MedPath

BBR 2778 for Relapsed, Aggressive Non-Hodgkin's Lymphoma (NHL)

Phase 3
Completed
Conditions
Lymphoma, Non-Hodgkin
Interventions
Drug: pixantrone, cyclophosphamide, vincristine, rituximab, prednisone
Drug: Vinorelbine, Oxalplatin, Ifosfasmide, Etoposide, Mitoxatrone, Gemcitabine or Rituximab
Registration Number
NCT00088530
Lead Sponsor
CTI BioPharma
Brief Summary

BBR 2778 is a novel aza-anthracenedione that has activity in experimental tumors and shows reduced potential for cardiotoxicity in animal models. This cytotoxic agent has structural similarities with mitoxantrone as well as general similarities with anthracyclines (such as the tricyclic central quinoid chromophore).

Detailed Description

The primary study objective is to compare the efficacy of BBR 2778 to a selection of single agents. Secondary objectives are to compare the safety and tolerability of BBR 2778 to a selection of single agents, and to assess the pharmacokinetic parameters of BBR 2778 in a subset of this patient population.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
140
Inclusion Criteria
  • Histologically confirmed aggressive [de novo or transformed] NHL according to REAL/WHO classification.
  • At least one objectively measurable lesion as demonstrated by CT, spiral CT, or MRI and plain radiograph of the chest (chest x-ray, for chest lesions only) that can be followed for response as target lesion.
  • Relapse after 2 or more prior regimens of chemotherapy
  • ECOG performance status of 0, 1, or 2
  • Adequate hematologic, renal and hepatic function
  • LVEF ≥50% determined by MUGA scan
Exclusion Criteria
  • Prior treatment with a cumulative dose of doxorubicin or equivalent exceeding 450 mg/m²
  • Prior allogenic stem cell transplant
  • Histological diagnosis of Burkitt lymphoma, lymphoblastic lymphoma or Mantle cell lymphoma
  • Active CNS lymphoma or HIV-related lymphoma.
  • Any chemotherapy, radiotherapy, or other anticancer treatment (including corticosteroid, 10 or more mg/day of prednisone or equivalent) within the 2 weeks before randomization
  • Pregnant women or nursing mothers

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Experimental Armpixantrone, cyclophosphamide, vincristine, rituximab, prednisonePixantrone (BBR2778)
Comparator ArmVinorelbine, Oxalplatin, Ifosfasmide, Etoposide, Mitoxatrone, Gemcitabine or RituximabTo be chosen by the investigator, among vinorelbine, oxaliplatin, ifosfamide, etoposide or mitoxantrone
Primary Outcome Measures
NameTimeMethod
Complete Response (CR) and Complete Response Unconfirmed (CRu)EOT; approximately 6 months

Proportion of patients with a best response of complete response (CR) or Complete Response unconfirmed (CRu) in the End Of Treatment (EOT) or End Of Study (EOS) analyses by independent assessment in the Intent-to-treat (ITT) population through the End of Treatment (EOT)

Secondary Outcome Measures
NameTimeMethod
Progression-Free Survival (PFS)18 months after 6 cycles of treatment; approximately 24 months

The time between the date of randomization and the date of the initial documentation of progressive/relapsed disease or death due to any cause.

Overall Survival18 months after 6 cycles of treatment; approximately 24 months

The time between the date of randomization and the date of death due to any cause.

Overall Response Rate (ORR) Lasting at Least 4 Monthsapproximately 24 months

The proportion of patients with Complete response or Partial Response with a difference from the first documented objective response to disease progression or death of at least 4 months.

Trial Locations

Locations (99)

Hospital Solca Quito

🇪🇨

Quito, Ecuador

Institute Bergonie

🇫🇷

Bordeaux, France

Charite, Campus Benjamin Franklin

🇩🇪

Berlin, Germany

FUNDALEU - fundacion para combatir le Leucernia

🇦🇷

Buenos Aires, Argentina

State Institution: Hematological Research Center under the Russian Academy of Medical Sciences

🇷🇺

Moscow, Russian Federation

State Medical Institution

🇷🇺

Irkutsk, Russian Federation

Staedtische Kliniken Hoechst

🇩🇪

Frankfurt, HE, Germany

Bekes Megyei Pandy Kalman Korhaz

🇭🇺

Gyula, Hungary

Ospedale Oncologico "A. Businco"

🇮🇹

Cagliari, Italy

Kliniken Maria Hilf GmbH

🇩🇪

Moenchengladbach, Germany

Institute of Clinical Radiology of the Research Center for Radiation Medicine under the UAMS

🇺🇦

Kyiv, Ukraine

Clinica Modelo S.A.

