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Combination Chemotherapy, Donor Stem Cell Transplant, Tacrolimus, Mycophenolate Mofetil, and Cyclophosphamide in Treating Patients With Hematologic Cancer

Phase 2
Completed
Conditions
Lymphoma
Leukemia
Myelodysplastic Syndromes
Interventions
Procedure: allogeneic hematopoietic stem cell transplantation
Procedure: peripheral blood stem cell transplantation
Registration Number
NCT00782379
Lead Sponsor
Northside Hospital, Inc.
Brief Summary

RATIONALE: Giving chemotherapy, such as fludarabine, busulfan, and cyclophosphamide, before a donor peripheral blood stem cell transplant helps stop the growth of cancer cells and helps stop the patient's immune system from rejecting the donor's stem cells. When the healthy stem cells from a donor are infused into the patient they may help the patient's bone marrow make stem cells, red blood cells, white blood cells, and platelets. Sometimes the transplanted cells from a donor can make an immune response against the body's normal cells. Giving high-dose cyclophosphamide together with tacrolimus and mycophenolate mofetil after transplant may stop this from happening.

PURPOSE: This phase II trial is studying how well combination chemotherapy works when given together with a donor stem cell transplant, followed by tacrolimus, mycophenolate mofetil, and high-dose cyclophosphamide, in treating patients with high-risk hematologic cancer.

Detailed Description

OBJECTIVES:

Primary

* To estimate the incidence of graft rejection and severe graft-versus-host disease after myeloablative HLA-mismatched peripheral blood stem cell transplantation (PBSCT) from first-degree relatives in patients with high-risk hematologic malignancies.

Secondary

* To estimate overall survival, relapse, non-relapse mortality, and event-free survival in these patients.

* To characterize additional hematologic and non-hematologic toxicities of myeloablative haploidentical PBSCT.

* To characterize donor hematopoietic chimerism in peripheral blood stem cells after PBSCT.

OUTLINE:

* Preparative regimen: Patients receive fludarabine phosphate IV over 30 minutes on days -7 to -2, busulfan IV over 3 hours on days -7 to -4, and cyclophosphamide IV over 1-2 hours on days -3 and -2.

* Allogeneic peripheral blood stem cell transplantation (PBSCT): Patients undergo infusion of unmanipulated peripheral blood stem cells on day 0.

* Post-transplant regimen: Patients receive high-dose cyclophosphamide IV over 1-2 hours on days 3 and 4, tacrolimus IV over 24 hours or orally twice daily on days 5-180, and oral mycophenolate mofetil 3 times daily on days 5-34 followed by a taper to day 90. Treatment continues in the absence of disease progression or clinically significant graft-vs-host disease.

After completion of PBSCT, patients are followed periodically for 1 year.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
20
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Myeloablative Haploidentical Transplantallogeneic hematopoietic stem cell transplantationAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical Transplantperipheral blood stem cell transplantationAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical TransplantbusulfanAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical TransplantcyclophosphamideAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical TransplanttacrolimusAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical Transplantfludarabine phosphateAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Myeloablative Haploidentical Transplantmycophenolate mofetilAll patients will receive treatment using Fludarabine, Busulfan and Cyclophosphamide prior to receiving a haploidentical transplant followed by post-transplant cyclosphosphamide.
Primary Outcome Measures
NameTimeMethod
Incidence of Graft Rejection for Patients at Day 100Day 100

Number of patients who experienced graft rejection by Day 100

Number of Patients Who Experienced Severe Graft-versus-host Disease (GVHD)(Grade 3 or 4)Day 100

Number of patients who experienced post-transplant complication (GVHD) as seen by clinical evidence

Secondary Outcome Measures
NameTimeMethod
Overall Survival at Day 100Day 100

Overall survival is assessed, without regard to disease status, post-transplant, at Day 100.

Non-relapse Mortality at 1 Year After Peripheral Blood Stem Cell Transplantation (PBSCT)1 year

Non-relapse mortality refers to whether a patient dies of causes related to something other than the primary disease.

Achievement of >90% (Full) Donor Chimerism in the T-Cell Lineage as Measured by PCR at Day 30 Post-transplantationDay 30

Chimerism analysis of peripheral blood mononuclear cells using PCR (polymerase chain reaction) for STR/VNTR (short tandme repeat/variable number tandem repeat) will be performed post transplant. On each occasion, the peripheral blood will be separated into the T-cell component (using e.g. CD3 selection) and the myeloid component (using e.g.CD14/15 selection) before assessment of chimerism.

Non-relapse Mortality at Day 100 After Peripheral Blood Stem Cell Transplantation (PBSCT)Day 100
Achievement of >90% (Full) Donor Chimerism in the T-Cell Lineage as Measured by PCR at Day 60 Post-transplantationDay 60

Chimerism analysis of peripheral blood mononuclear cells using PCR for STR/VNTR will be performed post transplant. On each occasion, the peripheral blood will be separated into the T-cell component (using e.g. CD3 selection) and the myeloid component (using e.g.CD14/15 selection) before assessment of chimerism.

Achievement of >90% (Full) Donor Chimerism in the T-Cell Lineage as Measured by PCR at Day 90 Post-transplantationDay 90

Chimerism analysis of peripheral blood mononuclear cells using PCR for STR/VNTR will be performed post transplant. On each occasion, the peripheral blood will be separated into the T-cell component (using e.g. CD3 selection) and the myeloid component (using e.g.CD14/15 selection) before assessment of chimerism.

Overall Survival at 12 Months12 months

Overall survival, defined as a patient being alive after transplant, is without regard to disease status.

Disease Free Survival at 12 Months12 months

Disease free survival refers to patients with no evidence of disease after transplant, at the 12 month time point.

Disease Free Survival at Day 100Day 100

Disease free survival refers to patients with no evidence of disease after transplant, at the Day 100 time point.

Trial Locations

Locations (1)

Blood and Marrow Transplant Group of Georgia

🇺🇸

Atlanta, Georgia, United States

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