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A Phase 4 Safety and Efficacy Study to Evaluate Lesinurad 200 mg in Participants With Gout and Renal Impairment

Phase 4
Terminated
Conditions
Chronic Kidney Disease (CKD)
Gout
Interventions
Drug: XOI
Drug: Placebo
Drug: corticosteroids
Registration Number
NCT03226899
Lead Sponsor
Ironwood Pharmaceuticals, Inc.
Brief Summary

This study evaluates the safety and efficacy of lesinurad administered with an XOI versus a placebo plus an XOI in gout participants who have moderate renal impairment and who are not at target level of serum urate (sUA).

Detailed Description

This postmarketing study is a randomized, double-blind, placebo-controlled study to evaluate safety (with particular focus on renal and cardiovascular events) and efficacy of lesinurad 200 mg once daily (QD) in combination with an XOI for up to 24 months compared with XOI monotherapy, in participants with gout and moderate renal impairment who have not reached target sUA levels (\<6.0 mg/dL) on an XOI alone.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
242
Inclusion Criteria
  1. Subject is able to understand the study procedures, the risks involved, and willing to provide written informed consent before the first study related activity.
  2. Subject is willing to adhere to the protocol schedule.
  3. Subject is ≥ 18 years and ≤ 85 years of age.
  4. Subject has a diagnosis of gout.
  5. Subject has moderate renal impairment with estimated creatinine clearance (eCrCl; calculated by the Cockcroft-Gault formula using ideal body weight) 25.0 to ≤ 65.0 mL/min at Screening Visits 1 and 2 and an average eCrCl for both screening visits of 30.0 to < 60.0 mL/min.
  6. Subject has been taking an XOI as ULT indicated for the treatment of gout for at least 4 weeks prior to Screening at a stable, medically appropriate dose, as determined by the Investigator. The minimum dose of allopurinol is 200 mg daily, and the minimum dose of febuxostat is the lowest approved dose per the local product label.
  7. Subject has a serum uric acid level ≥ 6.0 mg/dL (357 µmol/L) at Screening Visits 1 and 2.
  8. Subject is male or female; females must not be pregnant or breastfeeding and females of childbearing potential must agree to use nonhormonal contraception during the Screening Period and while taking investigation product (IP).
  9. Subject has a body mass index < 45 kg/m^2.
Exclusion Criteria
  1. Subject had unstable angina, New York Heart Association class III or IV heart failure, myocardial infarction, or stroke within the last 6 months prior to randomization; or had a deep venous thrombosis within the previous 3 months prior to randomization.
  2. Subject has uncontrolled hypertension (defined as systolic pressure above 160 or diastolic pressure above 95 mm Hg at either Screening Visits 1 or 2).
  3. Subject has severe hepatic impairment (defined as Child-Pugh Class C) or is known human immunodeficiency virus (HIV) positive.
  4. Subject is a solid organ transplant recipient.
  5. Subject has a urine protein of 3+ or higher by dipstick by the central laboratory at Screening Visit 2.
  6. Subject has a history of glomerulonephritis.
  7. Subject is taking valpromide, progabide, valproic acid, or other known inhibitors of epoxide hydrolase, or subject is taking ranolazine, cyclosporine, azathioprine or mercaptopurine.
  8. Subject is receiving chronic treatment with more than 325 mg of salicylates per day.
  9. Subject is unable to initiate gout flare prophylaxis with colchicine or low-dose oral corticosteroids at Baseline.
  10. Subject is taking any other drug approved for use as a urate-lowering medication other than allopurinol or febuxostat (eg, pegloticase, probenecid, benzbromarone) within 4 weeks prior to Screening or during Screening.
  11. For subjects who will be taking colchicine for gout flare prophylaxis: Subject is taking, or anticipated to take during the first 6 months on study, moderate or strong Cytochrome P450 3A4 (CYP3A4) inhibitors (ie, verapamil or diltiazem, clarithromycin, and fluconazole; or grapefruit or grapefruit juice).
  12. Subject previously participated in a clinical study involving lesinurad (RDEA594) or verinurad (RDEA3170) and received active treatment or placebo, or has taken commercially-available lesinurad.
  13. Subject has a gout flare during the Screening Period.
  14. Subject is pregnant or breastfeeding.
  15. Subject consumes more than 14 drinks of alcohol per week (eg, 1 drink = 5 oz [150 mL] of wine, 12 oz [360 mL] of beer, or 1.5 oz [45 mL] of hard liquor).
  16. Subject has a history of malignancy and has been on active treatment within the previous 5 years prior to randomization with the exception of non-melanoma skin cancer, treated in situ Grade 1 cervical cancer, or treated ductal carcinoma in situ of the breast.
  17. Subject has been hospitalized (other than for elective surgery) or received intravenous contrast (eg, for computerized tomography (CT) scan or any angiography) within 1 month prior to Screening or during Screening.
  18. Subject has participated in a clinical trial within 8 weeks prior to Screening.
  19. Subject has any other medical or psychological condition, which in the opinion of the Investigator might create undue risk to the subject or interfere with the subject's ability to comply with the protocol requirements or to complete the study.
  20. The maximum number of subjects in the eCrCl stratification subgroup has been reached.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Lesinurad + XOIcolchicinelesinurad 200 mg oral tablet QD plus a stable, medically appropriate dose of an XOI
Placebo + XOIXOIplacebo tablet QD plus a stable, medically appropriate dose of an XOI
Lesinurad + XOILesinuradlesinurad 200 mg oral tablet QD plus a stable, medically appropriate dose of an XOI
Placebo + XOIPlaceboplacebo tablet QD plus a stable, medically appropriate dose of an XOI
Lesinurad + XOIXOIlesinurad 200 mg oral tablet QD plus a stable, medically appropriate dose of an XOI
Lesinurad + XOIcorticosteroidslesinurad 200 mg oral tablet QD plus a stable, medically appropriate dose of an XOI
Placebo + XOIcolchicineplacebo tablet QD plus a stable, medically appropriate dose of an XOI
Placebo + XOIcorticosteroidsplacebo tablet QD plus a stable, medically appropriate dose of an XOI
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Who Achieve Serum Urate (sUA) < 6.0 mg/dL at Month 6Month 6
Secondary Outcome Measures
NameTimeMethod
Percentage of Participants Who Achieve sUA < 6.0 mg/dL Over TimeBaseline, Months 1, 3, 6, 9, 12, 15, 18
Change From Baseline in sUA Over Time, Including the Last Value On and Off TreatmentBaseline, Months 1, 3, 6, 9, 12, 15, 18
Percent Change From Baseline in sUA Over Time, Including the Last Value On and Off TreatmentBaseline, Months 1, 3, 6, 9, 12, 15, 18
Change From Baseline in Estimated Creatinine Clearance (eCrCl) at Month 24Baseline, 24 months

