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Study of a Prothrombin Complex Concentrate for Rapid Reversal of Coagulopathy Induced by Vitamin K Antagonists in Japanese Subjects

Phase 3
Completed
Conditions
Acute Major Bleeding
Reversal of Coagulopathy
Interventions
Biological: BE1116 (Prothrombin Complex Concentrate)
Registration Number
NCT02281201
Lead Sponsor
CSL Behring
Brief Summary

The purpose of this study is to evaluate efficacy and safety of a Prothrombin Complex Concentrate (PCC), BE1116. BE1116 will be used for the rapid reversal of coagulopathy induced by vitamin K antagonists in Japanese subjects who require immediate correction of international normalized ratio (INR) due to a major bleed or emergency surgery.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
11
Inclusion Criteria
  • Male and female Japanese subjects greater than or equal to 20 years
  • Subjects currently on vitamin K antagonist (VKA) therapy
  • INR greater than or equal to 2 within 3 hours before start of BE1116 infusion
  • Urgent reversal of VKA therapy for a surgical or invasive medical procedure is required within 24 hours of the start of BE1116 infusion, or presentation with an acute major bleed
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Exclusion Criteria
  • Subjects for whom administration of I.V. vitamin K and VKA withdrawal, alone, can adequately correct the subject's coagulopathy before the infusion of BE1116

  • Subjects in whom lowering the INR to within the normal range is not a treatment goal

  • Use of anticoagulants other than VKAs (or expected use within 1 day)

  • Medical history for which PCCs are contraindicated

  • History of thromboembolic event within 3 months of screening

  • Congenital or acquired abnormality of hemostasis other than receipt of VKAs

  • Administration of whole blood, plasma, plasma fractions, or platelets within 2 weeks prior to the start of BE1116 infusion

  • For subjects with intracranial hemorrhage (ICH):

    • Glasgow Coma Score (GCS) < 7
    • Intracerebral hematoma volume > 30 cm3 as assessed by computed tomography (CT) scan
    • For subdural hematomas: maximum thickness ≥ 10 mm, midline shift ≥ 5 mm, or acute subdural hematomas (based on neurosurgeon review)
    • For subarachnoid hemorrhage: any evidence of hydrocephalus, or Hunt and Hess Scale > 2, or concomitant subdural hematoma
    • Infratentorial ICH location
    • Epidural hematomas
    • Intraventricular rupture of hemorrhage
    • Requires surgical intervention
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
BE1116BE1116 (Prothrombin Complex Concentrate)Single intravenous (I.V.) infusion, dosage depending on baseline INR and body weight
Primary Outcome Measures
NameTimeMethod
Percentage of Subjects With a Rapid Reversal of VKA EffectAt baseline and at 30 minutes after the end of infusion

A rapid reversal of (Vitamin K antagonist) VKA effect is a reduction of the INR to ≤ 1.3 at 30 minutes after the end of infusion.

Secondary Outcome Measures
NameTimeMethod
45-Day All-cause MortalityUntil Day 45
Overall Treatment-emergent Adverse Events (TEAEs)From the start of infusion up to the allowed time window of the Day 14 visit for non-serious AEs and from the start of infusion up to the allowed time window of the Day 45 visit for SAEs

Number of participants with TEAEs. TEAEs are defined as adverse events that developed or worsened following exposure to investigational medicinal product. Serious TEAEs are treatment-emergent serious adverse events (SAEs).

Mean Predicted and Actual Blood Loss (mls) for all Surgical/Invasive ProceduresFrom the start of surgery/procedure until the end of surgery/procedure
Mean Time (mins) Between Last Suture and Cessation of Wound Drainage for all Surgical/Invasive ProcedureFrom the time of last suture until the end of wound drainage, up to the final safety follow-up visit (Day 45)
Viral serologyAt baseline and until Day 45

Percentage of participants with negative viral serology (for Human immunodeficiency virus, Hepatitis B, Hepatitis A, Hepatitis C and Parvovirus B19) before infusion who become positive after infusion.

