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Zoledronic Acid - Letrozole Adjuvant Synergy Trial (ZFAST) - Cancer Treatment Related Bone Loss in Postmenopausal Women With Estrogen Receptor Positive and/or Progesterone Receptor Positive Breast Cancer Receiving Adjuvant Hormonal Therapy

Phase 3
Completed
Conditions
Breast Neoplasms
Osteoporosis
Interventions
Registration Number
NCT00050011
Lead Sponsor
Novartis Pharmaceuticals
Brief Summary

This protocol is designed to compare the effect on bone of Zoledronic Acid 4 mg every 6 months when given upfront versus delayed start (based on a post-baseline BMD T- Score below -2.0 SD at either the lumbar spine or total hip, or any clinical fracture unrelated to trauma, or an asymptomatic fracture discovered at the month 36 scheduled visit) in stage I-IIIb postmenopausal women with hormone receptor positive breast cancer who will receive Letrozole 2.5 mg daily as an adjuvant therapy.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
602
Inclusion Criteria
  1. Signed informed consent

  2. Postmenopausal status defined by one of the following :

    • women equal to or greater than 55 years with cessation of menses
    • spontaneous cessation of menses within the past 1 year, but amenorrheic in women less than or equal to 55 years (e.g., spontaneous or secondary to hysterectomy), and with postmenopausal gonadotrophin levels (follicle stimulating hormone levels >40 IU/L) or postmenopausal estradiol levels (< 5 ng/dL) or according to the definition of "postmenopausal range" for the laboratory involved
    • bilateral oophorectomy (prior to the diagnosis of breast cancer).
  3. Adequately diagnosed and treated breast cancer defined as:

    • Patients with breast cancer whose tumor can be removed by an appropriate surgical procedure such as mastectomy or breast conserving surgery and who receive appropriate additional local treatments such as radiotherapy according to best practice.
    • Patients must be at the end of their local treatment without evidence of local residual disease.
    • Patients must have no clinical or radiological evidence of distant metastasis.
  4. Hormone receptor positive defined as:

    • ER and/or PR greater than or equal to1 0 fmol/mg cytosol protein; or greater than or equal to 10% of the tumor cells positive by
    • immunohistochemical evaluation.
  5. Patients with a baseline lumbar spine and total hip BMD T-score at or above -2.0 SD are eligible.

  6. Patients who will receive adjuvant chemotherapy are eligible for participation. Adjuvant chemotherapy must be completed prior to randomization.

  7. The date of randomization must not be more than the following:

    • 12 weeks from completion of surgery;
    • 12 weeks after completion of adjuvant chemotherapy;
    • 12 weeks after completion of surgery and radiation therapy; however the patient may be randomized while receiving radiation therapy - this decision is at the Investigator's discretion.
    • 12 weeks after completion of chemotherapy and radiation therapy; however, the patient may be randomized while receiving radiation therapy - this decision is at the Investigator's discretion.
  8. Patients who have undergone neoadjuvant chemotherapy are eligible.

  9. No prior treatment with Femara.

Exclusion criteria:

