MedPath

Dose-Finding Study of Favipiravir in the Treatment of Uncomplicated Influenza

Phase 2
Completed
Conditions
Influenza
Interventions
Drug: Placebo comparator
Registration Number
NCT01068912
Lead Sponsor
MDVI, LLC
Brief Summary

This is a Phase 2, randomized, double-blind, placebo-controlled multicenter study evaluating the efficacy and safety of two doses of favipiravir in adult patients with uncomplicated influenza.

Detailed Description

This is a Phase 2, randomized, double-blind, placebo-controlled, multicenter study designed to evaluate the efficacy and safety of a 5-day regimen of favipiravir in influenza patients aged 20-80 years. Enrolled patients will be randomly assigned to 1 of 3 parallel treatment dose groups:Placebo; Low-dose favipiravir (1000 mg favipiravir BID for 1 day, followed by 400 mg favipiravir BID for 4 days); High-dose favipiravir (1200 mg favipiravir BID for 1 day, followed by 800 mg favipiravir BID for 4 days).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
530
Inclusion Criteria
  1. Patients who test positive for influenza A or B by a commercially available Rapid Antigen Test (RAT) of the nasopharynx. A patient with a negative RAT result may still enroll if the sponsor and investigator agree that there is a known influenza outbreak circulating in the community.

  2. Patients ≥ 20 but < 65 years of age with a temperature (oral) of 100.4°F (38.0°C) or more; patients ≥ 65 years of age with a temperature (oral) of 100.0°F (37.8°C) or more at the first visit, or in the 6 hours prior if antipyretics were taken.

  3. Patients with 2 or more of the following symptoms (moderate to severe in intensity) at the time of enrollment:

    • Cough
    • Sore throat
    • Headache
    • Nasal congestion
    • Feeling feverish
    • Body aches and pains
    • Fatigue (tiredness)
Exclusion Criteria
  1. Patients who have had influenza symptoms or fever (i.e., one of the symptoms listed under the inclusion criteria) for 36 hours or more prior to study screening.
  2. Patients who have underlying chronic respiratory disease (e.g., chronic obstructive pulmonary disease [COPD], chronic bronchitis, diffuse panbronchiolitis, bronchiectasis, pulmonary emphysema, pulmonary fibrosis, bronchial asthma, or old tuberculosis).
  3. Patients who at the beginning of the study are suspected of having bacterial respiratory infection (i.e., expectoration of purulent or mucopurulent sputum and/or infiltrate in lung in a chest x-ray, etc.).
  4. Patients who have serious chronic diseases. For example, patients with HIV, cancer (i.e., requiring chemotherapy within the preceding 6 months), cirrhosis (end-stage), and/or unstable renal, cardiac, pulmonary, neurologic, vascular, or endocrinologic disease states requiring medication dose adjustments within the last 30 days.

Study & Design

Study Type
INTERVENTIONAL
Study Design
FACTORIAL
Arm && Interventions
GroupInterventionDescription
PlaceboPlacebo comparatorPlacebo
2: ExperimentalFavipiravirHigh-dose favipiravir regimen: 1200 mg favipiravir BID x 1 day, and 800 mg favipiravir BID x 4 days
1: ExperimentalFavipiravirLow-dose favipiravir regimen: 1000 mg favipiravir twice a day (BID) x 1 day, and 400 mg favipiravir BID x 4 days
Primary Outcome Measures
NameTimeMethod
Clinical Efficacy of 2 Dose Regimens of Favipiravir Compared With Placebo in Treating Patients With Influenza22 weeks

Overall time required from first study drug administration to alleviation of the 6 primary influenza symptoms and for temperature (oral) measurements to be less than 38.0°C for patients aged 20 to less than 65 years and less than 37.8°C for patients aged 65 years or older. "Alleviated" was defined as all 6 symptom scores had to be decreased to 1 or below and the decrease remain unchanged for 21.5 hours.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (227)

