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A Study Of PF-05212384 Plus Irinotecan Vs Cetuximab Plus Irinotecan In Patients With KRAS And NRAS Wild Type Metastatic Colorectal Cancer

Phase 2
Terminated
Conditions
Metastatic Colorectal Cancer
Interventions
Registration Number
NCT01925274
Lead Sponsor
Pfizer
Brief Summary

This study will investigate whether the combination of PF-05212384 plus Irinotecan improves progression free survival in patients with KRAS and NRAS wild type metastatic colorectal cancer when compared with the combination of cetuximab plus Irinotecan. A Japanese Lead in Cohort will assess the safety of the combination of PF-05212384 + irinotecan in patients enrolled at Japanese sites.

Detailed Description

Not available

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
19
Inclusion Criteria
  • KRAS and NRAS wild type metastatic colorectal cancer
  • Progression following treatment for colorectal cancer with irinotecan, oxaliplatin and fluoropyrimidine therapy in the metastatic setting.
  • Eastern Cooperative Oncology Group [ECOG] Performance Status of 0, 1, or 2
  • At least one measurable lesion by Response Evaluation Criterion in Solid Tumors [RECIST]
Exclusion Criteria
  • More than 2 prior cytotoxic chemotherapy regimens for metastatic colorectal cancer.
  • Prior treatment with a PI3K, mTOR, AKT or EGFR inhibitor
  • Patients who have discontinued treatment with prior irinotecan therapy due to toxicity.
  • Prior radiation to the pelvis or abdomen
  • Patients with history of interstitial lung disease.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arm APF-05212384PF-05212384 plus Irinotecan
Arm BIrinotecanCetuximab plus Irinotecan
Arm AIrinotecanPF-05212384 plus Irinotecan
Arm BCetuximabCetuximab plus Irinotecan
Primary Outcome Measures
NameTimeMethod
Progression Free Survival (PFS) as Assessed by InvestigatorsFrom date of first dose until the date of first documented progression or date of death from any cause, whichever came first, assessed up to 2 years

Progression-free survival (PFS) was the time from the first dose of study treatment to the first documentation of objective tumor progression or death due to any cause, whichever occurred first. Objective progression was defined as 20% increase in the sum of diameters of target measurable lesions above the smallest sum observed (over baseline if no decrease in the sum was observed during therapy), with a minimum absolute increase of 5 mm. Median PFS was estimated based on the Kaplan-Meier method.

Secondary Outcome Measures
NameTimeMethod
Overall Survival (OS)2 years

Overall survival (OS) was defined as the duration from enrollment to death. Participants last known to be alive were censored at date of last contact.

Number of Participants With ECG Maximum Increase From Baseline Meeting Pre-defined Criteria2 years

The number of participants with ECG maximum increase from baseline meeting the following criteria was reported:

Criterion A: maximum QTc interval increase from baseline \>30 msec and ≤60 msec; criterion B: maximum QTc interval increase from baseline \>60 msec; criterion C: maximum QTcB interval increase from baseline \>30 msec and ≤60 msec; criterion D: maximum QTcB interval increase from baseline \>60 msec; criterion E: maximum QTcF interval increase from baseline \>30 msec and ≤60 msec; criterion F: maximum QTcF interval increase from baseline \>60 msec.

Maximum Plasma Concentration (Cmax) of SN-38Pre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

SN-38 is an irinotecan metabolite. Cmax of SN-38 was observed directly from data.

Area Under Plasma Concentration Time Profile From Time Zero to the Time for the Last Quantifiable Concentration (AUClast) of IrinotecanPre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

AUClast refers to the area under plasma concentration time profile from time zero to the time for the last quantifiable concentration. AUClast of irinotecan was determined using linear/log trapezoidal method.

Area Under Plasma Concentration Time Profile From Time Zero Extrapolated to Infinite Time (AUCinf) of PF-05212384Pre-dose (0 hour), 0.5, 1, 2, 4, 6, 24, 72, 120 hours post PF-05212384 infusion on Cycle 1 Day 9.

AUCinf refers to the area under plasma concentration time profile from time zero extrapolated to infinite time. AUCinf of PF-05212384 was calculated using the formula: AUCinf = AUClast + (Clast\*/kel), where Clast\* was the predicted plasma concentration at the last quantifiable time point estimated from the log-linear regression analysis.