The eCrCl was calculated by the Cockcroft-Gault formula using ideal body weight.

Percent Change From Baseline in eCrCl at Month 24Baseline, 24 months

The eCrCl was calculated by the Cockcroft-Gault formula using ideal body weight.

Change From Baseline in eCrCl Over the Study Period, Including the Last Value On and Off TreatmentBaseline, Months 1, 3, 6, 9, 12, 15, 18

The eCrCl was calculated by the Cockcroft-Gault formula using ideal body weight.

Percent Change From Baseline in eCrCl Over the Study Period, Including the Last Value On and Off TreatmentBaseline, Months 1, 3, 6, 9, 12, 15, 18

The eCrCl was calculated by the Cockcroft-Gault formula using ideal body weight.

Percentage of Participants With Serum Creatinine (sCr) Elevations (≥1.5 × Baseline) Over the Study Periodup to 18 months
Percentage of Participants Meeting Criteria (eg, Based on sCr or eCrCl Criteria) for Treatment Discontinuations Over the Study Periodup to 18 months

Kidney function was monitored throughout the study by measuring sCr and calculating eCrCl by Cockcroft-Gault formula using ideal body weight. Treatment discontinuations were required if a participant experienced an absolute sCr ≥4.0 mg/dL or an eCrCl \<20 mL/min (based on central laboratory results).

