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Efficacy and Safety of Palonosetron Intravenous in Prevention of Chemotherapy Induced Nausea and Vomiting in Pediatric Patients

Phase 3
Completed
Conditions
Chemotherapy-Induced Nausea and Vomiting
Interventions
Registration Number
NCT01442376
Lead Sponsor
Helsinn Healthcare SA
Brief Summary

The primary objective is to evaluate the efficacy of two different doses of IV palonosetron in the prevention of chemotherapy induced nausea and vomiting in MEC and HEC patients through 120 hours after start of chemotherapy in single and repeated chemotherapy cycles. The secondary objectives are to evaluate the safety and tolerability of IV palonosetron in pediatric patients and evaluate the pharmacokinetics of IV palonosetron in a subset of pediatric CINV patients.

Detailed Description

For neonates (\<28 days, full term) an open-label sub-study will be conducted to assess exposure and tolerability in this age group with escalating doses of palonosetron, starting with 3 mcg/kg to the first three or more neonates included in the study. If this dose is shown to be safe and well tolerated then the following three neonates will be treated with a dose of 10 mcg/kg. If also this dose is safe and well tolerated, then the following three neonates will be treated with a dose of 20 mcg/kg. If this last dose is also shown to be safe and well tolerated, then all the following neonates will be randomized to the main study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
502
Inclusion Criteria
  • Written informed consent signed by parent(s)/legal guardians of the pediatric patient in compliance with the local laws and regulations. In addition signed children's assent form according to local requirements
  • Male or female in- or out-patients from neonates (full term) to <17 years at the time of randomization
  • Patient weight at least 3.2 kg
  • Histologically, and/or cytologically (or imaging in the case of brain tumors) confirmed malignant disease
  • Naïve or non-naïve to chemotherapy
  • Scheduled and eligible to receive at least one of the moderately or highly emetogenic chemotherapeutic agents on Study Day 1
  • For patients aged ≥ 10 years to <17 years: ECOG PS ≤ 2
  • For patients with known hepatic impairment: in the Investigator's opinion the impairment should not jeopardize patient's safety during the study
  • For patients with known renal impairment: in the Investigator's opinion the impairment should not jeopardize patient's safety during the study
  • For patients with known history or predisposition to cardiac abnormalities: in the Investigator's opinion the history/predisposition should not jeopardize patient's safety during the study
  • For patients with known clinically relevant abnormal laboratory values: in the Investigator's opinion the abnormality should not jeopardize the patient's safety during the study
  • Fertile patients (male or female) must use reliable contraceptive measures
  • Female patients who have attained menarche must have a negative pregnancy test at the screening visit (Visit 1) and at study treatment visit (Visit 2)
Exclusion Criteria
  • Lactating or pregnant female patient
  • Patient has received total body irradiation, upper abdomen radiotherapy, radiotherapy of the cranium, craniospinal regions or the pelvis within 1 week prior to study entry (screening)
  • Scheduled to receive concomitant total body irradiation, radiotherapy of the upper abdomen, lower thorax region, or cranium/craniospinal regions up to 24 hours after study drug administration
  • Known history of allergy to any component or other contraindications to any 5-HT3 receptor antagonists
  • Active infection
  • Uncontrolled medical condition
  • Marked baseline prolongation of QTc interval [QTcB or QTcF > 460 msec] in any of the ECG assessments at screening. For this purpose, assessment will rely on the automatic interpretation by the ECG machine
  • Patient suffering from ongoing vomiting from any organic etiology (including patients with history of gastric outlet obstruction or intestinal obstruction due to adhesions or volvulus) or patients with hydrocephalus
  • Patient who experienced any vomiting, retching, or nausea within 24 hours prior to the administration of the study drug
  • Patient who received any drug with potential anti-emetic effect within 24 hours prior to administration of study treatment, including but not limited to:
  • NK1- receptor antagonists (e.g. aprepitant)
  • 5-HT3 antagonists (e.g., ondansetron, granisetron, dolasetron);
  • Phenothiazines (e.g., perphenazine, prochlorperazine, promethazine, fluphenazine, chlorpromazine, thiethylperazine);
  • Butyrophenones (e.g., droperidol, haloperidol);
  • Benzamides (e.g., metoclopramide, alizapride);
  • Corticosteroids (e.g., prednisone, methylprednisolone; except inhaled steroids for respiratory disorders and topical steroids for skin disease with doses of ≤ 10 mg of prednisone daily or its equivalent); Corticosteroids foreseen in the chemotherapy regimen or to reduce intracranial pressure are allowed. According to the guidelines1,2, patients will receive also dexamethasone as a co-medication in accordance with standard clinical practice and if deemed appropriate by the Investigator.
  • Dimenhydrinate; Hydroxyzine; Domperidone; Lorazepam; Cyclizine; Cannabinoids; Scopolamine; Trimethobenzamide HCl; Meclizine hydrochloride; Pseudoephedrine HCl;
  • Over the Counter (OTC) antiemetics, OTC cold or OTC allergy medications;
  • Herbal preparations containing ephedra or ginger.
  • Patient aged ≤ 6 years who received any investigational drug (defined as a medication with no marketing authorization granted for any age group and any indication) within 90 days prior to Day 1, or patient aged > 6 years who received any investigational drug within 30 days prior to Day 1 or is expected to receive investigational drugs prior to study completion
  • Patient who participated in any previous trial with palonosetron