Number of Participants With Laboratory Test (Hematology) Abnormalities2 years

The following hematology parameters were evaluated in this study: hemoglobin, white blood cells (WBC) with differential, and platelets.

Maximum Plasma Concentration (Cmax) of PF-05212384Pre-dose (0 hour), 0.5, 1, 2, 4, 6, 24, 72, 120 hours post PF-05212384 infusion on Cycle 1 Day 9 and Cycle 1 Day 16.

Cmax of PF-05212384 was observed directly from data.

Time for Maximum Plasma Concentration (Tmax) of SN-38Pre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

SN-38 is an irinotecan metabolite. Tmax of SN-38 was observed directly from data as time of first occurrence.

Terminal Elimination Half Life (t½) of IrinotecanPre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

T½ was calculated as loge(2)/kel, where kel was the terminal phase rate constant calculated by a linear regression of the log-linear concentration-time curve. Only those data points judged to describe the terminal log-linear decline were used in the regression.

Percentage of Participants With Objective Response2 years

Percentage of participants with objective response was based on assessment of confirmed complete response (CR) or confirmed partial response (PR) according to Response Evaluation Criteria In Solid Tumors (RECIST), version 1.1. Confirmed PR was defined as disappearance of all target lesions. Confirmed PR was defined as \>=30% decrease in sum of the longest dimensions of the target lesions taking the baseline sum as a reference. Confirmed responses were those that persisted on repeat imaging study \>=4 weeks after initial documentation of response.

Number of Participants With Treatment-Emergent Adverse Events (AEs) or Serious Adverse Events (SAEs)Administration of the first dose of study drug through 28 calendar days after the last administration of study drug

An AE was defined as any untoward medical occurrence in a clinical investigation participant administered a product or medical device; the event need not necessarily have a causal relationship with the treatment or usage. An SAE was defined as any untoward occurrence at any dose that resulted in death; was life threatening (immediate risk of death); required inpatient hospitalization or prolongation of existing hospitalization; resulted in persistent or significant disability/incapacity (substantial disruption of the ability to conduct normal life functions); resulted in congenital anomaly/birth defect. AEs included both serious and non-serious AEs. Treatment-emergent AEs were those with initial onset or increasing in severity after the first dose of study drug.

Duration of Response2 years

For participants with an objective response (CR or PR), duration of response was defined as the time from first documentation of CR or PR to date of first documentation of objective progression or death. Date of first documentation of progression and date of first documentation of CR or PR were based on Investigator's assessment of response.

Number of Participants With Laboratory Test (Chemistry) Abnormalities2 years

The following chemistry parameters were evaluated in this study: sodium, potassium, magnesium, chloride, aspartate aminotransferase (AST), alanine aminotransferase (ALT), alkaline phosphatase, total bilirubin, albumin, blood urea nitrogen (BUN) or urea, creatinine, total calcium, glycosylated hemoglobin (HbA1c), glucose, uric acid, phosphorus or phosphate, insulin, and C-peptide.

Number of Participants With Laboratory Test (Coagulation) Abnormalities2 years

Coagulation analysis included partial thromboplastin time (PTT) and international normalized ratio (INR) or prothrombin time (PT).

Area Under Plasma Concentration Time Profile From Time Zero to the Time for the Last Quantifiable Concentration (AUClast) of SN-38Pre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

AUClast refers to the area under plasma concentration time profile from time zero to the time for the last quantifiable concentration. AUClast of SN-38 (an irinotecan metabolite) was determined using linear/log trapezoidal method.

Area Under Plasma Concentration Time Profile From Time Zero Extrapolated to Infinite Time (AUCinf) of SN-38Pre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

AUCinf refers to the area under plasma concentration time profile from time zero extrapolated to infinite time. AUCinf of SN-38 (an irinotecan metabolite) was calculated using the formula: AUCinf = AUClast + (Clast\*/kel), where Clast\* was the predicted plasma concentration at the last quantifiable time point estimated from the log-linear regression analysis.

Change From Baseline in Functional Assessment of Cancer Therapy-Colorectal (FACT-C)2 years

Functional Assessment of Cancer Therapy-Colorectal (FACT-C) was used in this study to assess Health-Related Quality of Life (HRQoL) and CRC-related symptoms in participants enrolled to the randomized portion of the study. The FACT-C is part of the Functional Assessment of Chronic Illness Therapy (FACIT) measurement system, a comprehensive and extensive set of self-reported instruments for the assessment of health-related quality of life in participants with cancer or other chronic illnesses.