🇦🇷

Parana, Entre Rios, Argentina

State Medical Institution: Clinical Oncological Center

🇷🇺

Krasnodar, Russian Federation

Centre Hospitalier Lyo Sud, Service d'Hematologie et d'Oncologie

🇫🇷

Pierre-Benite, France

State Medical Institution Altai Territorial Oncological Center

🇷🇺

Barnaul, Russian Federation

Ospedale S. Eugenio

🇮🇹

Roma, Italy

Colentina Clinical Hospital Hem Dept

🇷🇴

Bucharest, Romania

Prof. Dr. Ian Chiricuta, Institute of Oncology, Radiotheraphy

🇷🇴

Cluj Napoca, Romania

State Research Institution: Research Institute of Oncology

🇷🇺

St. Petersburg, Russian Federation

Weston Park Hospital

🇬🇧

Sheffield, United Kingdom

Zhtomyr O.F. Gerbachevsky Regional Hospital

🇺🇦

Zhytomyr, Ukraine

Medical Radiological Research Center under the Russian academey of Medical Sciences

🇷🇺

Obninsk, Russian Federation

Petz Aladar Megyei Okato Korhaz

🇭🇺

Gyor, Hungary

Azienda ospedaliera Pisana "Santa Chiara"

🇮🇹

Pisa, Italy

St. Petersburg State Medical univ. n.a. I.P. Pavlov

🇷🇺

St. Petersburg, Russian Federation

State Medical Institution Replubican Oncological Center

🇷🇺

Bashkortostan, Russian Federation

Indo-American Cancer Institute & Research Center

🇮🇳

Hyderabaad, AndhPrad, India

Fundei Clinical Institute

🇷🇴

Bucharest, Romania

Klinika Hematologii, Onkologii i Chorob Wewnetrznych

🇵🇱

Gdansk, Poland

Kyiv Bone Marrow Transplantation

🇺🇦

Kyiv, Ukraine

Russian Oncological Research Center n.a. N.N. Blokhin

🇷🇺

Moscow, Russian Federation

Universita La Sapienza

🇮🇹

Roma, Italy

Hospital Maciel

🇺🇾

Montevideo, Uruguay

Policlinico S. Maria alle Scotte

🇮🇹

Siena, Italy

Hospital Carlos Andrade Marin Oncologia

🇪🇨

Quito,, Pinchincha, Ecuador

Institutul Oncologic "Ion Chiricuta" Oncologie Medicala

🇷🇴

Cluj-Napoca, Romania

Tartu University Clinics, Hematology Oncology Clinic

🇪🇪

Tartu, Estonia

Medical Solutions

🇲🇽

Guatimala, Guatemala, Mexico

Hospital Policial de Montevideo

🇺🇾

Poblado Montevideo Chico, Uruguay

Shirdi Sai Baba Cancer Hospital, K.M.C. Manipal

🇮🇳

Manipala, Karna, India

Tata Memorial Hospital

🇮🇳

Mumbai, India

Complejo Hospitalario "Arnulfo Arias Madrid

🇵🇦

Panama, Panama

Hospital Edgardo Rebagliati Martins

🇵🇪

Lima, Peru

Onococenter

🇵🇪

San Borja, Peru

Brasov Counthy Hospital

🇷🇴

Brasov, Romania

Mures County Clinical Hospital

🇷🇴

Targu Mures, Romania

St. Georges Hospital

🇬🇧

London, United Kingdom

Research Insitute of Hematology and Blood Transfusion

🇷🇺

St. Petersburg, Russian Federation

St. Petersburg State Medical Institution: Municipal Hospital #31

🇷🇺

St. Petersburg, Russian Federation

Robert A. Moss, M.D., FACP, Inc.

🇺🇸

Fountain Valley, California, United States

UCLA Medical Center

🇺🇸

Los Angeles, California, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

Northwest Kaiser Permanente

🇺🇸

Portland, Oregon, United States

Northern Utah Hematology Oncology, P.C.