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Palonosetron 10 mcg/kgPlacebo to OndansetronPalonosetron and placebo to Ondansetron Intervention: Drug: Palonosetron
Palonosetron 20 mcg/kgPlacebo to OndansetronPalonosetron and placebo to Ondansetron Intervention: Drug: Palonosetron
OndansetronPlacebo to PalonosetronOndansetron and placebo to Palonosetron Drug: Comparator: Ondansetron
Palonosetron 10 mcg/kgPalonosetronPalonosetron and placebo to Ondansetron Intervention: Drug: Palonosetron
Palonosetron 20 mcg/kgPalonosetronPalonosetron and placebo to Ondansetron Intervention: Drug: Palonosetron
OndansetronOndansetronOndansetron and placebo to Palonosetron Drug: Comparator: Ondansetron
Primary Outcome Measures
NameTimeMethod
Proportion of Patients With Complete Response 0 to 24 Hours (Acute Phase) in Cycle 10 to 24 hours after T0

Complete Response (CR) was defined as no vomiting, no retching, and no use of antiemetic rescue medication from 0 to 24 hours (acute phase) after T0 (start of administration of the most emetogenic chemotherapy) during first cycle. Time 0 (T0) is defined as the time when the patient starts the first cycle of chemotherapy.

Secondary Outcome Measures
NameTimeMethod
Proportion of Patients With Complete Response >24 to 120 Hours (Delayed Phase) in Cycle 1from >24 to 120 hours (delayed phase) after T0

Complete Response (CR) was defined as no vomiting, no retching, and no use of antiemetic rescue medication from \>24 to 120 hours (delayed phase) after T0 (start of administration of the most emetogenic chemotherapy) during first cycle.

Trial Locations

Locations (66)

A. I. duPont Hospital for Children

🇺🇸

Wilmington, Delaware, United States

Nemours Children's Clinic

🇺🇸

Pensacola, Florida, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Clinica Davila

🇨🇱

Santiago, Chile

Specialised Hospital for Active Treatment of Oncohematological Diseases in Children

