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Efficacy Study of Granulocytapheresis Plus Steroids vs Steroids Alone in Active Steroid Dependant Ulcerative Colitis

Phase 4
Terminated
Conditions
Ulcerative Colitis
Interventions
Device: Granulocyte Monocyte Apheresis (GMA-Apheresis)
Registration Number
NCT00702611
Lead Sponsor
Grupo Espanol de Trabajo en Enfermedad de Crohn y Colitis Ulcerosa
Brief Summary

The purpose of this study is to evaluate the efficacy of the addition of GMA apheresis to steroid conventional treatment for achieving and maintaining remission in Active steroid dependant Ulcerative Colitis patients

Detailed Description

This is a multicenter randomized controlled trial which will compare the efficacy and safety of Adacolumn GMA apheresis plus oral steroids vs steroids alone in a strictly selected population of moderate to severe active steroid dependant Ulcerative Colitis patients.

Recruitment & Eligibility

Status
TERMINATED
Sex
All
Target Recruitment
133
Inclusion Criteria
  • 18 - 75 years old
  • Active ulcerative colitis with documented clinical symptoms and endoscopic findings
  • Active disease defined as DAI (Mayo score) ≥ 4 and ≤10 with at least 1 point in flexible sigmoidoscopy
  • Steroid dependency as defined by:

A. Inability to withdraw corticosteroids within three months of starting treatment, without recurrent active disease

B. appearance of relapse within 3 months after withdrawal of corticosteroids

  • Colonic involvement with ulcerative colitis beyond 15cm of the anal verge
  • Stable doses:A. Aminosalicylates for the last 4 weeks B. Prednisolone or equivalent dose ≤ 20 mg/day for the last 2 weeks C. Azathioprine or 6-mercaptopurine at stable dose for the last 12 weeks
  • Signed informed consent form
  • Agree to participate in the required follow-up visits
  • Able to complete the diary
Exclusion Criteria
  • Febrile (> 38ºC)
  • Evidence of toxic megacolon
  • Anticipated need for surgery within 24 weeks
  • Known obstructive diseases of the gastrointestinal system
  • Proctocolectomy, total colectomy, ileostomy, stoma or ileal pouch-anal anastomosis
  • A history of allergic reaction to heparin or heparin-induced thrombocytopenia
  • A history of hypersensitivity reaction associated with an apheresis procedure or intolerance of apheresis procedures
  • Requires a central venous access catheter for the apheresis treatments
  • Known infection with enteric pathogens, pathogenic ova or parasites, C. difficile toxin or CMV
  • Hypotension (systolic blood pressure <80 mmHg and/or diastolic blood pressure <50 mmHg) at screening visit only
  • Uncontrolled hypertension (systolic blood pressure >180 mmHg or diastolic blood pressure >120 mmHg) despite medical therapy
  • A history of myocardial infarction or unstable angina within the past 6 months
  • A history of coronary artery bypass grafting surgery or angioplasty within the past 6 months
  • Prosthetic heart valve, pacemaker or other permanent implant
  • Severe cardiovascular or peripheral vascular disease, severe renal disease
  • Liver disease defined as levels of SGOT [AST], SGPT [ALT] or alkaline phosphatase >2.5x the upper limit of the normal range for the laboratory performing test
  • History of cirrhosis
  • Known bleeding disorder (PT or PTT>1.5x the upper limit of the normal range for the laboratory performing the test), or concomitant anticoagulant therapy for purposes other than apheresis treatment
  • Prior history suggestive of a hypercoagulable disorder, including 1 or more episodes of pulmonary embolism or deep vein thrombosis
  • Known infection with Hepatitis B or C, or HIV
  • Abnormal hematology parameters defined as severe anemia with hemoglobin <8.5g/dL, white blood cell count of <3,500/μl and a granulocyte count < 2,000/μl
  • Fibrinogen level >700mg/dL
  • Major surgery within the past 6 months
  • Infection:Active infections less than 4 weeks from successful completion of antibiotic treatment for routine bacterial infectionFebrile viral infection within 4 weeks of entry into the clinical investigationLess than 12 weeks from conclusion of therapy for systemic fungal infections
  • Malignancy within the past 2 years other than surgically cured skin carcinoma or cervical dysplasia (CIN I-II)
  • History of dysplasia or carcinoma of the colon or lack of a complete colonoscopy in the last 12 months in patients with longstanding UC (> 10 años)
  • Current drug or alcohol abuse
  • Pregnant, lactating or planning to become pregnant during the course of the clinical investigation
  • Used within the last 30 days an investigational drug, biologic or device or 5 half-lifes, if known, for any investigational drug or biologic
  • Received cyclosporine or tacrolimus within the last 8 weeks
  • Received infliximab within the last 8 weeks
  • Fulminant ulcerative colitis

