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Post Marketing Study of emizibumab in hemophilia A pedicatric patients less than 12 years without FVIII Inhibitors(AOZORA)

Phase 4
Completed
Conditions
Hemophilia A
Registration Number
jRCT1080224629
Lead Sponsor
Chugai Pharmaceutical Co., Ltd.
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
completed
Sex
All
Target Recruitment
30
Inclusion Criteria

(1) Aged <12 years at the time of informed consent (2) Body weight >3 kg at the time of informed consent (3) Diagnosis of severe (endogenous FVIII level <1%) congenital hemophilia A (4) Negative results for FVIII inhibitors (<0.6 BU/mL) in the most recent assay within 8 weeks prior to enrollment

Exclusion Criteria

(1) Inherited or acquired bleeding disorder other than hemophilia A (2) Current receipt of immune tolerance induction (ITI) therapy (3) Previous (within the past 12 months) or current treatment for thromboembolic disease (except patients with previous catheter-associated thrombus who are not currently receiving treatment) or signs of thromboembolic disease

Study & Design

Study Type
Interventional
Study Design
a multicenter, open-label, single-arm
Primary Outcome Measures
NameTimeMethod
-

safety

exploratory

Observation, Laboratory tests

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Japan

Location not specified

Japan

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