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Bumetanide to Ameliorate Tuberous Sclerosis Complex Hyperexcitable Behaviors

Conditions
Tuberous Sclerosis Complex (TSC)
Registration Number
NL-OMON26926
Lead Sponsor
niversity Medical Center Utrecht
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
20
Inclusion Criteria

General inclusion criteria:

1. Males and females aged 8-15 years

Exclusion Criteria

1. Inability to comply with the protocol-specified procedures

2. Presence of a severe medical or genetic disorder other than related to TSC or epilepsy

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Aberrant Behavior Checklist (ABC) irritability subscale
Secondary Outcome Measures
NameTimeMethod
Questionnaires<br /><br>- PedsQL<br /><br>- WHOQOL-BREF, EQ-5D-5L and EQ5D-Youth<br /><br>- TRF, BRIEF<br /><br>- ABC subscales<br /><br>- RBS-V<br /><br>- SRS<br /><br>- SP-NL and SP-SC<br /><br>- TAND<br /><br>Neurocognitive measurements <br /><br>- Cognitive test battery<br /><br>Epilepsy related variables<br /><br>- Seizure frequency<br /><br>- Number of occasions rescue medication is necessary<br>Electroencephalography<br /><br>- Resting state EEG and ERP assessments<br /><br>
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