MedPath

Debio 1143-201 Dose-finding and Efficacy Phase I/II Trial

Not Applicable
Completed
Conditions
Squamous Cell Carcinoma of the Head and Neck
Interventions
Radiation: Radiotherapy
Drug: Placebo
Registration Number
NCT02022098
Lead Sponsor
Debiopharm International SA
Brief Summary

The use of multiple drugs in a single clinical trial or as a therapeutic strategy has become common, particularly in the treatment of cancer. Because traditional trials are designed to evaluate one agent at a time, the evaluation of therapies in combination requires specialized trial designs. In place of the traditional separate phase I and II trials, this trial uses a single phase I/II clinical trial to evaluate simultaneously the safety and efficacy of combination dose levels, and select the optimal combination dose.

Therefore, this is a two part trial of Debio 1143 combined with concurrent cisplatin and radiotherapy (CRT) in participants with previously untreated stage III, IVa or IVb head and neck cancer. The trial begins with an initial period of dose escalation (Phase I) to investigate the maximum tolerated dose (MTD) of Debio 1143 that can safely be given in combination with CRT.

Using the MTD determined in the Phase I portion, the randomized phase II trial in 94 participants compares Debio 1143 to placebo, both with concomitant CRT. The aim is to evaluate the efficacy and safety of Debio 1143.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
144
Inclusion Criteria
  • Meets protocol-specified criteria for qualification and contraception
  • Is willing and able to comply with study procedures and restrictions related to food, drink and medications
  • Voluntarily consents to participate and provides written informed consent prior to any protocol-specific procedures
Exclusion Criteria
  • Has history or current use of over-the-counter medications, dietary supplements, or drugs (including nicotine and alcohol) outside protocol-specified parameters

  • Has signs, symptoms or history of any condition that, per protocol or in the opinion of the investigator, might compromise:

    1. the safety or well-being of the participant or study staff;
    2. the safety or well-being of the participant's offspring (such as through pregnancy or breast-feeding);
    3. the analysis of results

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Debio 1143RadiotherapyIn addition to Cisplatin and Radiotherapy, Debio 1143 in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
Debio 1143Debio 1143In addition to Cisplatin and Radiotherapy, Debio 1143 in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
PlaceboRadiotherapyIn addition to Cisplatin and Radiotherapy, matching placebo in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
PlaceboPlaceboIn addition to Cisplatin and Radiotherapy, matching placebo in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
Debio 1143CisplatinIn addition to Cisplatin and Radiotherapy, Debio 1143 in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
PlaceboCisplatinIn addition to Cisplatin and Radiotherapy, matching placebo in solution form will be administered orally or by feeding tube (while fasting) daily for 14 days every three weeks (on days 1-14, 22-35 and 43-56).
Primary Outcome Measures
NameTimeMethod
Phase II: Percentage of participants achieving Locoregional Control (LRC) at 18 months from the end of chemo-radiation therapy (CRT)within 4 years
Secondary Outcome Measures
NameTimeMethod
Phase II: Best Overall response rate, Disease Control rate and Response Rate after 10 weeks from the end of CRTwithin 5 years
Phase II: Locoregional control rate at 6 months and one year after completion of CRTwithin 5 years
Phase II: Progression free survival rate at one year, 18 months and at 2 years as of initiation of CRTwithin 5 years
Phase II: Distant relapse rate at six months, one year and 18 months after completion of CRTwithin 5 years
Phase II: Disease specific survival rate one year and at 2 years as of initiation of CRTwithin 5 years
Phase II: Overall survival rate at one year and at 2 years as of initiation of CRTwithin 5 years
Phase II: Number of participants with clinically significant change in vital signs during participation in the trialwithin 5 years
Phase II: Number of participants with Serious Adverse Eventswithin 5 years
Phase II: Number of participants with Adverse Events (AEs)within 5 years

Categories will be based on severity graded according to NCI-CTCAE version 4 criteria

Phase II: Number of participants with Laboratory Abnormalitieswithin 5 years

Categories will be based on severity graded according to NCI-CTCAE version 4 criteria

Phase II: Number of participants with Late Toxicity as of initiation of CRTwithin 5 years

Categories: at 1 year, at 2 years

Phase II: Number of participants with treatment changes due to AEswithin 5 years

Categories: Treatment discontinuation, Treatment modification

Phase II: Complete Response Rate (by RECIST version 1.1) at six months after completion of chemo-radiation therapy (CRT) therapywithin 5 years
Phase II: Best Overall response rate, Disease Control rate and Response Rate after 6 months from the end of CRTwithin 5 years

Trial Locations

Locations (19)

C.H.U. Sud Amiens

🇫🇷

Amiens, France

Centre Jean Perrin

🇫🇷

Clermont-Ferrand Cedex 01, France

Centre Hospitalier de Bretagne Sud - HÔPITAL DU SCORFF

🇫🇷

Lorient, Bp 2233, France

CHD Vendée

🇫🇷

La Roche Sur Yon cedex 9, France

Institut Sainte-Catherine

🇫🇷

Avignon Cedex 9, France

CHU Grenoble

🇫🇷

Grenoble, France

Hôpital Nord Franche-Comté

🇫🇷

Montbéliard, France

Centre Guillaume le Conquérant

🇫🇷

Le Havre, France

Centre Henri Becquerel

🇫🇷

Rouen, France

ICM - Val D'Aurelle

🇫🇷

Montpellier, France

Centre Jean Bernard

🇫🇷

Le Mans, France

Institut Curie

🇫🇷

Paris, France

Institut Claudius Regaud

🇫🇷

Toulouse, France

Institut de Cancérologie de l'Ouest (ICO) René Gauducheau

🇫🇷

Saint-Herblain, France

Institut de Cancérologie Lucien Neuwirth (ICLN)

🇫🇷

Saint-Priest en Jarez, France

Inselspital Bern, Universitätsklinik für Radio-Onkologie, Freiburgstrasse 4

🇨🇭

Bern, Switzerland

L'Institut de Cancérologie de Lorraine (ICL) Alexis Vautrin

🇫🇷

Vandoeuvre-lès-Nancy, France

Institut Gustave Roussy

🇫🇷

Villejuif, France

Centre Hospitalier Universitaire Vaudois (CHUV)

🇨🇭

Lausanne, Switzerland

© Copyright 2025. All Rights Reserved by MedPath