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Expanded Access Use of Itacitinib to Treat a Single Patient With STAT1 Gain of Function (GOF) Disease

Conditions
STAT1 Gain-of-Function Disease
Registration Number
NCT05561985
Lead Sponsor
Incyte Corporation
Brief Summary

Expanded access use of Itacitinib to treat a single patient with aplastic anemia.

Detailed Description

Not available

Recruitment & Eligibility

Status
AVAILABLE
Sex
Not specified
Target Recruitment
Not specified
Inclusion Criteria
Exclusion Criteria

Study & Design

Study Type
EXPANDED_ACCESS
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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