Percentage of Participants Renal-Related and Kidney Stone Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)From first dose of study drug through each participant's study duration, up to approximately 18 months.

Renal-related and kidney stone events were based on Medical Dictionary for Regulatory Activities (MedDRA) "Renal and Urinary Disorders" system organ classification. AEs that started on or after the first dose of study drug in this study, or those AEs with onset prior to the first dose of study drug but worsened after the first dose of study drug, were considered treatment emergent.

Percentage of Participants With Contributing Factors to Renal SAEs as Adjudicated by the Renal Event Adjudication Committee (REAC)From first dose of study drug through each participant's study duration, up to approximately 18 months.
Percentage of Participants With Cardiac Event Adjudication Committee (CEAC)-Adjudicated Major Adverse Cardiovascular Events (MACEs)From first dose of study drug through each participant's study duration, up to approximately 18 months.

MACEs are defined as Cardiovascular Death, Nonfatal Myocardial Infarction, and Nonfatal Stroke.

Incidence of CEAC-Adjudicated MACEs or Hospitalization for Unstable Angina (MACE+)From first dose of study drug through each participant's study duration, up to approximately 18 months.

MACEs are defined as Cardiovascular Death, Nonfatal Myocardial Infarction, and Nonfatal Stroke.

Trial Locations

Locations (116)

Four Rivers Clinical Research

🇺🇸

Paducah, Kentucky, United States

Southern Arizona VA Health Care System

🇺🇸

Tucson, Arizona, United States

Dr Lakatos Ferenc Belgyogyaszati-Kardiologiai Maganrendelo

🇭🇺

Békéscsaba, Hungary

Clinexpert Kft.

🇭🇺

Budapest, Hungary

DRC Gyogyszervizsgalo Kozpont Kft

🇭🇺

Balatonfüred, Hungary

Prywatny Gabinet Lekarski NZOZ Centrum Medyczne Aeskulap

🇵🇱

Radom, Poland

Centrum Terapii Wspolczesnej J. M. Jasnorzewska Spolka Komandytowo Akcyjna

🇵🇱

Łódź, Poland

BKS Research Kft.

🇭🇺

Hatvan, Hungary

Praktyka Lekarska Ewa Krzyzagorska

🇵🇱

Poznań, Poland

Centrum Medyczne K2J2

🇵🇱

Wołomin, Poland

Mentahaz Maganorvosi Kozpont (SMO)

🇭🇺

Székesfehérvár, Hungary

Medical Expert Kft.

🇭🇺

Veszprem, Hungary

Centrum Kliniczno Badawcze J. Brzezicki B. Gornikiewicz - Brzezicka Lekarze Sp. p.

🇵🇱

Elbląg, Poland

AppleTreeClinics Sp. z o.o.

🇵🇱

Łódź, Poland

Centrum Medyczne Pratia Warszawa

🇵🇱

Warszawa, Poland

Centrum Medyczne AMED Oddzial w Lodzi

🇵🇱

Łódź, Poland

Centrum Dializa Sp. z o.o. - Zyrardow

🇵🇱

Żyrardów, Poland

Samodzielny Publiczny ZOZ Uniwersytecki Szpital Kliniczny nr 1 im. Norberta Barlickiego Uniwersytetu Medycznego w Lodzi, Oddzial Kliniczny Nefrologii, Hipertensjologii i Transplantologii Nerek

