MedPath

A Trial to Compare Xifaxan to Vancomycin for the Treatment of Clostridium Difficile-Associated Diarrhea (CDAD)

Phase 3
Completed
Conditions
Clostridium Infections
Diarrhea
Interventions
Registration Number
NCT00269399
Lead Sponsor
Bausch Health Americas, Inc.
Brief Summary

The purpose of this study is to assess the treatment and safety of a 10-day course of rifaximin (Xifaxan) as compared to vancomycin for treatment of Clostridium difficile-associated diarrhea (CDAD).

Detailed Description

Clostridium difficile is a bacterium that proliferates when normal colonic flora have been altered, most commonly due to antibiotic use. Clostridium difficile is non-invasive and localized to the lumen of the colon. Once established, it produces 2 potent toxins, A and B. The principal reservoir for Clostridium difficile is the hospital environment, with the risk of acquiring Clostridium difficile increasing in direct proportion to the length of hospital stay.

Patients with CDAD typically present with profuse watery or mucoid diarrhea and cramping abdominal pain. Additional symptoms include fever, nausea, anorexia, malaise, and bloody stool. More severe cases may be complicated by dehydration, electrolyte disturbances, ileus, and peritonitis. Systemic manifestations may include prerenal azotemia, sepsis syndrome, and toxic colitis. White blood cell counts (WBCs) also may be markedly elevated with a shift to immature forms. Extreme presentation of fulminant colitis may require a colectomy and even result in death. Symptoms of CDAD may begin a few days after initiation of antibiotic therapy or up to 8 weeks after its discontinuation.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
237
Inclusion Criteria
  • Subject is 18 years of age or older, has acute diarrhea and at least 1 other sign of enteric infection present, such as fever, nausea/loss of appetite, vomiting, severe abdominal pain or discomfort.
  • Subject has a positive Clostridium difficile stool toxin assay at screening
Exclusion Criteria
  • Subject has had a previous episode of clinically diagnosed Clostridium difficile within the past 6 months.
  • Subject has chronic diseases associated with diarrhea (e.g., inflammatory bowel disease or diarrhea predominant irritable bowel syndrome [DIBS])
  • Subject has had any therapy with any agent administered for the treatment of Clostridium difficile prior to randomization.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Vancomycin Comparator ArmVancomycinvancomycin 125mg taken 4 times a day
Rifaximin Treatment ArmRifaximin (Xifaxan)rifaximin 400mg taken 3 times a day
Primary Outcome Measures
NameTimeMethod
Proportion of Participants Achieving Clinical Success, Where Clinical Success is Defined as Resolution or Improvement of Baseline Signs and Symptoms i.e., Abdominal Pain, Fever, Diarrhea.14 days

Resolution or improvement of baseline signs and symptoms was assessed as

* Absence of severe abdominal pain for 2 consecutive days at the test of cure (TOC) Visit (Day 14 +/-1);

* Absence of fever (\< 38°C/100.4°F) for 2 consecutive days at the TOC Visit; and

* 3 unformed (loose or watery) stools per day for at least 48 hours that was sustained through the TOC Visit.

Secondary Outcome Measures
NameTimeMethod
Proportion of Participants Recurrence-free of Clostridium Difficile-associated Diarrhea (CDAD), After Achieving Clinical Success42 days

Recurrence of CDAD was defined as diarrhea and a positive Clostridium difficile stool toxin assay that occurs after initial clinical success.

Trial Locations

Locations (63)

Newland Medical Association

🇺🇸

Southfield, Michigan, United States

University of Maryland

🇺🇸

Baltimore, Maryland, United States

Digestive Health Specialists, PA

🇺🇸

Tupelo, Mississippi, United States

East Carolina Gastroenterology, PA

🇺🇸

Jacksonville, North Carolina, United States

Baltimore VA Medical Center

🇺🇸

Baltimore, Maryland, United States

Center for Clinical Research at Washington County Hospital

🇺🇸

Hagerstown, Maryland, United States

Shah Associates

🇺🇸

Prince Frederick, Maryland, United States

The University of Chicago

🇺🇸

Chicago, Illinois, United States

Michael E. DeBakey VA Medical Center

🇺🇸

Houston, Texas, United States

Minneapolis VAMC

🇺🇸

Minneapolis, Minnesota, United States

Infectious Disease - Minneapolis Ltd.