  1. Patients with any clinical or radiological evidence of distant spread of their disease at any point before randomization.
  2. Patients with clinical or radiological evidence of existing fracture in the lumbar spine and/or total hip.
  3. Patients with a history of fracture with low-intensity or no associated trauma.
  4. Patients who have started adjuvant hormonal therapy or who have completed adjuvant hormonal therapy prior to randomization.
  5. Patients who have received any endocrine therapy within the past 12 months (other than neoadjuvant tamoxifen or toremifene, insulin and/or oral anti-diabetic medications, and thyroid hormone replacement). Hormone replacement therapy must be discontinued prior to randomization.
  6. Patients who have received prior treatment with intravenous bisphosphonates within the past 12 months.
  7. Patients currently receiving oral bisphosphonates. Oral bisphosphonates must be discontinued within 3 weeks of baseline evaluations.
  8. Patients who have received prior treatment with systemic corticosteroids within the past 12 months (short term corticosteroid therapy, e.g. to prevent/treat chemotherapy-induced nausea/vomiting, is acceptable).
  9. Patients with prior exposure to anabolic steroids or growth hormone within the past 6 months.
  10. Patients with prior use of Tibolone within the last 6 months.
  11. Any prior use of PTH for more than 1 week.
  12. Prior use of systemic sodium fluoride for > 3 months during the past 2 years.
  13. Patients currently treated with any drugs known to affect the skeleton (e.g., calcitonin, mithramycin, or gallium nitrate) within 2 weeks prior to randomization.
  14. Patients with previous or concomitant malignancy (not breast cancer) within the past 5 years EXCEPT adequately treated basal or squamous cell carcinoma of the skin or in situ carcinoma of the cervix. Patients who have had a previous other malignancy must have been disease free for five years.
  15. Patients with other non-malignant systemic diseases including uncontrolled infections, uncontrolled type 2 diabetes mellitus, uncontrolled thyroid dysfunction, cardiovascular, renal, hepatic, and lung diseases which would prevent prolonged follow-up. Patients with previous history of thrombosis or thromboembolism can be included only if medically suitable. Patients with a known history of HIV are excluded.
  16. Uncontrolled seizure disorders associated with falls.
  17. Patients with abnormal renal function as evidenced by a serum creatinine equal to or greater than 3 mg/dL (265.2 mmol/L).
  18. History of diseases with influence on bone metabolism, such as Paget's disease, Osteogenesis Imperfecta, and primary or secondary hyperthyroidism within 12 months prior to study entry.
  19. Patients with baseline lumber spine or total hip BMD T-score below -2.0 SD.
  20. Patients treated with systemic investigational drug(s) and/or device(s) within the past 30 days or topical investigational drugs within the past 7 days.

Additional

Exclusion Criteria

(for Spine DXA)

  • History of surgery at the lumbosacral spine, with or without implantable devices.
  • Scoliosis with a Cobb angle >15 degree at the lumbar spine.
  • Immobility, hyperostosis or sclerotic changes at the lumbar spine, or evidence of sclerotic abdominal aorta sufficient to interfere with DXA scan.
  • Any disease of the spine that would preclude the proper acquisition of a lumbar spine DXA.

Additional protocol-defined inclusion/exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Zoledronic Acid upfrontZoledronic AcidParticipants in the upfront arm received zoledronate 4 mg i.v. on Day 1 and every 6 months until disease progression (recurrence) or the end of study. Participants also received Letrozole 2.5 daily plus calcium (1000-1200 mg) and vitamin D (400-800 IU) daily.
Zoledronate delayed-startZoledronic AcidIn lieu of a placebo arm, which was considered unethical for this trial, a delayed start arm was used. Participants who met certain clinical criteria indicating risk of lumbar spine or total hip fracture, or experienced clinical fracture unrelated to trauma or any asymptomatic fracture discovered at the Month 36 scheduled visit, were started on zoledronate 4 mg i.v. and for every 6 months until disease progression (recurrence) or end of study. Participants also received Letrozole 2.5 daily plus calcium (1000-1200 mg) and vitamin D (400-800 IU) daily.
Zoledronic Acid upfrontLetrozoleParticipants in the upfront arm received zoledronate 4 mg i.v. on Day 1 and every 6 months until disease progression (recurrence) or the end of study. Participants also received Letrozole 2.5 daily plus calcium (1000-1200 mg) and vitamin D (400-800 IU) daily.
Zoledronate delayed-startLetrozoleIn lieu of a placebo arm, which was considered unethical for this trial, a delayed start arm was used. Participants who met certain clinical criteria indicating risk of lumbar spine or total hip fracture, or experienced clinical fracture unrelated to trauma or any asymptomatic fracture discovered at the Month 36 scheduled visit, were started on zoledronate 4 mg i.v. and for every 6 months until disease progression (recurrence) or end of study. Participants also received Letrozole 2.5 daily plus calcium (1000-1200 mg) and vitamin D (400-800 IU) daily.
Primary Outcome Measures
NameTimeMethod
Percent Change From Baseline in Lumbar Spine (L1-L4) Bone Mineral Density (BMD)Baseline, 12 months

