NL-OMON45750
Completed
Not Applicable
SELECTING OUTCOME MEASURES IN PAEDIATRIC MITOCHONDRIAL ENCEPHALOPATHY: A PILOT STUDY - SO-MITO encephalopathy
niversitair Medisch Centrum0 sites20 target enrollmentTBD
Overview
- Phase
- Not Applicable
- Intervention
- Not specified
- Conditions
- Not specified
- Sponsor
- niversitair Medisch Centrum
- Enrollment
- 20
- Status
- Completed
- Last Updated
- 2 years ago
Overview
Brief Summary
No summary available.
Investigators
Eligibility Criteria
Inclusion Criteria
- •\- Genetically confirmed mitochondrial disease
- •\- Encephalopathy (e.g. psychomotor retardation, epilepsy, abnormalities at neurological examination, etc).
Exclusion Criteria
- •\- The treating physician estimates that it is too burdensome for the patient to visit to participate in this study
- •\- Vision problems (\<50% sight)
Outcomes
Primary Outcomes
Not specified
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