MedPath

FoxBioNet: ECV (Extracellular Vesicle) 004

Completed
Conditions
Parkinson Disease
Interventions
Procedure: Lumbar Puncture
Registration Number
NCT04603326
Lead Sponsor
Michael J. Fox Foundation for Parkinson's Research
Brief Summary

The goal of this study is to identify reliable markers of LRRK2 activity in human CSF.

Detailed Description

Specific aims of this project are:

Primary Objectives:

To evaluate each assay performance for its ability to detect LRRK2, its activity and/or the detection and activity of the pathways it impacts using a variety of different approaches (quantitative western blot, immunoassays and LC-MS). Assay performance will be assessed and those demonstrating high sensitivity and consistency will be considered for further development.

Secondary Objectives:

To assess the ability of the assay or a combination of assays to differentiate pathogenic LRRK2 variant manifesting and non-manifesting carriers, idiopathic PD and healthy non-carriers.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
140
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
Non-manifesting LRRK2 mutation carriersLumbar PuncturePatients must have confirmed LRRK2 G2019S mutation Age 30 years or older at date of informed consent.
LRRK2 Parkinson Disease (PD) Participants:Lumbar PuncturePatients must have confirmed LRRK2 G2019S mutation Patients must meet the MDS criteria for Parkinson's disease Disease duration: any Age 30 years or older at time of PD diagnosis.
Idiopathic PD (iPD) Particpants:Lumbar PuncturePatients must meet the MDS criteria for Parkinson's disease. Disease duration: any Age 30 years or older at time of PD diagnosis.
Control (C) Participants:Lumbar PunctureAge 30 years or older at date of informed consent.
Primary Outcome Measures
NameTimeMethod
Assay Evaluation1 year

Evaluate each assay performance for ability to detect LRRK2, its activity and/or the detection and activity of the pathways it impacts using a variety of different approaches (quantitative western blot, immunoassays and LC-MS).

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (4)

Northwestern University

🇺🇸

Chicago, Illinois, United States

Oregon Health Sciences Univeristy

🇺🇸

Portland, Oregon, United States

The Trustees of the University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

The Trustees of Columbia University

🇺🇸

New York, New York, United States

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