🇺🇸

Minneapolis, Minnesota, United States

Kansas Medical Clinic

🇺🇸

Topeka, Kansas, United States

Mayo Clinic Scottsdale

🇺🇸

Scottsdale, Arizona, United States

Inland Empire Digestive & Liver Diseases

🇺🇸

Redlands, California, United States

Gastroenterology of the Rockies

🇺🇸

Longmont, Colorado, United States

Halifax Medical Center

🇺🇸

Daytona Beach, Florida, United States

The George Washington University Medical Center

🇺🇸

Washington, District of Columbia, United States

Webster Surgical Center LLC

🇺🇸

Tallahassee, Florida, United States

Digestive Healthcare of Georgia

🇺🇸

Atlanta, Georgia, United States

Sky Blue, M.D.

🇺🇸

Boise, Idaho, United States

Southeast Regional Research Group

🇺🇸

Columbus, Georgia, United States

Gastroenterology, Ltd.

🇺🇸

Peoria, Illinois, United States

Howard Brown Health Center

🇺🇸

Chicago, Illinois, United States

Carle Clinic Association NCW5

🇺🇸

Urbana, Illinois, United States

Springfield Clinic

🇺🇸

Springfield, Illinois, United States

Memorial Medical Center

🇺🇸

Springfield, Illinois, United States

Iowa Digestive Disease Center, PC

🇺🇸

Des Moines, Iowa, United States

GI Specialists

🇺🇸

Olathe, Kansas, United States

Gastrointestinal Associates

🇺🇸

Overland Park, Kansas, United States

Chevy Chase Clinical Research

🇺🇸

Chevy Chase, Maryland, United States

Henry Ford Hospital

🇺🇸

Detroit, Michigan, United States

Arnold Markowitz, MD, PC

🇺🇸

Keego Harbor, Michigan, United States

Mayo Clinic Rochester

🇺🇸

Rochester, Minnesota, United States

Deaconess Billings Clinic Research

🇺🇸

Billings, Montana, United States

St. Michael's Medical Center

🇺🇸

Newark, New Jersey, United States

Infectious Diseases Associates, PC

🇺🇸

Omaha, Nebraska, United States

Drs. Scherl, Chessler, Zingler, Spinnel and Meininger

🇺🇸

Fort Lee, New Jersey, United States

Marlboro Gastroenterology PC

🇺🇸

Manalapan, New Jersey, United States

Institute for Clinical Research (ICR) at Holy Name Hospital

🇺🇸

Teaneck, New Jersey, United States

The Gastroenterology Group of South Jersey

🇺🇸

Vineland, New Jersey, United States

AMS Clinical Research

🇺🇸

Elmira, New York, United States

Brookdale University Hospital and Medical Center

🇺🇸

Brooklyn, New York, United States

North Shore Hepatology

🇺🇸

Manhasset, New York, United States

New York Medical College/Westchester Medical Center

🇺🇸

Valhalla, New York, United States

University of Rochester School of Medicine

🇺🇸

Rochester, New York, United States

Weill Medical College

🇺🇸

New York, New York, United States

Southern Gastroenterology Associates

🇺🇸

New Bern, North Carolina, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Lima Memorial Health System

🇺🇸

Lima, Ohio, United States

Regional Infectious Diseases - Infusion Center

🇺🇸

Lima, Ohio, United States

Lehigh Valley Hospital

🇺🇸

Allentown, Pennsylvania, United States

Drexel University College of Medicine

🇺🇸

Philadelphia, Pennsylvania, United States

RPS Infectious Diseases

🇺🇸

West Reading, Pennsylvania, United States

University Gastroenterology

🇺🇸

Providence, Rhode Island, United States

Digestive Disease Associates of Dallas

🇺🇸

Dallas, Texas, United States

University of Texas Health Sciences Center

🇺🇸

Houston, Texas, United States

Associated Physicians, LLP

🇺🇸

Madison, Wisconsin, United States

Infectious Disease Associates of Central Virginia

🇺🇸

Lynchburg, Virginia, United States

North Pacific Clinical Research

🇺🇸

Redmond, Washington, United States

St. Mary's/Duluth Clinic Health System

🇺🇸

Duluth, Minnesota, United States

Connecticut Gastroenterology Institute

🇺🇸

Bristol, Connecticut, United States

Advanced Medical Research Center

🇺🇸

Port Orange, Florida, United States

Dartmouth Hitchcock Medical Center

🇺🇸

Lebanon, New Hampshire, United States

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