#048

🇺🇸

Elkridge, Maryland, United States

#132

🇺🇸

Houston, Texas, United States

#157

🇺🇸

Houston, Texas, United States

#176

🇺🇸

Las Vegas, Nevada, United States

#032

🇺🇸

Chino, California, United States

#091

🇺🇸

Pacific Palisades, California, United States

#097

🇺🇸

Pomona, California, United States

#068

🇺🇸

Sacramento, California, United States

#007

🇺🇸

Delray Beach, Florida, United States

#060

🇺🇸

Coral Gables, Florida, United States

#014

🇺🇸

Hialeah, Florida, United States

#149

🇺🇸

Miami Gardens, Florida, United States

#040

🇺🇸

Miami, Florida, United States

#823

🇺🇸

Alexandria, Louisiana, United States

#187

🇺🇸

Worcester, Massachusetts, United States

#170

🇺🇸

Bellevue, Nebraska, United States

#178

🇺🇸

High Point, North Carolina, United States

#189

🇺🇸

Morganton, North Carolina, United States

#083

🇺🇸

Wadsworth, Ohio, United States

#066

🇺🇸

Corpus Christi, Texas, United States

#084

🇺🇸

Clarksville, Tennessee, United States

#039

🇺🇸

Houston, Texas, United States

#090

🇺🇸

Orem, Utah, United States

#172

🇺🇸

Spokane, Washington, United States

#214

🇦🇺

Carlton, New South Wales, Australia

#221

🇦🇺

Deception Bay, Queensland, Australia

#607

🇨🇱

Santiago, Chile

#603

🇨🇱

Santiago, Chile

#704

🇵🇾

Campos Cervera, Luque, Paraguay

#505

🇵🇪

Arequipa, Peru

#517

🇵🇪

Lima, Peru

#410

🇿🇦

Krugersdorp, South Africa

#224

🇦🇺

Spearwood, Western Australia, Australia

#831

🇺🇸

Pawleys Island, South Carolina, United States

#002

🇺🇸

Rapid City, South Dakota, United States

#147

🇺🇸

Simpsonville, South Carolina, United States

#081

🇺🇸

Lincoln, Nebraska, United States

#079

🇺🇸

Las Vegas, Nevada, United States

#801

🇺🇸

Baton Rouge, Louisiana, United States

#600

🇨🇱

Temuco, Chile

#511

🇵🇪

Callao, Peru

#506

🇵🇪

Cusco, Peru

#167

🇺🇸

Oklahoma City, Oklahoma, United States

#810

🇺🇸

Oklahoma City, Oklahoma, United States

#832

🇺🇸

Salt Lake City, Utah, United States

#180

🇺🇸

San Antonio, Texas, United States

#817

🇺🇸

San Antonio, Texas, United States

#117

🇺🇸

Salt Lake City, Utah, United States

#065

🇺🇸

Birmingham, Alabama, United States

#151

🇺🇸

Mobile, Alabama, United States

#173

🇺🇸

Toney, Alabama, United States

#161

🇺🇸

Tuscumbia, Alabama, United States

#110

🇺🇸

Mesa, Arizona, United States

#105

🇺🇸

Phoenix, Arizona, United States

#188

🇺🇸

Tucson, Arizona, United States

#107

🇺🇸

Jonesboro, Arkansas, United States

#052

🇺🇸

Hialeah, Florida, United States

#088

🇺🇸

Hialeah, Florida, United States

#153

🇺🇸

Kissimmee, Florida, United States

#034

🇺🇸

Miami, Florida, United States

#047

🇺🇸

Miami, Florida, United States

#082

🇺🇸

Miami, Florida, United States

#835

🇺🇸

Oak Lawn, Illinois, United States

#803

🇺🇸

Franklin, Indiana, United States

#195

🇺🇸

Munci, Indiana, United States

#106

🇺🇸

Wichita, Kansas, United States

#171

🇺🇸

Brooklyn, New York, United States

#037

🇺🇸

Beaumont, Texas, United States

#113

🇺🇸

Bryan, Texas, United States

#136

🇺🇸

Houston, Texas, United States

#158

🇺🇸

Katy, Texas, United States

#818

🇺🇸

San Antonio, Texas, United States

#830

🇺🇸

Sugar Land, Texas, United States

#135

🇺🇸

Tomball, Texas, United States