Number of Participants With Unacceptable Toxicity in Cycle 1 (Japanese LIC Only)28 days

Unacceptable toxicity (according to Common Terminology Criteria for Adverse Events \[CTCAE\], Version 4.0) was any of the following occurrences: (1) Grade 4 neutropenia \>7 days, or febrile neutropenia, or Grade 4 thrombocytopenia; (2) Grade \>=3 nausea/vomiting despite optimal antiemetic treatment, or Grade \>=3 diarrhea despite optimal anti diarrheal treatment; (3) unmanageable Grade \>=3 hyperglycemia; (4) mean QTc interval (time from electrocardiogram \[ECG\] Q wave to the end of the T wave corresponding to electrical systole, corrected for heart rate) \>501 msec in triplicate 12-lead ECG, or myocardial infarction, or ventricular arrhythmia; (5) Grade \>=3 non-hematologic toxicity; (6) treatment delay of \>=2 weeks due to study drug related toxicity; (7) persistent, intolerable toxicities which resulted in failure to deliver at least 75% of doses of both PF-05212384 and irinotecan during Cycle 1; (8) Grade \>=2 respiratory toxicities.

Number of Participants With Treatment-Emergent Adverse Events (TEAEs) by Common Terminology Criteria for Adverse Events (CTCAE) GradeAdministration of the first dose of study drug through 28 calendar days after the last administration of study drug

TEAEs were those AEs with initial onset or increasing in severity after the first dose of study drug. CTCAE version 4.0 was used to grade the severity of TEAEs. Grade 1 referred to mild AEs; Grade 2 referred to moderate AEs; Grade 3 referred to severe AEs; Grade 4 referred to AEs with life-threatening consequences, and urgent intervention was needed to manage them; Grade 5 referred to death related to AE.

Number of Participants With Laboratory Test (Urinalysis) Abnormalities2 years

Urinalysis included urine dipstick for protein and blood: if positive, perform a microscopic analysis. Number of participants with urine protein tested positive is presented.

Number of Participants With ECG Post-Baseline Maximum Absolute Values Meeting Pre-defined Criteria2 years

The number of participants with ECG post-baseline maximum absolute values meeting the following criteria was reported: (1) maximum QTc interval ranged from 450 to 480 msec; \>480-500 msec; \>500 msec; (2) maximum QTcB (QT corrected for heart rate using Bazett's formula) interval ranged from 450 to 480 msec; \>480-500 msec; \>500 msec; (3) maximum QTcF (QT corrected for heart rate using Fridericia's formula) interval ranged from 450 to 480 msec; \>480-500 msec; \>500 msec.

Maximum Plasma Concentration (Cmax) of IrinotecanPre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

Cmax of irinotecan was observed directly from data.

Time for Maximum Plasma Concentration (Tmax) of PF-05212384Pre-dose (0 hour), 0.5, 1, 2, 4, 6, 24, 72, 120 hours post PF-05212384 infusion on Cycle 1 Day 9 and Cycle 1 Day 16.

Tmax of PF-05212384 was observed directly from data as time of first occurrence.

Time for Maximum Plasma Concentration (Tmax) of IrinotecanPre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

Tmax of irinotecan was observed directly from data as time of first occurrence.

Area Under Plasma Concentration Time Profile From Time Zero to the Time for the Last Quantifiable Concentration (AUClast) of PF-05212384Pre-dose (0 hour), 0.5, 1, 2, 4, 6, 24, 72, 120 hours post PF-05212384 infusion on Cycle 1 Day 9.

AUClast refers to the area under plasma concentration time profile from time zero to the time for the last quantifiable concentration. AUClast of PF-05212384 was determined using linear/log trapezoidal method.

Terminal Elimination Half Life (t½) of PF-05212384Pre-dose (0 hour), 0.5, 1, 2, 4, 6, 24, 72, 120 hours post PF-05212384 infusion on Cycle 1 Day 9 and Cycle 1 Day 16.

T½ was calculated as loge(2)/kel, where kel was the terminal phase rate constant calculated by a linear regression of the log-linear concentration-time curve. Only those data points judged to describe the terminal log-linear decline were used in the regression.