🇺🇸

Ogden, Utah, United States

Bhagwan Mahaveer Cancer Hospital & Research Center

🇮🇳

Jaipur, Rajasthan, India

Ospedale Civile

🇮🇹

Udine, Italy

New Mexico Oncology/Hematology

🇺🇸

Albuquerque, New Mexico, United States

Instituto de Investigaciones Clinicas

🇦🇷

Rosario, Santa Fe, Argentina

Watson Clinic for Cancer Care and Research

🇺🇸

Lakeland, Florida, United States

SUNY Upstate Medical University

🇺🇸

Syracuse, New York, United States

Centro Oncologico Rosario

🇦🇷

Rosario, Santa Fe, Argentina

Academia Nacional de Medicina

🇦🇷

Caba, Argentina

National Centre for Hemotransfusion

🇧🇬

Sofia, Bulgaria

Hospital Privado Centro Medico de Cordoba S.A.

🇦🇷

Cordoba, Argentina

Hospital Universitario Austral

🇦🇷

Buenos Aires, Argentina

University General Hospital for Active Treatment "St. Marina" Clinic of Hematology

🇧🇬

Varna, Bulgaria

ISIS Clinica Especializada

🇦🇷

Santa Fe, Argentina

University Gernal Hospital for Active Treatment "Alexandrovska" - Clinic of Hematology

🇧🇬

Sofia, Bulgaria

Hospital CIMA San Jose

🇨🇷

Escazu, Costa Rica

Hospital Oncologico de Solca

🇪🇨

Capilla Mauta, Guayaquil, Ecuador

Hopitaux Universitaires de Strabourg - Hopital de Hautepierre

🇫🇷

Strasbourg, France

Universitatklinik des Saarlandes, Innere Medzin I

🇩🇪

Hamburg, Germany

Westpfalzklinikum Kaiserslautern

🇩🇪

Kaiserslautern, Germany

Klinikum der Universitaet zu Koeln

🇩🇪

Koeln, Germany

Mutterhaus der Borromaeerinne

🇩🇪

Trier, Germany

Szent Laszlo Korhaz

🇭🇺

Budapest, Hungary

Kaposi Mor Megyei Korhaz

🇭🇺

Kaposvar, Hungary

Regional Cancer Center

🇮🇳

Thiruvananthapuram, Kerla, India

Szegedi Tudomanyegyetem Szent-Gyorgyi Albert Orvos-es Gyogy II

🇭🇺

Szeged, Hungary

Nizam's Institute of Medical Sciences

🇮🇳

Panjagutta, Hyderabad, India

Pecsi Tudomanyegyetem

🇭🇺

Pecs, Hungary

Manipal Hospital

🇮🇳

Bangalore, Karnataka, India

M.S. Ramaiah Medical College

🇮🇳

Bangalore, India

Policlinico S. Orsola, Instituto di Ematologia

🇮🇹

Bologna, Italy

Ospedale S. Martino

🇮🇹

Genova, Italy

Universita degli Studi Perugia Policlinico Monteluce

🇮🇹

Perugia, Italy

Azienda Ospedaliera Pisanan "Santana Chiara"

🇮🇹

Pisa, Italy

Ospedale Oncolgoico Regionale della Basilicata

🇮🇹

Rionero in Vulture, Italy

Ospedale Casa Sollievo della Sofferenza

🇮🇹

San Giovanni Rotondo, Italy

Presidio San Giuseppe Moscati

🇮🇹

Taranto, Italy

Fundacion Centro De Investigacion

🇲🇽

Medellin, Columbia, Mexico

State Therapeutical & Prophlatic Institution: Cheylabinsk Regional Oncological Center

🇷🇺

Chelyabinsk, Russian Federation

St. Petersburg Pavlov State Medical Clinic of Intensive Care & Bone Marrow Transplantation

🇷🇺

St. Petersburg, Russian Federation

Semashko Central Clinical Hospital

🇷🇺

Moscow, Russian Federation

Beatson Oncology Centre, Western Infirmary

🇬🇧

Glasgow, United Kingdom

Central Research Rontgenological and Radiological Institute

🇷🇺

St. Petersburg, Russian Federation

Institute of Blood Pathology & Transfusion Medicine under the UAMS

🇺🇦

Lviv, Ukraine

State Institution: Moscow Regional Research Clinical institute n.a. M.F.

🇷🇺

Moscow, Russian Federation

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