#809

🇺🇸

Tomball, Texas, United States

#825

🇺🇸

South Jordan, Utah, United States

#133

🇺🇸

West Jordan, Utah, United States

#800

🇺🇸

Alexandria, Virginia, United States

#201

🇦🇺

Maroubra, New South Wales, Australia

#220

🇦🇺

Nerang, Queensland, Australia

#206

🇦🇺

Sherwood, Queensland, Australia

#614

🇨🇱

Rancagua, Chile

#601

🇨🇱

Temuco, Chile

#611

🇨🇱

Viña del Mar, Chile

#304

🇳🇿

Dunedin, Otago, New Zealand

#307

🇳🇿

Auckland, New Zealand

#308

🇳🇿

Hamilton, New Zealand

#703

🇵🇾

esquina Pai Perez, Asunción, Paraguay

#500

🇵🇪

Lima, Peru

#508

🇵🇪

Lima, Peru

#509

🇵🇪

Lima, Peru

#510

🇵🇪

Lima, Peru

#514

🇵🇪

Piura, Peru

#507

🇵🇪

Trujillo, Peru

#421

🇿🇦

Benoni, South Africa

#402

🇿🇦

Cape Town, South Africa

#406

🇿🇦

Durban, South Africa

#408

🇿🇦

Durban, South Africa

#412

🇿🇦

Durban, South Africa

#414

🇿🇦

Durban, South Africa

#411

🇿🇦

Kraaifontein, South Africa

#407

🇿🇦

Port Elizabeth, South Africa

#409

🇿🇦

Pretoria, South Africa

#413

🇿🇦

Pretoria, South Africa

#419

🇿🇦

Pretoria, South Africa

#420

🇿🇦

Pretoria, South Africa

#423

🇿🇦

Pretoria, South Africa

#417

🇿🇦

Sandton, South Africa

#416

🇿🇦

Somerset West, South Africa

#401

🇿🇦

Soweto, South Africa

#166

🇺🇸

Miami, Florida, United States

#018

🇺🇸

Green Valley, Arizona, United States

#156

🇺🇸

Huntsville, Alabama, United States

#089

🇺🇸

Chandler, Arizona, United States

#019

🇺🇸

North Little Rock, Arkansas, United States

#179

🇺🇸

Anaheim, California, United States

#004

🇺🇸

Garden Grove, California, United States

#139

🇺🇸

Los Angeles, California, United States

#140

🇺🇸

Searcy, Arkansas, United States

#154

🇺🇸

Cypress, California, United States

#096

🇺🇸

Oxnard, California, United States

#144

🇺🇸

Long Beach, California, United States

#059

🇺🇸

Anaheim, California, United States

#054

🇺🇸

San Diego, California, United States

#114

🇺🇸

Pasadena, California, United States

#042

🇺🇸

Torrance, California, United States

#197

🇺🇸

Bridgeport, Connecticut, United States

#022

🇺🇸

Boca Raton, Florida, United States

#152

🇺🇸

Boynton Beach, Florida, United States

#086

🇺🇸

Edgewater, Florida, United States

#111

🇺🇸

Pico Rivera, California, United States

#016

🇺🇸

Ft. Myers, Florida, United States

#094

🇺🇸

Kissimmee, Florida, United States

#012

🇺🇸

Melbourne, Florida, United States

#163

🇺🇸

Venice, Florida, United States

#177

🇺🇸

Lauderdale Lakes, Florida, United States

#827

🇺🇸

West Des Moines, Iowa, United States

#008

🇺🇸

Newton, Kansas, United States

#134

🇺🇸

Pinellas Park, Florida, United States

#063

🇺🇸

Boise, Idaho, United States

#814

🇺🇸

Snellville, Georgia, United States

#198

🇺🇸

Greenfield, Indiana, United States

#006

🇺🇸

Cleveland, Ohio, United States

#055

🇺🇸

Hazard, Kentucky, United States

#138

🇺🇸

Shawnee, Kansas, United States

#112

🇺🇸

Henderson, Nevada, United States

#146

🇺🇸

Henderson, Nevada, United States

#015

🇺🇸

Bellevue, Nebraska, United States

#085

🇺🇸

Silver Spring, Maryland, United States

#811

🇺🇸

Detroit, Michigan, United States

#182

🇺🇸

Grove City, Ohio, United States

#816

🇺🇸

Philladelphia, Pennsylvania, United States

#164