Area Under Plasma Concentration Time Profile From Time Zero Extrapolated to Infinite Time (AUCinf) of IrinotecanPre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

AUCinf refers to the area under plasma concentration time profile from time zero extrapolated to infinite time. AUCinf of irinotecan was calculated using the formula: AUCinf = AUClast + (Clast\*/kel), where Clast\* was the predicted plasma concentration at the last quantifiable time point estimated from the log-linear regression analysis.

Terminal Elimination Half Life (t½) of SN-38Pre-dose (0 hour), 1.5, 2, 4, 6 and 24 hours post irinotecan infusion on Cycle 1 Day 1 and Cycle 2 Day 1.

T½ was calculated as loge(2)/kel, where kel was the terminal phase rate constant calculated by a linear regression of the log-linear concentration-time curve. Only those data points judged to describe the terminal log-linear decline were used in the regression.

Levels of Signaling Proteins in Paired and Single Tumor Biopsies2 years

Pre defined signaling proteins included Akt (protein kinase B), p-Akt (phosphorylated Akt), p-S6 (phosphorylated ribosomal protein S6), p-Met (phosphorylated Met, a receptor tyrosine kinase), p-mTOR (phosphorylated mammalian target of rapamycin), EGFR (epithelial growth factor receptor), and p-EGFR (phosphorylated EGFR).

Number of Participants With Expression of Pre-defined Gene Sequences in Biopsied Tumor Tissues2 years

Pre-defined gene sequences were those related to EGFR, PI3K (phosphoinositide-3 kinase) and other oncogenic pathways; examples included but were not limited to PIK3CA (this gene encodes the catalytic subunit of PI3K), PIK3R1 (this gene encodes the regulatory subunit of PI3K), KRAS, NRAS and BRAF (this gene encodes serine/threonine-protein kinase B-Raf) sequences and PIK3CA gene amplification. Due to early termination of this study, these pre-defined gene sequences were not analyzed, except for KRAS and NRAS. Number of participants who had KRAS and NRAS wild type status confirmed by the central laboratory is presented.

Trial Locations

Locations (28)

Kadlec Clinic Hematology and Oncology

🇺🇸

Kennewick, Washington, United States

Siteman Cancer Center - St Peters

🇺🇸

Saint Peters, Missouri, United States

Kadlec Medical Center

🇺🇸

Richland, Washington, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

CBCC Global Research, Inc. at Comprehensive Blood and Cancer Center

🇺🇸

Bakersfield, California, United States

TRIO_US

🇺🇸

Los Angeles, California, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Siteman Cancer Center - South County

🇺🇸

Saint Louis, Missouri, United States

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Barnes-Jewish Hospital

🇺🇸

Saint Louis, Missouri, United States

Outpatient Imaging Center

🇺🇸

Richland, Washington, United States

Hospital General Universitario Gregorio Marañón

🇪🇸

Madrid, Spain

West Valley Hematology/Oncology Med Group

🇺🇸

Northridge, California, United States

National Cancer Center

🇰🇷

Goyang-si, Gyeonggi-do, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Drug Management Only: UCLA West Medical Pharmacy, Att: Steven L Wong, Pharm D

🇺🇸

Los Angeles, California, United States

TRIO-US Central Administration (Regulatory Management only)

🇺🇸

Los Angeles, California, United States

Regulatory Management Only: TRIO-US Central Administration

🇺🇸

Los Angeles, California, United States

Drug Management Only: UCLA West Medical Pharmacy

🇺🇸

Los Angeles, California, United States

UCLA West Medical Pharmacy

🇺🇸

Los Angeles, California, United States

Siteman Cancer Center - West County

🇺🇸

Creve Coeur, Missouri, United States

Seoul National University Hospital / Department of Internal Medicine

🇰🇷

Seoul, Korea, Republic of

Spokane Valley Cancer Center

🇺🇸

Spokane Valley, Washington, United States

Regulatory Office: Comprehensive Cancer Centers of Nevada

🇺🇸

Henderson, Nevada, United States

Comprehensive Cancer Centers of Nevada

🇺🇸

Las Vegas, Nevada, United States

National Cancer Center Hospital East

🇯🇵

Kashiwa, Chiba, Japan

Aichi cancer center central hospital

🇯🇵

Nagoya, Aichi, Japan

Medical Oncology Associates, PS

🇺🇸

Spokane, Washington, United States

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