MedPath

A Phase 2a Master Protocol Assessing Inebilizumab and Blinatumomab in Autoimmune Diseases

Phase 2
Not yet recruiting
Conditions
Systemic Lupus Erythematosus
Active Refractory Rheumatoid Arthritis
Interventions
Registration Number
NCT06570798
Lead Sponsor
Amgen
Brief Summary

The main objective is to assess the safety and tolerability of inebilizumab in adult participants with active and refractory systemic lupus erythematosus (SLE) with nephritis (Subprotocol A) and to assess the safety and tolerability of subcutaneous (SC) blinatumomab in adult participants with active and refractory (SLE) with nephritis (Subprotocol B) and in adult participants with active refractory rheumatoid arthritis (RA) (Subprotocol C).

Detailed Description

Not available

Recruitment & Eligibility

Status
NOT_YET_RECRUITING
Sex
All
Target Recruitment
110
Inclusion Criteria
  • Subprotocol A and B: Diagnosis of SLE and lupus nephritis (LN) according to 2019 European League Against Rheumatism and the American College of Rheumatology (ACR) classification criteria.

  • Subprotocol A and B: Participant must be positive for at least one of the following autoantibodies:

    1. Antinuclear antibodies (ANA) ≥ 1:80
    2. Anti-double stranded deoxyribonucleic acid (anti-dsDNA) antibodies elevated to above normal range as established by central laboratory (ie, positive results)
    3. Anti-Smith antibodies elevated to above normal (ie, positive results).
  • Subprotocol A and B: SLEDAI-2K ≥ 8.

  • Subprotocol A and B: Active, biopsy-proven, proliferative LN demonstrating class III or class IV with or without co-existing features of Class V LN according to 2018 International Society of Nephrology/Renal Pathology Society (ISN/RPS) criteria. Renal biopsy must have been performed within 6 months before enrollment. The local biopsy report will be used. A central review center will confirm the eligibility.

  • Subprotocol A and B: Inadequate response, for lack of efficacy or intolerance after 6 months to at least 1 therapy (Subprotocol A) or 2 therapies (Subprotocol B) at the maximally tolerated doses as recommended by the Kidney Disease: Improving Global Outcomes (KDIGO) guidelines (KDIGO, 2024). Inadequate response is defined as:

    1. UPCR ≥ 1.5 mg/mg
    2. Less than 50% of proteinuria improvement in the past 3 months.
  • Subprotocol C: Diagnosis of RA according to the 2010 ACR/ European Alliance of Associations for Rheumatology (EULAR) classification criteria.

  • Subprotocol C: Active disease defined as having all the following criteria:

    1. DAS28-CRP > 3.2 at screening
    2. at least 6 tender joints at screening
    3. at least 6 swollen joints at screening
  • Subprotocol C: Refractory disease defined as:

  • Moderate to severe active disease despite having received treatment with:

    1. at least 1 conventional synthetic disease-modifying antirheumatic drug (csDMARD), AND
    2. at least 2 biologic disease-modifying antirheumatic drugs (bDMARDs) of different mechanisms of action OR 1 bDMARD and at least 1 targeted synthetic disease-modifying antirheumatic drugs (tsDMARD).
  • Inadequate response or intolerance to csDMARDs, bDMARDs, and tsDMARDs should be defined as:

    1. Participant having active disease despite a minimum of 12 weeks of treatment with a csDMARD, bDMARD, or tsDMARD.
    2. Intolerance to treatment as defined by participant having experienced an adverse effect from treatment with a csDMARD, bDMARD, or tsDMARD.
Exclusion Criteria
  • Subprotocol A and B: Estimated glomerular filtration rate (eGFR) of < 45 mL per minute per 1.73 m^2 of body surface area (calculated using the Modification of Diet in Renal Disease [MDRD] formula, with screening laboratory results for serum creatinine value).
  • Subprotocol A and B: Significant likely irreversible organ damage related to SLE (eg, end-stage renal disease [ESRD]).
  • Subprotocol A and B: Any acute, severe lupus related flare during screening that needs immediate treatment.
  • Subprotocol A and B: A previous kidney transplant or planned transplant within study treatment period.
  • Subprotocol A and B: History of or current renal diseases (other than LN) that in the opinion of the investigator could interfere with the LN assessment and confound the disease activity assessment (eg, diabetic nephropathy).
  • Subprotocol A and B: Renal biopsy showing pure class V.
  • Subprotocol C: Prior history of current inflammatory joint disease other than RA including but not limited to systemic lupus erythematosus, mixed connective tissue disorder, scleroderma, polymyositis, or significant systemic involvement secondary to RA (eg, vasculitis, pulmonary fibrosis, or Felty's syndrome).
  • Subprotocol C: Functional Class IV as defined by the ACR classification of functional status in RA.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Subprotocol A: Inebilizumab 3 DosesInebilizumabParticipants will receive 3 doses of inebilizumab administered via an intravenous (IV) infusion.
Subprotocol A: Inebilizumab 4 DosesInebilizumabParticipants will receive 4 doses of inebilizumab administered via an IV infusion.
Subprotocol B: Blinatumomab Low-doseBlinatumomabParticipants will receive blinatumomab low-dose administered via SC injection.
Subprotocol B: Blinatumomab Medium-doseBlinatumomabParticipants will receive blinatumomab medium-dose administered via SC injection.
Subprotocol B: Blinatumomab High-doseBlinatumomabParticipants will receive blinatumomab high-dose administered via SC injection.
Subprotocol C: Blinatumomab Low-doseBlinatumomabParticipants will receive blinatumomab low-dose administered via SC injection.
Subprotocol C: Blinatumomab Medium-doseBlinatumomabParticipants will receive blinatumomab medium-dose administered via SC injection.
Subprotocol C: Blinatumomab High-doseBlinatumomabParticipants will receive blinatumomab high-dose administered via SC injection.
Primary Outcome Measures
NameTimeMethod
Number of Participants Who Experience a Treatment-emergent Adverse Event (TEAE)Day 1 to Week 52
Number of Participants Who Experience a Serious TEAEDay 1 to Week 52
Secondary Outcome Measures
NameTimeMethod
Subprotocol A and B: Number of Participants With a 24-hour Urine Protein-creatinine Ratio (UPCR) ≤ 0.5 mg/mgWeek 12 and Week 24
Subprotocol A: Number of Participants With Anti-inebilizumab Antibody FormationDay 1 to Week 52
Subprotocol C: Percentage of participants achieving Clinical Disease Activity Index (CDAI) ≤ 2.8Week 12 and Week 26
Subprotocol A and B: Percent Change From Baseline in UPCRBaseline, Week 12 and Week 24
Subprotocol A and B: Number of Participants With Remission in SLE as Defined by Definition of Remission in SLE (DORIS)Week 12 and Week 24
Subprotocol A and B: Number of Participants With a Lupus Low Disease Activity State (LLDAS)Week 12 and Week 24
Subprotocol A and B: Change From Baseline in SLE Activity Index-2000 (SLEDAI-2K) ScoreBaseline, Week 12 and Week 24
Subprotocol B and C: Cmax of BlinatumomabDay 1 to Week 12
Subprotocol A and B: Percent Change From Baseline in SLEDAI-2K ScoreBaseline, Week 12 and Week 24
Subprotocol A: Time to Cmax (tmax) of InebilizumabDay 1 to Week 52
Subprotocol A and B: Change From Baseline in UPCRBaseline, Week 12 and Week 24
Subprotocol A: Maximum Concentration (Cmax) of InebilizumabDay 1 to Week 52
Subprotocol A: Area Under the Concentration-time Curve (AUC) of InebilizumabDay 1 to Week 52
Subprotocol C: Percentage of participants achieving Disease Activity Score-28 Joint C-Reactive Protein (DAS28-CRP) < 2.6Week 12 and Week 26
Subprotocol B and C: tmax of BlinatumomabDay 1 to Week 12
Subprotocol B and C: AUC of BlinatumomabDay 1 to Week 12
Subprotocol B and C: Number of Participants With Anti-blinatumomab Antibody FormationDay 1 to Week 52
Subprotocol C: Percentage of participants achieving Simplified Disease Activity Index (SDAI) ≤ 3.3Week 12 and Week 26
Subprotocol C: Percentage of participants achieving American College of Rheumatology (ACR)20 responseWeek 12 and Week 26
Subprotocol C: Percentage of participants achieving ACR50 responseWeek 12 and Week 26
Subprotocol C: Percentage of participants achieving ACR70 responseWeek 12 and Week 26

Trial Locations

Locations (12)

Vitaly Clinical Research

🇺🇸

Miami, Florida, United States

Northwell Health

🇺🇸

Great Neck, New York, United States

Prolato Clinical Research Center

🇺🇸

Houston, Texas, United States

Centre Hospitalier Universitaire de Liege - Sart Tilman

🇧🇪

Liege, Belgium

Centre Hospitalier Universitaire de Lyon - Hopital Edouard Herriot

🇫🇷

Lyon Cédex 3, France

Centre Hospitalier Universitaire de Strasbourg - Nouvel Hopital Civil

🇫🇷

Strasbourg, France

Centre Hospitalier Universitaire de Toulouse - Hopital Rangueil

🇫🇷

Toulouse Cedex 9, France

Klinikum der LMU Muenchen

🇩🇪

Muenchen, Germany

IRCCS Ospedale San Raffaele

🇮🇹

Milano, Italy

IRCCS Istituto Clinico Humanitas

🇮🇹

Rozzano, Italy

Vida Research Center

🇺🇸

Hialeah, Florida, United States

Homestead Associates In Research Inc

🇺🇸

Homestead, Florida, United States

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