🇧🇬

Sofia, Bulgaria

Hospital Dr Luis Calvo Mackenna

🇨🇱

Santiago, Chile

Clinica Santa Maria SA

🇨🇱

Santiago, Chile

Hospital Clinico UC

🇨🇱

Santiago, Chile

University Hospital in Ostrava, Clinic of Pediatric

🇨🇿

Ostrava, Czech Republic

Instituto Nacional de Enfermedades Neoplásicas

🇵🇪

Lima, Peru

University Hospital in Pilsen

🇨🇿

Plzen-Lochotin, Czech Republic

University Hospital Motol, Department of Paediatric Heamatology and Oncology

🇨🇿

Praha 5, Czech Republic

Tallin Children's Hospital

🇪🇪

Tallinn, Estonia

Tartu University Hospital, Hematology - Oncology Clinic

🇪🇪

Tartu, Estonia

Clinica Anglo Americana - Centro de Investigacion Oncologica CAA

🇵🇪

San Isidro Lima, Peru

Szpital Uniwersytecki - Department of Pediatrics, Hematology and Oncology

🇵🇱

Bydgoszcz, Poland

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Uniwersytecki Szpital

🇵🇱

Lodz, Poland

Fundeni Clinical Institute, Pediatrics Clinic

🇷🇴

Bucharest, Romania

St. Petersburg State Medical University

🇷🇺

St. Petersburg, Russian Federation

Pediatric Regional Clinical Hospital

🇷🇺

Krasnodar, Russian Federation

Upstate Medical University

🇺🇸

Syracuse, New York, United States

Department of Pediatrics

🇺🇸

Valhalla, New York, United States

Nationwide Children's Hospital

🇺🇸

Columbus, Ohio, United States

Nemours Children's Clinic-Orlando

🇺🇸

Orlando, Florida, United States

University of Kentucky - Chandler Medical Center

🇺🇸

Lexington, Kentucky, United States

Backus Children's Hospital at University Pediatrics

🇺🇸

Savannah, Georgia, United States

Hospital Italiano de Buenos Aires

🇦🇷

Buenos Aires, Argentina

Hospital Privado Centro Medico de Cordoba

🇦🇷

Cordoba, Argentina

Institut Pomnik - The Children Memorial Health Institute, Department of Oncology

🇵🇱

Warsaw, Poland

Samodzielny Publiczny Szpital

🇵🇱

Wroclaw, Poland

Russian Oncology Research Center

🇷🇺

Moscow, Russian Federation

Omsk Regional Clinical Oncology Center

🇷🇺

Omsk, Russian Federation

State Clinical Hospital

🇷🇺

St. Petersburg, Russian Federation

Department for hematology and oncology

🇷🇸

Belgrade, Serbia

Clinical Center Nis, Clinic for pediatrics internal diseases, Department for hematology and oncology

🇷🇸

Nis, Serbia

Public Healthcare Institution: Regional Children's Clinical Hospital #1

🇺🇦

Kharkiv, Ukraine

State Institution: V. K. Husak Institute of Urgent and Reconstructive Surgery

🇺🇦

Donetsk, Ukraine

National Institute of Cancer

🇺🇦

Kyiv, Ukraine

Public Treatment and Prophylaxis Institution: Regional Children's Clinical Hospital

🇺🇦

Donetsk, Ukraine

The Children's Hospital

🇺🇸

Aurora, Colorado, United States

Hospital Nacional "Prof. Dr. Alejandro Posadas"

🇦🇷

El Palomar, Argentina

CEMIC

🇦🇷

Buenos Aires, Argentina

University Hospital Brno, Children's Medical Centre, Clinic of Pediatric Oncology

🇨🇿

Brno, Czech Republic

University Medical Center Freiburg

🇩🇪

Freiburg, Germany

Pediatrics and Genetic Medicine Clinic

🇧🇬

Plovdiv, Bulgaria

Arkansas Children's Hospital

🇺🇸

Little Rock, Arkansas, United States

Specialised Pediatric Clinic of Clinical Hematology and Oncology Mutiprofile Hospital for Active Treatment "Sveta Marina"

🇧🇬

Varna, Bulgaria

Children's Cancer Research Institute

🇦🇹

Wien, Austria

Medical University of Vienna

🇦🇹

Wien, Austria

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

University of Szeged, Szent-Gyorgyl Albert Clinical Center, Department of Pediatrics

🇭🇺

Szeged, Hungary

CHRU de Tours - Centre de Pediatrie Gatien de Clocheville

🇫🇷

Tours Cedex 09, France

Semmelweis University, 2nd Department of Pediatrics

🇭🇺

Budapest, Hungary

University Hospital of Cologne

🇩🇪

Cologne, Germany

CHRU de Lille - Hopital d'Hematologie Pediatrique

🇫🇷

Lille Cedex, France

Hopital Arnaud de Villenueve

🇫🇷

Montpellier, France

Oncosalud SAC RCI 300

🇵🇪

Lima, Peru

Uniwersyteckie Centrum Kliniczne

🇵🇱

Gdansk, Poland

Dzieciecy Szpital Kliniczny

🇵🇱

Lublin, Poland

Chelyabinsk Pediatric Regional Clinical Hospital, Oncohematology Department

🇷🇺

Chelyabinsk, Russian Federation

"Prof. Dr. Alexandru Trestioreanu" Institute of Oncology, Pediatric Oncology Department

🇷🇴

Bucharest, Romania

"Prof. Dr. Ion Chiricuta" Institute of Oncology, Cluj-Napoca Pediatric Department

🇷🇴

Cluj, Romania

Sf. Maria - Chidren's Emergency Clinical Hospital

🇷🇴

Iasi, Romania

Regional Pediatric Clinical Hospital #1

🇷🇺

Ekaterinburg, Russian Federation

Moscow State Institution: Morozovskaya Pediatric City Clinical Hospital

🇷🇺

Moscow, Russian Federation

City of Hope National Medical Center

🇺🇸

Duarte, California, United States

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