MedPath

A Study to Evaluate the Safety and Efficacy of Ruxolitinib Cream in Pediatric Participants With Nonsegmental Vitiligo

Phase 3
Recruiting
Conditions
NonSegmental Vitiligo
Interventions
Drug: Vehicle Cream
Registration Number
NCT06548360
Lead Sponsor
Incyte Corporation
Brief Summary

The purpose of this study is to to evaluate the safety and efficacy of ruxolitinib cream in pediatric participants with nonsegmental vitiligo.

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
180
Inclusion Criteria
  • Clinical diagnosis of nonsegmental vitiligo with depigmented area including ≥ 0.5% BSA on the face, ≥ 0.5 F-VASI, ≥ 3% BSA on nonfacial areas, ≥ 3 T-VASI.
  • Total body vitiligo area does not exceed 10% BSA.
  • Pigmented hair within some of the areas of vitiligo on the face.
  • Must agree to discontinue all agents used to treat vitiligo from screening through the final safety follow-up visit.
  • For sexually active participants (except participants who are prepubescent) willingness to avoid pregnancy or fathering a child from screening through 30 days after the last application of study cream.
Exclusion Criteria
  • Diagnosis of other forms of vitiligo (eg, segmental).
  • Other differential diagnosis of vitiligo or other skin depigmentation disorders (eg, piebaldism, pityriasis alba, leprosy, postinflammatory hypopigmentation, progressive macule hypomelanosis, nevus anemicus, chemical leukoderma, and tinea versicolor).
  • Any other skin disease that, in the opinion of the investigator, would interfere with the study drug application or study assessments.
  • Prior or current use of depigmentation treatments (eg, monobenzone).
  • Any serious illness or medical, physical, or psychiatric condition(s) that, in the investigator's opinion, would interfere with full participation in the study, including application of study cream and attending required study visits; pose a significant risk to the participant; or interfere with interpretation of study data.
  • Use of protocol-defined treatments within the indicated washout period before baseline.
  • Current or previous use of JAK inhibitors, systemic or topical.
  • Protocol-defined clinically significant abnormal laboratory values at screening.
  • BMI-for-age < 5th percentile or ≥ 85th percentile according to the CDC BMI Percentile Calculator for Child and Teen.
  • Pregnant or lactating participants or those considering pregnancy during the period of their study participation.
  • In the opinion of the investigator, unable or unlikely to comply with the application schedule and study evaluations.
  • Living with anyone participating in any current Incyte-sponsored ruxolitinib cream study.
  • Employees of the sponsor or investigator or are otherwise dependents of them.
  • Known allergy or reaction to any component of the study cream formulation.

Other protocol-defined Inclusion/Exclusion Criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Ruxolitinib 1.5 % CreamRuxolitinib CreamParticipants received ruxolitinib 1.5% cream, applied topically to the affected area as defined in the protocol.
Vehicle CreamVehicle CreamParticipants received vehicle cream, applied topically to the affected area as defined by the protocol.
Primary Outcome Measures
NameTimeMethod
Proportion of Participants Achieving a ≥ 75% Improvement From Baseline in the Facial Vitiligo Area Scoring Index (F-VASI75)Week 24

≥75% improvement in facial Vitiligo Area Scoring Index.

Secondary Outcome Measures
NameTimeMethod
Proportion of Participants Achieving Facial Vitiligo Area Scoring Index (F-VASI50)Week 52

≥50% improvement in facial Vitiligo Area Scoring Index.

Proportion of Participants Achieving Facial Vitiligo Area Scoring Index (F-VASI90)Week 52

≥90% improvement in facial Vitiligo Area Scoring Index.

Percentage change from baseline in F-BSAWeek 24

Facial body surface area (F-BSA) takes into account the facial depigmented areas as a percentage of the total body area.

Proportion of Participants Achieving Total Body Vitiligo Area Scoring Index (T-VASI90)Week 24 and Week 52

≥90% improvement in total body Vitiligo Area Scoring Index

Pharmacokinetic (PK) of Ruxolitinib: Trough concentrationsWeeks 6, 24, 30 and 52

Trough is defined as the concentration reached by a drug immediately before the next dose is administered.

Proportion of Participants Achieving a ≥ 50% Improvement From Baseline in the Total Body Vitiligo Area Scoring Index (T-VASI50)Week 24

≥50% improvement in total body Vitiligo Area Scoring Index.

