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Donor Mesenchymal Stem Cell Infusion in Treating Patients With Acute or Chronic Graft-Versus-Host Disease After Undergoing a Donor Stem Cell Transplant

Phase 1
Completed
Conditions
Cancer
Registration Number
NCT00361049
Lead Sponsor
Case Comprehensive Cancer Center
Brief Summary

RATIONALE: Donor mesenchymal stem cell infusion may be an effective treatment for acute or chronic graft-versus-host disease caused by a donor stem cell transplant.

PURPOSE: This phase I trial is studying the side effects and best dose of donor mesenchymal stem cells in treating patients with acute or chronic graft-versus-host disease after undergoing a donor stem cell transplant.

Detailed Description

OBJECTIVES:

Primary

* Determine the safety of donor mesenchymal stem cell (MSC) infusion in patients with acute or extensive chronic graft-vs-host disease (GVHD) after undergoing HLA-identical sibling donor stem cell transplant.

Secondary

* Describe the rates of complete and partial resolution of GVHD when MSCs are used in addition to the standard GVHD therapy.

* Determine inflammatory cytokine levels, lymphocyte subsets, and donor-reactive lymphocyte numbers in blood of patients with acute GVHD prior to therapy and at 7 and 14 days post-MSC therapy.

* Determine if donor MSCs engraft in tissues inflamed by GVHD in patients who have undergone gender-mismatched transplantation.

OUTLINE: This is a multicenter, dose-escalation study of donor mesenchymal stem cells (MSC).

Within 72 hours after the initiation of medical therapy (e.g., corticosteroids, cyclosporine) for graft-vs-host disease, patients undergo donor MSC infusion over 10-15 minutes.

Cohorts of 3-6 patients receive escalating doses of donor MSCs until the maximum tolerated dose (MTD) is determined. The MTD is defined as the dose preceding that at which 2 of 3 or 2 of 6 patients experience dose-limiting toxicity.

Blood samples are obtained periodically and examined by immunoenzyme techniques for mixed lymphocyte reaction (as a surrogate marker for alloreactivity) and cytokine levels (TH1 \[i.e., interleukin (IL)-2 and interferon-gamma\], TH2 \[i.e., IL-10 and IL-4\], and inflammatory cytokines \[i.e., tumor necrosis factor-alpha and IL-1\]). Tissue specimens are examined by CD45 immunohistochemistry and fluorescent in situ hybridization to detect hematopoietic and nonhematopoietic cells.

After completion of study treatment, patients are followed periodically for 1 year.

PROJECTED ACCRUAL: A total of 24 patients will be accrued for this study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
49
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
SafetyMonitored for 6 hours for infusion related toxicity. Temperature, blood pressure, pulse and O2 saturation will be measured at baseline and every 10 minutes x 2, every 30 minutes x 2, and every hour x 3.
Secondary Outcome Measures
NameTimeMethod
Complete and partial resolution of graft-vs-host disease (GVHD)Patients will be evaluated for clinical signs and symptoms of GVHD weekly for up to 28 days.
Cytokine levels, lymphocyte subsets, and donor-reactive lymphocyte numbers in patients with acute GVHDPre-transplant, at diagnosis, 7 and 14 days after MSC infusion

Trial Locations

Locations (8)

Geauga Regional Hospital

🇺🇸

Cleveland, Ohio, United States

Lake/University Ireland Cancer Center

🇺🇸

Cleveland, Ohio, United States

Ireland Cancer Center at University Hosptials Case Medical Center, Case Comprehensive Cancer Center

🇺🇸

Cleveland, Ohio, United States

UHHS Chagrin Highlands Medical Center

🇺🇸

Cleveland, Ohio, United States

Mercy Cancer Center at Mercy Medical Center

🇺🇸

Cleveland, Ohio, United States

Southwest General Health Center

🇺🇸

Cleveland, Ohio, United States

UHHS Westlake Medical Center

🇺🇸

Cleveland, Ohio, United States

University Suburban Health Center

🇺🇸

Cleveland, Ohio, United States

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