"Natural History" Study of Choroideremia
- Conditions
- Choroideremia
- Interventions
- Other: Observation
- Registration Number
- NCT02994368
- Lead Sponsor
- 4D Molecular Therapeutics
- Brief Summary
The purpose of this study is to understand the rate of progression of all stages of choroideremia using a variety of assessments performed in the clinic including visual field measures, specialized photography of the eye and participant-reported visual problems
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- TERMINATED
- Sex
- Male
- Target Recruitment
- 57
Not provided
Not provided
Study & Design
- Study Type
- OBSERVATIONAL
- Study Design
- Not specified
- Arm && Interventions
Group Intervention Description Primary Cohort Observation No intervention Expansion Cohort Observation No intervention
- Primary Outcome Measures
Name Time Method Rate of progression of disease 4 years A variety of psychophysical, anatomical and image-based endpoints
- Secondary Outcome Measures
Name Time Method
Trial Locations
- Locations (4)
Retina Foundation of the Southwest
🇺🇸Dallas, Texas, United States
Baylor College of Medicine, Ophthalmology-Cullen Eye Center
🇺🇸Houston, Texas, United States
University of Alberta
🇨🇦Edmonton, Alberta, Canada
Moran Eye Center, University of Utah
🇺🇸Salt Lake City, Utah, United States