Number of Treatment Emergent Adverse Events (TEAEs)Up to Week 52 and 30 days

TEAE defined as any adverse event either reported for the first time or worsening of a pre-existing event after first dose of study drug.

Proportion of Participants Achieving Total Body Vitiligo Area Scoring Index (T-VASI25)Week 24 and Week 52

≥25% improvement in total body Vitiligo Area Scoring Index.

Proportion of Participants Achieving Total Body Vitiligo Area Scoring Index (T-VASI75)Week 24 and Week 52

≥75% improvement in total body Vitiligo Area Scoring Index

Proportion of Participants Achieving Facial Vitiligo Area Scoring Index (F-VASI75)Week 52

≥75% improvement in facial Vitiligo Area Scoring Index.

Proportion of Participants Achieving Total Body Vitiligo Area Scoring Index (T-VASI50)Week 52

≥50% improvement in total body Vitiligo Area Scoring Index.

Trial Locations

Locations (91)

University of Alabama At Birmingham-School of Medicine

🇺🇸

Birmingham, Alabama, United States

Phoenix Children'S Hospital

🇺🇸

Phoenix, Arizona, United States

Affiliated Dermatology

🇺🇸

Scottsdale, Arizona, United States

Banner - University Medicine Multispecialty Services Clinic

🇺🇸

Tucson, Arizona, United States

Premier Dermatology Clinical Trials Institute At Northwest Arkansas

🇺🇸

Fayetteville, Arkansas, United States

Burke Pharmaceutical Research

🇺🇸

Hot Springs, Arkansas, United States

Axon Clinical Research

🇺🇸

Inglewood, California, United States

University of California Irvine

🇺🇸

Irvine, California, United States

Dermatology Research Associates

🇺🇸

Los Angeles, California, United States

La Universal Research Center, Inc

🇺🇸

Los Angeles, California, United States

Stanford School of Medicine

🇺🇸

Palo Alto, California, United States

Empire Clinical Research

🇺🇸

Pomona, California, United States

Norcal Clinical Research

🇺🇸

Rocklin, California, United States

Peninsula Research Associates Pra

🇺🇸

Rolling Hills Estates, California, United States

Integrative Skin Science and Research

🇺🇸

Sacramento, California, United States

Rady Children'S Hospital-San Diego

🇺🇸

San Diego, California, United States

Children'S Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Paradigm Clinical Research Centers, Inc.

🇺🇸

Wheat Ridge, Colorado, United States

Skin Care Research, Llc

🇺🇸

Boca Raton, Florida, United States

Encore Medical Research, Llc Boynton Beach

🇺🇸

Boynton Beach, Florida, United States

Pediatric Skin Research Llc

🇺🇸

Coral Gables, Florida, United States

Skin Care Research, Llc Scr Hollywood

🇺🇸

Hollywood, Florida, United States

Solutions Through Advanced Research, Inc

🇺🇸

Jacksonville, Florida, United States

Nicklaus Children'S Hospital

🇺🇸

Miami, Florida, United States

Dh Tamarac Research Center Etna Medical Center Emc

🇺🇸

Tamarac, Florida, United States

Usf Health Morsani Center For Advanced Healthcare

🇺🇸

Tampa, Florida, United States

Emory University

🇺🇸

Atlanta, Georgia, United States

Cleaver Medical Group

🇺🇸

Cumming, Georgia, United States

Advanced Medical Research Pc

🇺🇸

Sandy Springs, Georgia, United States

Treasure Valley Medical Research

🇺🇸

Boise, Idaho, United States

Illinois Dermatology Institute the Chicago Loop

🇺🇸

Chicago, Illinois, United States

Northwestern Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Advanced Dermatology Lincolnshire

