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Combined Inhalational With Intravenous Amphotericin B Versus Intravenous Amphotericin B Alone for Pulmonary Mucormycosis

Phase 2
Completed
Conditions
Pulmonary Mucormycosis
Interventions
Drug: Intravenous liposomal amphotericin B alone
Drug: Inhaled amp B deoxycholate+intravenous liposomal amp B
Registration Number
NCT04502381
Lead Sponsor
Post Graduate Institute of Medical Education and Research, Chandigarh
Brief Summary

To assess the safety and feasibility of combined inhalational and intravenous amphotericin B therapy for the treatment of pulmonary mucormycosis. And compare the efficacy of combined therapy with that of intravenous amphotericin B alone.

Detailed Description

Pulmonary mucormycosis is a relatively a rare disease with a high mortality. The angioinvasion associated with mucormycosis prevents efficient drug delivery at the diseased site. Inhaled amphotericin B achieves drug levels in lung tissue and has been shown to be useful in several diseases including chronic pulmonary and allergic bronchopulmonary aspergillosis. Further inhaled forms of amphotericin B are associated with less nephrotoxicity and other systemic adverse effects. The role of inhaled amphotericin B in pulmonary mucormycosis has been previously demonstrated in murine models and anecdotal reports. The study hypothesis is that combined therapy with inhalational and intravenous amphotericin B is likely to result in better outcomes as compared with intravenous amphotericin B alone for treatment of pulmonary mucormycosis

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
30
Inclusion Criteria

Subjects with a clinicoradiologic suspicion of pulmonary mucormycosis will be enrolled if the diagnosis of mucormycosis is pathologically or microbiologically (smear showing aseptate hyphae, culture or molecular evidence showing Mucorales) confirmed. Cases of disseminated mucormycosis will be included, only if the pulmonary infection is confirmed pathologically or microbiologically from respiratory secretions or biopsy samples

Exclusion Criteria
  • Lack of informed consent
  • Hypersensitivity to amphotericin B or any component of the formulation
  • Pregnancy
  • High likelihood of death within 48 h of enrolment
  • Suspected pulmonary mucormycosis without histological or microbiologic proof

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Conventional armIntravenous liposomal amphotericin B aloneParticipants will receive treatment with only intravenous liposomal amphotericin B (3 to 5 mg/kg body weight)
Intervention armInhaled amp B deoxycholate+intravenous liposomal amp BThe study participants in the intervention arm will receive nebulization with amphotericin B deoxycholate (10 mg twice a day every alternate day, as described below) along with intravenous liposomal amphotericin B (3 to 5 mg/kg body weight)
Intervention armIntravenous liposomal amphotericin B aloneThe study participants in the intervention arm will receive nebulization with amphotericin B deoxycholate (10 mg twice a day every alternate day, as described below) along with intravenous liposomal amphotericin B (3 to 5 mg/kg body weight)
Primary Outcome Measures
NameTimeMethod
Overall response (clinical and radiological improvement) at the end of six weeks of start of therapy6 weeks after the start of therapy

Complete response: Survival and resolution of all attributable symptoms and signs of disease plus Resolution of radiological lesion(s); persistence of only a scar or postoperative changes can be equated with complete radiological response Partial response: Survival and improvement of attributable symptoms and signs of disease plus At least 25% reduction in diameter of radiological lesion OR In cases of radiological stabilization (defined as 0%-25% reduction in the diameter), resolution of all attributable symptoms and signs of fungal disease can be equated with a partial response Stable response: Survival and minor or no improvement in attributable symptoms and signs; plus Radiological stabilization (defined as 0%-25% reduction in diameter) Progression: Worsening clinical symptoms or signs plus New sites of disease or radiological worsening Death Complete and partial response will be called "success"

Adverse events related to therapytill 6 weeks from randomization (start of therapy)

Adverse events related to therapy (especially, incidence of bronchospasm and acute kidney injury)

Secondary Outcome Measures
NameTimeMethod
90 day mortality90 days from the date of randomization

Death due to any cause till 90 days of randomization

Proportion of subjects requiring discontinuation or modification of therapy due to adverse eventstill 6 weeks from randomization (start of therapy)

Number of participants withdrawing therapy in each arm, divided by the total number of patients in the same arm

In-hospital mortalityDuring hospital stay, approximately till 6 weeks from randomization (start of therapy)

Death due to any cause in-hospital

Trial Locations

Locations (1)

Post graduate Institute medical education and research

🇮🇳

Chandigarh, India

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