Mean modified Rankin Scale for all subjects with intracranial haemorrhageBefore infusion and at Day 45
Increase in Plasma Levels of Factor (F)II, FVII, FIX, and FX, and Protein C and Protein SBefore infusion and up to 3 h after the start of infusion

The increase in plasma levels is assessed through response and in vivo recovery (IVR) of FII, FVII, FIX, FX, and protein C and protein S. The incremental IVR \[(IU/dL)/(IU/kg)\] is calculated as follows: (IU/dL activity rise in plasma)/(IU/kg body weight infused) = \[maximum increase in component plasma level within 3 hours compared to pre-infusion (IU/dL)\]/{\[exact dose of component in drug administered (IU)\]/\[body weight (kg)\]}.

Percentage of Subjects Who Receive Red Blood CellsFrom the start of infusion until 24 h after the start of infusion

Red blood cells are packed red blood cells (PRBCs).

Vital signsAt baseline and until 24 hours after the end of infusion

Percentage of participants with a clinically significant change in vital signs (including blood pressure, respiratory rate, temperature and pulse rate)

Percentage of Subjects Who Receive Other Blood Products and Hemostatic AgentsFrom the start of infusion until 24 h after the start of infusion

Other blood products and hemostatic agents containing coagulation factors (such as whole blood, plasma, albumin, platelets) not including PRBCs.

Percentage of Subjects Achieving Hemostatic Efficacy During SurgeryFrom the start of surgery/procedure until the end of surgery/procedure

Hemostatic efficacy is the binary endpoint of effective or non-effective hemostasis, where 'effective' is a hemostatic efficacy rating of "very good" or "satisfactory", and 'non-effective' is a hemostatic efficacy rating of "questionable" or "none".

Percentage of Subjects Achieving Hemostatic Efficacy of Stopping an Ongoing Major BleedBaseline CT scan, baseline haematology or the end of infusion, until 24 hours after the end of infusion

Hemostatic efficacy is the binary endpoint of effective or non-effective hemostasis, where 'effective' is a hemostatic efficacy rating of "excellent" or "good," and 'non-effective' is a hemostatic efficacy rating of "poor/none".

Percentage of Subjects With INR CorrectionFrom the start of infusion until INR correction, up to 24 hours after the end of infusion

The time taken from the start of infusion to INR correction (defined as an INR ≤ 1.3) is recorded. The percentage of participants with INR correction is calculated.

Percentage of Subjects With INR Correction at Various Times After the End of InfusionFrom the end of infusion until INR correction; calculated at 0.5, 1, 3, 6, 12, and 24 h after the end of infusion

The time taken from the end of infusion to INR correction (defined as an INR ≤ 1.3) is recorded. The percentage of participants with INR correction at 0.5, 1, 3, 6, 12, and 24 h after the end of infusion is calculated.

Mean Volume (mls) of Wound Drainage for all Surgical/Invasive ProceduresFrom the start of wound drainage until the end of wound drainage, up to the final safety follow-up visit (Day 45)

Trial Locations

Locations (11)

Nippon Medical School Hospital

🇯🇵

Sendagi, Bunkyo, Japan

Tohoku University Hospital

🇯🇵

Aoba-ku, Sendai, Japan

Kurashiki Central Hospital

🇯🇵

Miwa, Kurashiki, Japan

Kinki University

🇯🇵

Higashiosaka, Osaka, Japan

National Cerebral and Cardiovascular Center

🇯🇵

Suita, Osaka, Japan

Nippon Medical School Chiba Hokusoh Hospital

🇯🇵

Kamagari, Inzai, Japan

Kyushu Medical Center

🇯🇵

Chuo-ku, Fukuoka, Japan

Osaka National Hospital

🇯🇵

Chuo-ku, Osaka, Japan

Osaka University Hospital

🇯🇵

Yamadaoka, Suita, Japan

National Center for Global Health and Medicine

🇯🇵

Toyama, Shinjuku, Japan

St. Luke's International Hospital

🇯🇵

Chuo, Tokyo, Japan

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