Bone mineral density (BMD) measurements were assessed by dual energy x-ray absorptiometry (DXA). The DXA devices of participating sites were cross-calibrated and the DXA results were compiled and analyzed by a central reader. Percent change = 100\*((BMD at Month 12 - Baseline BMD)/Baseline BMD)). Missing data at month 12 were imputed by using the last observation carried forward (LOCF) method. Post-baseline non-missing data from month 6 were carried forward to month 12. Data prior to month 6 were not carried forward.

Secondary Outcome Measures
NameTimeMethod
Percent Change From Baseline in Biochemical Markers of Bone Turnover, Serum N-Telopeptide (sNTX) and Bone-specific Alkaline Phosphatase (BSAP)Baseline, 12 months, 2 years, 3 years, 5 years

Blood samples from a subset of participants (231 participants in total) were collected to measure the sNTX and BSAP. Missing data at month 12 were imputed by using the LOCF method. Post-baseline non-missing data from months 6 and 9 were carried forward to month 12. Data prior to month 6 were not carried forward. Missing data beyond month 12 were not imputed by LOCF.

Incidence Rate of All Clinical Fractures3 years

The number of participants who experienced a clinical fracture at month 36 was assessed. Initial x-ray (both AP and lateral views) of the lumbar and thoracic spine were performed at baseline to exclude participants with evidence of fracture. In addition, repeated bone scan and/or x-ray were performed at the Principal Investigator's discretion during the course of the study to confirm evidence of clinical fracture, or at month 36 if there was no evidence of clinical fracture (lumbar and thoracic spine - lateral view). X-ray films were sent to a central reader.

Time to Disease Recurrence/Relapseover 5 years

The median time to disease progression was assessed by Kaplan-Meier analysis. The Principal Investigator assessed each participant for disease recurrence at each visit. Further testing was performed at the discretion of the Principal Investigator and as clinically indicated. Disease progression was defined as chest wall and/or regional recurrence confirmed by positive cytology or biopsy, and/or distance recurrence of the 1) skin, subcutaneous tissue, and lymph nodes (other than local or regional), 2) bone marrow, 3) lung, 4) skeleton 5) liver and 6) central nervous system confirmed by positive cytology, biopsy, aspirate or radiology as appropriate.

Percent Change From Baseline in Lumbar Spine (L1-L4) BMDBaseline, 2 years, 3 years, 5 years

Bone mineral density (BMD) measurements were assessed by dual energy x-ray absorptiometry (DXA). The DXA devices of participating sites were cross-calibrated and the DXA results were compiled and analyzed by a central reader.

Percent change = 100\*((BMD at Time Frame - Baseline BMD)/Baseline BMD)). Missing data beyond month 12 were not imputed by LOCF.

Percent Change From Baseline in Total Hip BMDBaseline, 12 months, 2 years, 3 years, 5 years

Bone mineral density (BMD) measurements were assessed by dual energy x-ray absorptiometry (DXA). The DXA devices of participating sites were cross-calibrated and the DXA results were compiled and analyzed by a central reader.

Percent change = 100\*((BMD at Time Frame - Baseline BMD)/Baseline BMD)). Missing data at month 12 were imputed by using the LOCF method. Post-baseline non-missing data from month 6 were carried forward to month 12. Data prior to month 6 were not carried forward.

Rate of Change From Baseline in Lumbar Spine (L1-L4) BMDBaseline, 5 years

The rate of change from baseline in BMD was assessed.

Rate of Change From Baseline in Total Hip BMDBaseline, 5 years

The rate of change from baseline in BMD was assessed.

