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A Post-marketing, Blinded Study to Investigate How Effective Fidaxomicin is Compared to Vancomycin in the Sustained Cure of Clostridium Difficile Infection in Adults That Are Receiving Therapy to Suppress the Immune System

Phase 4
Terminated
Conditions
Clostridium Difficile
Interventions
Registration Number
NCT01775397
Lead Sponsor
Astellas Pharma Europe Ltd.
Brief Summary

The primary objective is to compare fidaxomicin versus vancomycin for the sustained clinical cure of Clostridium difficile Infection (CDI) in adult patients receiving immunosuppressive therapy.

Detailed Description

On Day 1, subjects with diarrhea defined as having three or more unformed bowel movements or \>200 mL of unformed stool (for subjects having rectal collection devices) within 24 hours, confirmed by a rapid CDI test (positive for both toxins A \& B and glutamate dehydrogenase) to have CDI will be randomized to receive fidaxomicin or vancomycin (1:1 randomization).

Subjects will be treated with study medication from Day 1 to Day 10. Assessment for clinical cure (Test of Cure \[TOC\]) will take place 48 - 72 hours after End of Treatment (EOT). Subjects not meeting the definition of clinical cure at TOC will be defined as treatment failures.

A stool sample for evaluation of microbial cure will be taken at TOC on Day 12.

Subjects meeting the criteria for clinical cure at TOC will be monitored for recurrence until 28 days after TOC (Day 40).

Treatment of subjects with recurrence of CDI will be at the

discretion of the Investigator.

Subjects not meeting the criteria for clinical cure at TOC will be followed for safety until Day 40. Further CDI treatment will be at the discretion of the Investigator.

The strain of Clostridium difficile will be determined for all samples.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
12
Inclusion Criteria
  • CDI is confirmed by clinical symptoms and rapid CDI test

  • Subject has not been treated with medication for CDI within the last 10 days

  • Subject is:

    • receiving immunosuppressive therapy (chemotherapy) or is undergoing a stem cell transplant procedure (defined as the time period from the start of conditioning prior to transplant until 6 months after infusion of stem cells) for a hematological malignancy; or
    • receiving immunosuppressive therapy (chemotherapy) for a solid tumor malignancy or following solid organ transplantation; or
    • being treated with immunosuppressive and /or anti-TNF therapy for an auto-immune disease
  • Any woman of childbearing potential requires negative serum or urine pregnancy test before entry to the study

  • Male and female subjects that are sexually active must agree to practice effective birth control during the study and for 30 days after the end of the study

Exclusion Criteria
  • The subject has experienced more than one previous episode of CDI within the 3 months prior to study inclusion
  • Taking or requiring to be treated with prohibited medications
  • Unable to take oral study medication
  • Female patients that are pregnant, intend to become pregnant or are breastfeeding
  • History of ulcerative colitis or Crohn's disease
  • History or diagnosis of toxic megacolon or pseudomembranous colitis
  • Hypersensitivity to fidaxomicin or any of its components
  • Hypersensitivity to vancomycin or any of its components

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
FidaxomicinFidaxomicinFidaxomicin with alternating matching placebo
FidaxomicinPlaceboFidaxomicin with alternating matching placebo
VancomycinVancomycinParticipants received 4 doses (1 dose every 6 hours) of oral vancomycin hydrochloride each day for the duration of the 10-day treatment period
Primary Outcome Measures
NameTimeMethod
Sustained clinical cure of CDI at day 26Day 26

Clinical cure is defined as a subject that at TOC no further CDI therapy is required since completion of study medication, and has either:

* ≤3 unformed bowel movements for two consecutive days

* ≥50% reduction in the number of unformed bowel movements compared to baseline; or

* 75% reduction in the volume of liquid stool collected or no longer passing liquid stools (for subjects having rectal collection device)

Secondary Outcome Measures
NameTimeMethod
Clinical Cure of CDIDay 12

Clinical cure is defined as a subject that at TOC no further CDI therapy is required since completion of study medication, and has either:

* ≤3 unformed bowel movements for two consecutive days

* ≥50% reduction in the number of unformed bowel movements compared to baseline; or

* 75% reduction in the volume of liquid stool collected or no longer passing liquid stools (for subjects having rectal collection device)

Microbial EradicationDay 12

Total viable count of clostridium difficile recovered from fecal specimen is below the limit of detection

Use of further CDI therapy requiredBetween Day 10 and Day 12
Number of unformed stoolsBetween Day 10 and Day 12
Resolution of diarrheaDay 12

First of two days with \<3 bowel movements per day

Sustained Clinical Cure of CDI at day 40Day 40

Clinical cure is defined as a subject that at TOC no further CDI therapy is required since completion of study medication, and has either:

* ≤3 unformed bowel movements for two consecutive days

* ≥50% reduction in the number of unformed bowel movements compared to baseline; or

* 75% reduction in the volume of liquid stool collected or no longer passing liquid stools (for subjects having rectal collection device)

>50% reduction in number of unformed stools compared to baselineDay 1 to Day 12
Recurrence of CDIBetween Day 1 and Day 40

After TOC, re-establishment of diarrhea to an extent that is greater than the frequency recorded on the last day of study medication

Time to recurrence of CDIBetween Day 12 and Day 40

Time elapsing (days) from TOC to confirmed recurrence of CDI

Trial Locations

Locations (16)

H.U. Gregorio Maranon

🇪🇸

Madrid, Spain

Universitätsklinikum

🇩🇪

Essen, Germany

Charité

🇩🇪

Berlin, Germany

Laiko General Hospital

🇬🇷

Athens, Greece

Metaxa Anticancer Hospital

🇬🇷

Piraeus, Greece

Univ. Klinik für Innere Medizi

🇦🇹

Salzburg, Austria

Hospital 12 de Octubre

🇪🇸

Madrid, Spain

Klinik I für Innere Medizin

🇩🇪

Koln, Germany

Herlev University Hospital

🇩🇰

Herlev, Denmark

Institut Curie

🇫🇷

Paris, France

Hôpital Necker

🇫🇷

Paris, France

Universitätsklinikum Halle

🇩🇪

Halle, Germany

General Hospital of Athens

🇬🇷

Athens, Greece

University Hospital of Crete

🇬🇷

Heraklion, Greece

Szpital Specjalistyczny w Brzo

🇵🇱

Brzozów, Poland

H. U. de Bellvitge

🇪🇸

Barcelona, Spain

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