foundation

🇺🇸

Cleveland, Ohio, United States

Vital Prospects Clin Res Pc

🇺🇸

Tulsa, Oklahoma, United States

Central PA Asth & Allergy Care; Research Division

🇺🇸

Altoona, Pennsylvania, United States

Allergy and Asthmas; Specialists of Harrisburg

🇺🇸

Harrisburg, Pennsylvania, United States

Allergy and Asthma Research of NJ, lnc

🇺🇸

Philadelphia, Pennsylvania, United States

Penn State Hershey Medical Group

🇺🇸

Hershey, Pennsylvania, United States

Inst for Resp & Sleep Med PC

🇺🇸

Langhorne, Pennsylvania, United States

South Hills Pulmonary Assoc

🇺🇸

Pittsburgh, Pennsylvania, United States

ADAC Research PA

🇺🇸

Greenville, South Carolina, United States

Upstate Pharma Research

🇺🇸

Simpsonville, South Carolina, United States

East Tennessee Center for Clinical Research

🇺🇸

Knoxville, Tennessee, United States

Respiratory Specialists

🇺🇸

Reading, Pennsylvania, United States

Vanderbilt Medical University

🇺🇸

Nashville, Tennessee, United States

Elliot J. Ginchansky, MD, PA

🇺🇸

Dallas, Texas, United States

Greater Austin Allergy Asthma and Immunology

🇺🇸

Austin, Texas, United States

Allergy Asthma Research Assoc

🇺🇸

Dallas, Texas, United States

University of Texas Medical Branch;Division of APICS

🇺🇸

Galveston, Texas, United States

Sugar Land Allerg Asthma Immun

🇺🇸

Sugar Land, Texas, United States

University of Texas Health Center at Tyler

🇺🇸

Tyler, Texas, United States

Bridgerland Clinical Research

🇺🇸

North Logan, Utah, United States

Allergy Associates of Utah

🇺🇸

Murray, Utah, United States

Pulmonary Research of Albingdon

🇺🇸

Abingdon, Virginia, United States

O & O Alpan, LLC

🇺🇸

Fairfax, Virginia, United States

Children's Hospital of the King's Daughter

🇺🇸

Norfolk, Virginia, United States

Bellingham Asthma, Allergy & Immunology

🇺🇸

Bellingham, Washington, United States

Pulmonary & Sleep Research

🇺🇸

Spokane, Washington, United States

Northwest Asthma Allergy Center

🇺🇸

Vancouver, Washington, United States

Dean Clinic

🇺🇸

Madison, Wisconsin, United States

University of Wisconsin;Allergy & Asthma Clinical Research

🇺🇸

Madison, Wisconsin, United States

USF Asthma Allergy & Immun; Clinical Research

🇺🇸

Tampa, Florida, United States

Central Florida Pulmonary Grou

🇺🇸

Orlando, Florida, United States

Capital Allergy Resp Dis Ctr

🇺🇸

Sacramento, California, United States

Nat'l Aller Asth-Charleston

🇺🇸

Charleston, South Carolina, United States

Little Rock Allergy & Asthma; Clinical Research Center

🇺🇸

Little Rock, Arkansas, United States

Montefiore Medical Center

🇺🇸

The Bronx, New York, United States

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