🇵🇱

Łódź, Poland

Arthritis, Autoimmune, & Allergy LLC

🇺🇸

Daytona Beach, Florida, United States

The Kaufmann Clinic, Inc

🇺🇸

Atlanta, Georgia, United States

Rocky Mountain Diabetes and Osteoporosis Center PA

🇺🇸

Idaho Falls, Idaho, United States

Nephrology Specialists

🇺🇸

Merrillville, Indiana, United States

Clinical Trials Management, LLC - Northshore

🇺🇸

Covington, Louisiana, United States

Michigan Kidney Consultants

🇺🇸

Pontiac, Michigan, United States

CRC of Jackson, LLC

🇺🇸

Jackson, Mississippi, United States

Meridian Clinical Research - Norfolk, NE

🇺🇸

Norfolk, Nebraska, United States

Buffalo VA Medical Center

🇺🇸

Buffalo, New York, United States

PhysiqueMed Clinical Trials

🇺🇸

Greensboro, North Carolina, United States

DJL Clinical Research PLLC

🇺🇸

Charlotte, North Carolina, United States

Trial Management Associates, LLC

🇺🇸

Wilmington, North Carolina, United States

Prestige Clinical Research

🇺🇸

Franklin, Ohio, United States

University of Pennsylvania

🇺🇸

Philadelphia, Pennsylvania, United States

Piedmont Research Partners, LLC

🇺🇸

Fort Mill, South Carolina, United States

Knoxville Kidney Center, PLLC

🇺🇸

Knoxville, Tennessee, United States

Mountain View Clinical Research - Greer

🇺🇸

Greer, South Carolina, United States

P&I Clinical Research

🇺🇸

Lufkin, Texas, United States

FMC Science

🇺🇸

Lampasas, Texas, United States

3rd Coast Research Associates

🇺🇸

Victoria, Texas, United States

Spectrum Medical, Inc.

🇺🇸

Danville, Virginia, United States

Manassas Clinical Research Center

🇺🇸

Manassas, Virginia, United States

CCBR Czech Brno, s. r. o

🇨🇿

Brno, Czechia

Revmatologie MUDr. Bilkova s.r.o.

🇨🇿

Olomouc, Czechia

CCBR Clinical Research, Pardubice

🇨🇿

Pardubice, Czechia

DTTO Faculty Hospital Brno

🇨🇿

Brno, Czechia

CCBR Ostrava s.r.o.

🇨🇿

Ostrava, Czechia

MEDICAL PLUS, s.r.o. - Revmatologicka ambulance

🇨🇿

Uherske Hradiste, Czechia

Krajska zdravotni, a.s. - Masarykova nemocnice v Usti nad Labem, o.z.

🇨🇿

Usti nad Labem, Czechia

Nemocnice Znojmo p.o - Interni oddeleni

🇨🇿

Znojmo, Czechia

Bajai Szent Rokus Korhaz

🇭🇺

Baja, Hungary

PV - MEDICAL, s.r.o.

🇨🇿

Zlín, Czechia

Selye Janos Hospital - Rheumatology Department

🇭🇺

Komárom, Hungary

Allergo-Derm Bakos Kft.

🇭🇺

Szolnok, Hungary

Clinfan Ltd SMO

🇭🇺

Szekszárd, Hungary

Stacja Dializ Zyrardow

🇵🇱

Zyrardow, Zyrardo, Poland

B_Serwis Popenda Sp. J.

🇵🇱

Chorzów, Poland

MCBK s.c.

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Grodzisk Mazowiecki, Poland

Centrum Medyczne Pratia Krakow

🇵🇱

Kraków, Poland

NZOZ Praktyka Lekarza Rodzinnego Elzbieta Kelm

🇵🇱

Katowice, Poland

Alfa Specjalistyczne Gabinety Lekarskie Ewa Moroz

🇵🇱

Nowy Sącz, Poland

Centrum Medyczne Chodzki

🇵🇱

Lublin, Poland

LCC Medical Research Institute, LLC

🇺🇸

Miami, Florida, United States

Sterling Research Group, Ltd. - Auburn

🇺🇸

Cincinnati, Ohio, United States

Clinical Advancement Center, PLLC

🇺🇸

San Antonio, Texas, United States

Sterling Research Group, Ltd. - Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Discovery Alliance International Inc. d/b/a Tennessee Health Research Alliance LLC

🇺🇸

Nashville, Tennessee, United States

Nephrology Associates, P.C.

🇺🇸

Nashville, Tennessee, United States

Central Alabama Research

🇺🇸

Birmingham, Alabama, United States

Columbia Research Group, Inc.

