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A Study of Tarceva (Erlotinib) as First Line Therapy in Participants With Non-Small Cell Lung Cancer Harbouring Epidermal Growth Factor Receptor (EGFR) Mutations

Phase 2
Completed
Conditions
Non-Squamous Non-Small Cell Lung Cancer
Interventions
Registration Number
NCT01310036
Lead Sponsor
Hoffmann-La Roche
Brief Summary

This open-label, single arm study will evaluate the safety and efficacy of Tarceva (erlotinib) as first-line therapy in participants with stage IV or recurrent non-small cell lung cancer who harbour epidermal growth factor receptor (EGFR) mutations. All participants will receive Tarceva 150 mg daily orally until disease progression or unacceptable toxicity occurs. At the investigator's discretion, participants may receive Tarceva beyond disease progression.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
208
Inclusion Criteria
  • Adult participants, >/= 18 years of age
  • Stage IV or recurrent non-small cell lung cancer (NSCLC)
  • Presence of mutation(s) in exon 18 through exon 21 of epidermal growth factor receptor (EGFR), (except T790M single mutation only)
  • Measurable disease (at least one lesion >= 10 mm in longest diameter)
  • Eastern Cooperative Oncology Group (ECOG) performance status 0-2
  • Adequate hematological, renal and liver function
Exclusion Criteria
  • Patients with T790M single mutation only
  • Prior exposure to agents directed at the human epidermal receptor (HER) axis, e.g. erlotinib, gefitinib, cetuximab, trastuzumab
  • Prior chemotherapy or systemic anti-cancer therapy for advanced NSCLC disease
  • Symptomatic or uncontrolled central nervous system (CNS) metastases
  • Other malignancy within the last 5 years, except for carcinoma in situ of the cervix, or basal or squamous cell carcinoma of the skin, or surgically treated localized prostate cancer, or surgically treated ductal cell carcinoma in situ of the breast
  • Any significant ophthalmologic abnormality
  • Pre-existing parenchymal lung disease such as pulmonary fibrosis
  • Use of coumarins (for anti-coagulation therapy the use of low molecular weight heparin is recommended instead)

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ErlotinibErlotinibErlotinib 150 mg daily
Primary Outcome Measures
NameTimeMethod
Progression-free Survival Per RECIST, v. 1.1 (PFS1)Approximately 68 months

PFS1 was defined as time from first dose until documented progressive disease (PD), assessed per Response Evaluation Criteria in Solid Tumors RECIST, v. 1.1, or death from any cause, whichever occurred first. PD was defined as: at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study, including baseline; an absolute increase of at least 5 mm in the sum of diameters of target lesions; and the appearance of one or more new lesions.

Secondary Outcome Measures
NameTimeMethod
Progression-free Survival Per Investigator (PFS2)Approximately 68 months

PFS2 was defined as time from first study dose to off-erlotinib progressive disease (PD), assessed by the investigator based on overall clinical evaluation.

Objective Response Rate (ORR) for All Participants and Participants With EGFR Mutation E19del or L858RApproximately 68 months

ORR was defined as the occurrence of either a confirmed complete (CR) or a partial response (PR, as a best overall response), as determined by RECIST, v. 1.1 criteria. CR was defined as disappearance of all target lesions. PR was defined as least a 30% decrease in the sum of diameters of target lesions, taking as reference the baseline sum of diameters.

Disease Control Rate (DCR) for All Participants and Participants With EGFR Mutation E19del or L858RApproximately 68 months

DCR was defined as CR + PR + Stable disease (SD). CR was defined as disappearance of all target lesions. PR was defined as least a 30% decrease in the sum of diameters of target lesions, taking as reference the baseline sum of diameters. SD was defined as neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for progressive disease (PD), taking as reference the smallest sum diameters while on study. PD was defined as: at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study, including baseline; an absolute increase of at least 5 mm in the sum of diameters of target lesions; and the appearance of one or more new lesions.

Progression-free Survival for Participants With EGFR Mutation E19del or L858R Per RECIST, v. 1.1 (PFS1)Approximately 68 months

PFS1 was defined as time from first dose until documented progressive disease (PD), assessed per Response Evaluation Criteria in Solid Tumors RECIST, v. 1.1, or death from any cause, whichever occurred first. PD was defined as: at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study, including baseline; an absolute increase of at least 5 mm in the sum of diameters of target lesions; and the appearance of one or more new lesions.

Overall Survival (OS) for All Participants and Participants With EGFR Mutation E19del or L858RApproximately 68 months

OS was defined as the time from baseline to the date of death from any cause.

Number of Participants With Adverse EventsApproximately 68 months

An adverse event is any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease temporally associated with the use of a study drug, whether or not considered related to the study drug.

Correlation Between EGFR Mutations in Plasma and Clinical Outcome (ORR/PFS/OS)Approximately 68 months

This outcome measure was not assessed.

Trial Locations

Locations (22)

Changhua Christian Hospital; Internal Medicine

🇨🇳

Changhua, Taiwan

Veterans General Hospital; Internal Medicine

🇨🇳

Kaohsiung, Taiwan

Chang Gung Medical Foundation - Linkou; Chest Dept

🇨🇳

Taoyuan, Taiwan

National Taiwan Uni Hospital; Internal Medicine

🇨🇳

Taipei, Taiwan

Songklanagarind Hospital; Department of Internal Medicine, Division of Respiratory

🇹🇭

Songkhla, Thailand

National Cheng Kung Uni Hospital; Dept of Hematology and Oncology

🇨🇳

Tainan, Taiwan

Seoul National University Bundang Hospital

🇰🇷

Gyeonggi-do, Korea, Republic of

Taichung Veterans General Hospital; Dept of Internal Medicine

🇨🇳

Taichung, Taiwan

Chi-Mei Medical Centre; Hematology & Oncology

🇨🇳

Tainan, Taiwan

China Medical University Hospital; Pulmonary and Critical Care Medicine

🇨🇳

Taichung, Taiwan

Pramongkutklao Hospital; Medicine - Medical Oncology Unit

🇹🇭

Bangkok, Thailand

Seoul St Mary's Hospital

🇰🇷

Seoul, Korea, Republic of

Yonsei University Severance Hospital; Medical Oncology

🇰🇷

Seoul, Korea, Republic of

Gil Hospital. Gachon University

🇰🇷

Incheon, Korea, Republic of

Asan Medical Center; Medical Oncology

🇰🇷

Seoul, Korea, Republic of

Queen Elizabeth Hospital; Clinical Oncology

🇭🇰

Hong Kong, Hong Kong

Princess Margaret Hospital; Oncology

🇭🇰

Hong Kong, Hong Kong

Kaohsiung Chang Gung Memorial Hospital; Dept of Internal Medicine

🇨🇳

Kaohsiung, Taiwan

Taipei Veterans General Hospital; Chest Dept , Section of Thoracic Oncology

🇨🇳

Taipei, Taiwan

Chulalongkorn Hospital; Medical Oncology

🇹🇭

Bangkok, Thailand

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Prince of Wales Hosp; Dept. Of Clinical Onc

🇭🇰

Shatin, Hong Kong

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