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
2Granulocyte Monocyte Apheresis (GMA-Apheresis)Treatment with starting dose of 40mg of oral prednisone per day at Week 00 for two weeks and tapered down to zero 5 mg/week within nine weeks
1Granulocyte Monocyte Apheresis (GMA-Apheresis)Seven apheresis treatments over seven consecutive weeks (1/week) in conjunction with a starting dose of 40mg of oral prednisone per day at Week 00 for two weeks which will be tapered down to zero 5 mg/week within nine weeks
Primary Outcome Measures
NameTimeMethod
Proportion of patients in steroid free clinical remission defined by Mayo Score less or equal to 2 with no individual subscore >1 at week 24week 24
Secondary Outcome Measures
NameTimeMethod
· Clinical response according to the activity indexes Truelove & Witts, Powell Tuc, Rachmiliewitz (Clinical Activity Index), Lichtiger (Modified Truelove & Witts Severity Index), Walmsley (Simple Clinical Colitis Index24 weeks
Steroid free remission (assessed by Mayo score)Week 12
Response at week 12 and 24 (defined by a decrease in Mayo Score > or = to 3 pointsweek 12 and week 24
Rescue therapy requirements (new courses of steroids, cyclosporine, infliximab, or surgery) during study period24 weeks
Time to relapse24 weeks
Clinical remission and response at weeks 12 and 24 analysed according to concomitant use of immunosupressants24 weeks
Adverse events24 weeks
Acute Phase reactants change at all lab analysis24 weeks

Trial Locations

Locations (48)

Hospital de Sao Bernardo

🇵🇹

Setubal, Portugal

Hospital Universitario de Bellvitge

🇪🇸

Hospitalet de Llobregat, Barcelona, Spain

Policlinico Universitario Tor Vergata

🇮🇹

Roma, Italy

Casa Sollievo della Sofferenza, Istituto di Ricovero e Cura a Carattere Scientifico, Opera di San Pio da Pietrelcina

🇮🇹

San Giovanni Rotondo, Italy

Ospedale di Belluno

🇮🇹

Belluno, Italy

Hospital Son Dureta

🇪🇸

Palma de Mallorca, Comunidad Balear, Spain

Hospital de Donostia

🇪🇸

San Sebastian, Guipuzcoa, Spain

Clínica Puerta de Hierro

🇪🇸

Madrid, Spain

Hospital da Universidade de Coimbra

🇵🇹

Coimbra, Portugal

Policlinico di Bari

🇮🇹

Bari, Italy

Azienda Ospedaliero-Universitaria di Careggi

🇮🇹

Firenze, Italy

Istituto Clinico Humanitas

🇮🇹

Rozzano, Italy

Hospital de Leon

🇪🇸

Leon, Spain

Hospital General Universitario de Alicante

🇪🇸

Alicante, Spain

Hospital Josep Trueta

🇪🇸

Girona, Spain

Hospital Geral Santo Antonio

🇵🇹

Porto, Portugal

Policlinico di Padova

🇮🇹

Padova, Italy

Markus-Krankenhaus

🇩🇪

Frankfurt, Germany

Complejo Hospitalario Reina Sofía

🇪🇸

Córdoba, Andalucía, Spain

Hospital Mutua de Terrassa

🇪🇸

Terrassa, Barcelona, Spain

Hospital Germans Trias i Pujol

🇪🇸

Badalona, Barcelona, Spain

Katolische Kliniken Ruhrhalbinsel

🇩🇪

Essen, Germany

Hospital de Galdakano

🇪🇸

Galdakao, Bilbao, Spain

Hospital Puerto de Sagunto

🇪🇸

Sagunto, Valencia, Spain

Complejo Universitario de Albacete

🇪🇸

Albacete, Spain

Hospital Insular de Las Palmas

🇪🇸

Las Palmas de Gran Canaria, Spain

Hospital Virgen de la Arrixaca

🇪🇸

Murcia, Spain

Complejo Hospitalario Universitario Juan Canalejo

🇪🇸

A Coruña, Galicia, Spain

Hospital de la Santa Creu i Sant Pau

🇪🇸

Barcelona, Spain

Hospital del Mar

🇪🇸

Barcelona, Spain

Hospital Fundación de Alcorcón

🇪🇸

Madrid, Spain

Hospital de Manises

🇪🇸

Valencia, Spain

Hospital do Meixoeiro

🇪🇸

Vigo, Spain

Medical University of Vienna

🇦🇹

Vienna, Austria

L'Azienda Unità Sanitaria Locale di Forlì

🇮🇹

Forli, Italy

Istituto Policlinico S. Donato

🇮🇹

Milan, Italy

Instituto Portuges Oncologia Lisboa Francisco Gentil

🇵🇹

Lisboa, Portugal

Hospital General de Elche

🇪🇸

Elche, Alicante, Spain

Hospital Clinic i Provincial

🇪🇸

Barcelona, Spain

Hospital Universitario Clínico de San Carlos

🇪🇸

Madrid, Spain

Hospital Costa del Sol

🇪🇸

Málaga, Spain

Hospital Universitario Virgen del Rocío

🇪🇸

Sevilla, Spain

Hospital de Sao Joao

🇵🇹

Porto, Portugal

Hospital Sao Teotonio

🇵🇹

Viseu, Portugal

Hospital Santa Maria

🇵🇹

Lisboa, Portugal

Complejo Hspitalario Universitario Santiago de Compostela

🇪🇸

Santiago de Compostela, A Coruña, Spain

Hospital de Navarra

🇪🇸

Pamplona, Navarra, Spain

Hospital Central de Asturias

🇪🇸

Oviedo, Asturias, Spain

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