Trial Locations

Locations (44)

FL Community Cancer Center

🇺🇸

Brooksville, Florida, United States

Eastern Connecticut Hematology/Oncology Associates

🇺🇸

Norwich, Connecticut, United States

Elmhurst Memorial Hospital

🇺🇸

Elhurst, Illinois, United States

Metro Minnesota CCOP

🇺🇸

St. Louis Park, Minnesota, United States

Virginia Physicians, Inc.- Oncology

🇺🇸

Richmond, Virginia, United States

Ocala Oncology Center

🇺🇸

Ocala, Florida, United States

Highlands Oncology Group

🇺🇸

Springdale, Arkansas, United States

Wilshire Oncology Medical Group

🇺🇸

LaVerne, California, United States

Cancer and Blood Institute of the Desert

🇺🇸

Rancho Mirage, Colorado, United States

Pacific Shores Medical Group

🇺🇸

Long Beach, California, United States

Space Coast Medical

🇺🇸

Titusville, Florida, United States

Northern Virginia Oncology Group

🇺🇸

Fairfax, Virginia, United States

Cook Research Department at Spectrum Health

🇺🇸

Grand Rapids, Michigan, United States

New Mexico Oncology Hematology, Ltd.

🇺🇸

Albuquerque, New Mexico, United States

Redwood Regional Medical Group

🇺🇸

Santa Rosa, California, United States

Pasco Pinellas Cancer Center

🇺🇸

New Port Richey, Florida, United States

St. Joseph Regional Cancer Center

🇺🇸

Bryan, Texas, United States

Hemoncare PC

🇺🇸

Brooklyn, New York, United States

Frederick Memorial Hospital Regional Cancer Therapy Center

🇺🇸

Frederick, Maryland, United States

Hematology-Oncology Associates of Northern NJ

🇺🇸

Morristown, New Jersey, United States

Dayton Clinical Oncology Program

🇺🇸

Dayton, Ohio, United States

Robert R. Carroll, MD, PA

🇺🇸

Gainesville, Florida, United States

Rockwood Clinic, PS

🇺🇸

Spokane, Washington, United States

New England Hematology/Oncology Associates

🇺🇸

Wellesley, Massachusetts, United States

East Valley Hematology & Oncology

🇺🇸

Burbank, California, United States

Louisiana Oncology Associates

🇺🇸

Lafayette, California, United States

Clinical Trials & Research Associates, Inc.

🇺🇸

Montebello, California, United States

Oncology Hematology Group of South Florida

🇺🇸

Miami, Florida, United States

Cancer Specialists of South Texas

🇺🇸

Corpus Christi, Texas, United States

Cancer Research Network, Inc.

🇺🇸

Plantation, Florida, United States

Odyssey Research Services

🇺🇸

Bismarck, North Dakota, United States

Nashat Y. Gabrail MD Inc.

🇺🇸

Canton, Ohio, United States

Swedish Cancer Institute

🇺🇸

Seattle, Washington, United States

Oncology Partners Network

🇺🇸

Cincinnati, Ohio, United States

Physician Associates, Inc.

🇺🇸

Cincinnati, Ohio, United States

University of Pittsburgh Cancer Institute/Magee Womens Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Center for Oncology Research & Tx. PA

🇺🇸

Dallas, Texas, United States

Hematology-Oncology Centers of the Northern Rockies, PC

🇺🇸

Billings, Montana, United States

VA Medical Center

🇵🇷

San Juan, Puerto Rico

Bay Area Oncology

🇺🇸

Tampa, Florida, United States

Charleston Hematology Oncology

🇺🇸

Charleston, South Carolina, United States

Kentuckiana Cancer Institute

🇺🇸

Louisville, Kentucky, United States

Methodist Cancer Center

🇺🇸

Omaha, Nebraska, United States

The Sarah Cannon Cancer Center

🇺🇸

Nashville, Tennessee, United States

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