🇺🇸

Portland, Oregon, United States

Medvin Clinical Research

🇺🇸

Covina, California, United States

Western Nephrology-Westminster

🇺🇸

Westminster, Colorado, United States

New England Research Associates, Llc

🇺🇸

Trumbull, Connecticut, United States

Inland Rheumatology Clinical Trials, Inc

🇺🇸

Upland, California, United States

Riverside Clinical Research

🇺🇸

Edgewater, Florida, United States

Eastern Research

🇺🇸

Hialeah, Florida, United States

San Marcus Research Clinic Inc

🇺🇸

Miami, Florida, United States

Clinical Investigation Specialists, Inc. - Gurnee

🇺🇸

Gurnee, Illinois, United States

Clinical Trials Management LLC - Southshore

🇺🇸

Metairie, Louisiana, United States

Arthritis and Diabetes Clinic

🇺🇸

Monroe, Louisiana, United States

Savin Medical Group

🇺🇸

Miami Lakes, Florida, United States

Ellipsis Group

🇺🇸

Atlanta, Georgia, United States

Kansas Nephrology Research Institute

🇺🇸

Wichita, Kansas, United States

Center for Arthritis & Osteoporosis

🇺🇸

Elizabethtown, Kentucky, United States

Ochsner Clinic Foundation

🇺🇸

Baton Rouge, Louisiana, United States

Ellipsis Research Group, LLC

🇺🇸

Brooklyn, New York, United States

Northwest Louisiana Nephrology

🇺🇸

Shreveport, Louisiana, United States

University of Massachusetts Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Winthrop University Hospital

🇺🇸

Mineola, New York, United States

Burke Primary Care

🇺🇸

Morganton, North Carolina, United States

Briggs Clinical Research, Inc.

🇺🇸

San Antonio, Texas, United States

CCBR Czech Prague s.r.o.

🇨🇿

Prague, Czechia

Vaszary Kolos Korhaz Esztergom - Reumatologiai osztaly

🇭🇺

Esztergom, Hungary

Malopolskie Centrum Medyczne

🇵🇱

Kraków, Poland

Centrum Zdrowia Metabolicznego Pawel Bogdanski

🇵🇱

Poznań, Poland

Kalocsai Szent Kereszt Korhaz

🇭🇺

Kalocsa, Hungary

CRU Hungary Kft.

🇭🇺

Miskolc, Hungary

Centrum Badan Klinicznych s.c.

🇵🇱

Poznań, Poland

KO - MED Centra Kliniczne Sp. z o.o., Osrodek Badan Klinicznych w Zamosciu

🇵🇱

Zamość, Poland

NZOZ All - Med Centrum Medyczne Specjalistyczne Gabinety Lekarskie Marcin Ogorek

🇵🇱

Łódź, Poland

Medvin Clinical Research - Whittier

🇺🇸

Whittier, California, United States

St. Clair Nephrology Research

🇺🇸

Roseville, Michigan, United States

REVMACLINIC s.r.o. - Revmatologicka ambulance

🇨🇿

Brno, Czechia

Northern California Research

🇺🇸

Sacramento, California, United States

Capital Nephrology Medical Group

🇺🇸

Sacramento, California, United States

Rheumatology Associates of Central Florida

🇺🇸

Orlando, Florida, United States

Omega Research Consultants, LLC

🇺🇸

Orlando, Florida, United States

BayCare Medical Group, Inc.

🇺🇸

Tampa, Florida, United States

Meridien Research - Tampa

🇺🇸

Tampa, Florida, United States

University of Michigan

🇺🇸

Ann Arbor, Michigan, United States

Low Country Rheumatology

🇺🇸

Charleston, South Carolina, United States

Clinical Research Partners, LLC

🇺🇸

Richmond, Virginia, United States

Florida Medical Research Institute

🇺🇸

Gainesville, Florida, United States

New Mexico Clinical Research & Osteoporosis Center Inc.

🇺🇸

Albuquerque, New Mexico, United States

VA Medical Center - Kansas City

🇺🇸

Kansas City, Missouri, United States

Northeast Clinical Research Center

🇺🇸

Bethlehem, Pennsylvania, United States

Altoona Center for Clinical Research

🇺🇸

Duncansville, Pennsylvania, United States

Rhode Island Hospital

🇺🇸

East Providence, Rhode Island, United States

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