🇺🇸

Lincolnshire, Illinois, United States

Northshore University Healthsystem

🇺🇸

Skokie, Illinois, United States

Indiana University School of Medicine

🇺🇸

Indianapolis, Indiana, United States

Wellskin Dermatology & Aesthetics

🇺🇸

Bowling Green, Kentucky, United States

Tulane University Health Sciences Center

🇺🇸

New Orleans, Louisiana, United States

Dermatology Associates Pc

🇺🇸

Rockville, Maryland, United States

Massachusetts General Hospital-Dermatology Associates

🇺🇸

Boston, Massachusetts, United States

Metro Boston Clinical Partners

🇺🇸

Brighton, Massachusetts, United States

Michigan Center For Research Company

🇺🇸

Clarkston, Michigan, United States

Medisearch Clinical Trials

🇺🇸

Saint Joseph, Missouri, United States

Boeson Research

🇺🇸

Missoula, Montana, United States

Skin Specialists Pc the Advanced Skin Research Center

🇺🇸

Omaha, Nebraska, United States

The University of New Mexico Unm Health Sciences Center Hsc

🇺🇸

Albuquerque, New Mexico, United States

Suny Downstate Medical Center

🇺🇸

Brooklyn, New York, United States

The Dermatology Specialists Greenwich

🇺🇸

New York, New York, United States

Equity Medical, Llc

🇺🇸

New York, New York, United States

Mount Sinai Doctors

🇺🇸

New York, New York, United States

Sadick Dermatology Sadick Research Group

🇺🇸

New York, New York, United States

Skin Search of Rochester

🇺🇸

Rochester, New York, United States

Dermatologists of Southwestern Ohio, Llc

🇺🇸

Bexley, Ohio, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Columbia Dermatology

🇺🇸

Columbia, South Carolina, United States

International Clinical Research Tennessee Llc

🇺🇸

Murfreesboro, Tennessee, United States

Dell Children'S Medical Group

🇺🇸

Austin, Texas, United States

The University of Texas Health Science Center At Houston

🇺🇸

Bellaire, Texas, United States

Dfw Clinical Trials

🇺🇸

Carrollton, Texas, United States

3A Research Llc West Location

🇺🇸

El Paso, Texas, United States

Reveal Research Institute

🇺🇸

Frisco, Texas, United States

Pediatric Dermatology of North Texas

🇺🇸

Grapevine, Texas, United States

Us Dermatology Partners Longview

🇺🇸

Longview, Texas, United States

Texas Dermatology and Laser Specialists

🇺🇸

San Antonio, Texas, United States

University of Utah Midvalley Dermatology

🇺🇸

Murray, Utah, United States

Jordan Valley Dermatology Center

🇺🇸

South Jordan, Utah, United States

Virginia Clinical Research, Inc Vcr Pariser Dermatology Specialists, Ltd Norfolk Location

🇺🇸

Norfolk, Virginia, United States

Frontier Dermatology

🇺🇸

Mill Creek, Washington, United States

Seattle Children'S Hospital

🇺🇸

Seattle, Washington, United States

Dermatology Specialists of Spokane

🇺🇸

Spokane, Washington, United States

University of Wisconsin School of Medicine

🇺🇸

Madison, Wisconsin, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Kirk Barber Research

🇨🇦

Calgary, Alberta, Canada

Dermatology Research Institute

🇨🇦

Calgary, Alberta, Canada

Alberta Health Services (Ahs) - Alberta Children'S Hospital (Ach)

🇨🇦

Calgary, Alberta, Canada

Laser Rejuvenation Clinics Edmonton D.T. Inc

🇨🇦

Edmonton, Alberta, Canada

Alberta Dermasurgery Centre

🇨🇦

Edmonton, Alberta, Canada

Coal Harbour Rejuvenation Dermatology, Inc.

🇨🇦

Vancouver, British Columbia, Canada

Winnipeg Clinic

🇨🇦

Winnipeg, Manitoba, Canada

Maritime Dermatology

🇨🇦

Halifax, Nova Scotia, Canada

Childrens Hospital of Eastern Ontario

🇨🇦

Ottawa, Ontario, Canada

Dar Clinical Research Inc

🇨🇦

Ottawa, Ontario, Canada

Research Toronto

🇨🇦

Toronto, Ontario, Canada

University of Toronto - the Hospital For Sick Children (Sickkids)

🇨🇦

Toronto, Ontario, Canada

Dermatelier on Avenue

🇨🇦

Toronto, Ontario, Canada

Centre de Recherche St-Louis

🇨🇦

Montreal, Quebec, Canada

Universite de Montreal - Centre Hospitalier Universitaire (Chu) Sainte-Justine - Centre de Recherche

🇨🇦

Montreal, Quebec, Canada

Centre Hospitalier Universitaire de Quebec - Centre Hospitalier de L'Universite Laval (Chul)

🇨🇦

Quebec City, Quebec, Canada

Centre de Recherche Saint-Louis

🇨🇦

Quebec City, Quebec, Canada

Saskatoon Dermatology Centre

🇨🇦

Saskatoon, Saskatchewan, Canada

Skincare Studio Dermatology Centre

🇨🇦

St. John's, Canada

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