🇺🇸

New York, New York, United States

#071

🇺🇸

Tulsa, Oklahoma, United States

#021

🇺🇸

Harrisburg, North Carolina, United States

#011

🇺🇸

Endwell, New York, United States

#030

🇺🇸

Carlisle, Ohio, United States

#024

🇺🇸

Bridgeville, Pennsylvania, United States

#192

🇺🇸

Harleysville, Pennsylvania, United States

#805

🇺🇸

Easley, South Carolina, United States

#819

🇺🇸

Clinton, South Carolina, United States

#812

🇺🇸

Arlington, Texas, United States

#824

🇺🇸

Uniontown, Pennsylvania, United States

#001

🇺🇸

Amarillo, Texas, United States

#053

🇺🇸

Houston, Texas, United States

#058

🇺🇸

Carrollton, Texas, United States

#003

🇺🇸

San Antonio, Texas, United States

#108

🇺🇸

San Antonio, Texas, United States

#822

🇺🇸

Draper, Utah, United States

#202

🇦🇺

Sydney, New South Wales, Australia

#215

🇦🇺

Caboolture, Queensland, Australia

#218

🇦🇺

Neutral Bay, New South Wales, Australia

#142

🇺🇸

Alexandria, Virginia, United States

#216

🇦🇺

Blacktown, New South Wales, Australia

#207

🇦🇺

Burwood, New South Wales, Australia

#208

🇦🇺

Darlinghurst, New South Wales, Australia

#219

🇦🇺

Biggera Waters, Queensland, Australia

#204

🇦🇺

Sydney, New South Wales, Australia

#609

🇨🇱

Santiago, Chile

#612

🇨🇱

Curico, Chile

#606

🇨🇱

Quillota, Chile

#223

🇦🇺

Mirrabooka, Western Australia, Australia

#613

🇨🇱

Antofagasta, Chile

#610

🇨🇱

Santiago, Chile

#602

🇨🇱

Talca, Chile

#306

🇳🇿

Otara, Auckland, New Zealand

#305

🇳🇿

Rotorua, Bay of Plenty, New Zealand

#702

🇵🇾

Florida, Asuncion, Paraguay

#501

🇵🇪

Lima, Peru

#302

🇳🇿

Tauranga, Bay of Plenty, New Zealand

#707

🇵🇾

Pai Perez, Asuncion, Paraguay

#513

🇵🇪

ICA, Peru

#502

🇵🇪

Lima, Peru

#504

🇵🇪

Lima, Peru

#512

🇵🇪

Lima, Peru

#516

🇵🇪

Lima, Peru

#404

🇿🇦

Johannesburg, South Africa

#405

🇿🇦

Durban, South Africa

#422

🇿🇦

Kemptonpark, South Africa

#415

🇿🇦

Pretoria, South Africa

#515

🇵🇪

Lima, Peru

#418

🇿🇦

Pretoria, South Africa

#205

🇦🇺

Glebe, New South Wales, Australia

#301

🇳🇿

Christchurch, Canterbury, New Zealand

#043

🇺🇸

Los Angeles, California, United States

#035

🇺🇸

Jacksonville, Florida, United States

#020

🇺🇸

West Palm Beach, Florida, United States

#815

🇺🇸

Clairton, Pennsylvania, United States

#828

🇺🇸

Scottdale, Pennsylvania, United States

#194

🇺🇸

Johnston, Rhode Island, United States

#191

🇺🇸

Pittsburgh, Pennsylvania, United States

#080

🇺🇸

Honolulu, Hawaii, United States

#017

🇺🇸

Omaha, Nebraska, United States

#041

🇺🇸

Omaha, Nebraska, United States

#137

🇺🇸

Austin, Texas, United States

#045

🇺🇸

Portland, Oregon, United States

#009

🇺🇸

Richmond, Virginia, United States

#038

🇺🇸

Gainesville, Florida, United States

#169

🇺🇸

Omaha, Nebraska, United States

#155

🇺🇸

Scottsboro, Alabama, United States

#050

🇺🇸

Port Orange, Florida, United States

#804

🇺🇸

Fishers, Indiana, United States

#168

🇺🇸

Council Bluffs, Iowa, United States

#160

🇺🇸

Murrells Inlet, South Carolina, United States

#833

🇺🇸

Orangeburg, South Carolina, United States

#217

🇦🇺

Jimboomba, Queensland, Australia

#222

🇦🇺

Morley, Western Australia, Australia

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