MedPath

Pediatric Philadelphia Positive Acute Lymphoblastic Leukemia

Phase 2
Completed
Conditions
Leukemia, Pediatric
Interventions
Registration Number
NCT01460160
Lead Sponsor
Bristol-Myers Squibb
Brief Summary

The purpose of this study is to determine whether Dasatinib when added to standard chemotherapy is effective and safe in the treatment of pediatric philadelphia chromosome positive acute lymphoblastic leukemia

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
106
Inclusion Criteria
  • Newly diagnosed Philadelphia chromosome positive Acute Lymphoblastic Leukemia (ALL)
  • Age >1 year and < less than 18 years old
  • Induction chemotherapy ≤ 14 days according to institutional standard of care
  • Adequate liver, renal and cardiac function
Exclusion Criteria
  • Prior treatment with a Oncogene fusion protein (BCR-ABL) inhibitor
  • Extramedullary involvement of the testicles
  • Active systemic bacterial, fungal or viral infection
  • Down syndrome

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Arm 1: DasatinibDasatinib-
Primary Outcome Measures
NameTimeMethod
3-year Event-free Survival (EFS) RateFrom first dose to 3 years following first dose

3-year EFS rate is defined as the percentage of participants without event after 3 years since the start of study treatment.

Events for EFS are defined as ANY first one of the following:

* Lack of complete response in bone marrow

* Relapse at any site

* Development of second malignant neoplasm

* Death from any cause

Secondary Outcome Measures
NameTimeMethod
Percentage of Participants Negative for Minimal Residual Disease (MRD)From first dose to End of Induction Period Ia (up to 5 weeks) or Ib (up to 9 weeks) or End of Consolidation Period (up to 22 weeks)

MRD was by real-time qPCR for clone-specific immunoglobulin and T-cell receptor gene rearrangements (IG/TCR). Participants were declared as MRD negative if the MRD level is undetectable providing the assay lower limit of quantification is at least 0.1%

Complete Remission RateFrom first dose to End of Induction Period Ia (up to 5 weeks) or Ib (up to 9 weeks) or End of Consolidation Period (up to 22 weeks)

Complete Remission rate is defined as the percentage of participants achieving a complete remission, i.e. \< 5% lymphoblasts in bone marrow and in CSF, with no evidence of other extramedullary disease. Complete remission will be assessed at the end of Induction IA, end of induction IB and end of the consolidation period for all treated participants.

Event-Free Survival (EFS) Rate (Kaplan-Meier Estimates)From first dose to 3 years or 5 years following first dose

Overall estimation of the EFS of dasatinib plus chemotherapy was performed utilizing the Kaplan-Meier (KM) Product Limit method. The 3-year and 5-year EFS rates were computed with the corresponding 95% CI's using Greenwood's formula. Analyses of EFS included KM plots with number of patients at risk. Participants who neither relapse nor die or who are lost to follow-up were censored on the date of their last bone marrow, CSF assessment or physical exam, whichever occurred last.

Percentage of Participants With BCR-ABL Mutations at Baseline and at Time of Disease Progression or RelapseAt baseline (prior to start of study treatment) and at disease progression or relapse (up to approximately 3 years)

A BCR-ABL mutation is defined as the presence of a detectable amino acid substitution in the ABL kinase domain, assessed by Real-time quantitative PCR.

Number of Participants Experiencing Adverse EventsFrom first dose to 100 days following last dose (up to approximately 23 months)

Number of participants experiencing different types of all causality all grade adverse events

Trial Locations

Locations (94)

University Of Arkansas For Medical Sciences

🇺🇸

Little Rock, Arkansas, United States

Miller Children's and Women Hospital

🇺🇸

Long Beach, California, United States

Mountain States Tumor Institute

🇺🇸

Boise, Idaho, United States

All Children'S Hospital

🇺🇸

Saint Petersburg, Florida, United States

Antranik Agop Bedros

🇺🇸

Loma Linda, California, United States

Children'S Hospital Of L.A.

🇺🇸

Los Angeles, California, United States

The Herbert Irving Pavilion

🇺🇸

New York, New York, United States

Southern California Permanente Medical Group

🇺🇸

Los Angeles, California, United States

Newark Beth Israel Medical Center

🇺🇸

Newark, New Jersey, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

The Cancer Institute Of New Jersey

🇺🇸

New Brunswick, New Jersey, United States

Michigan State University

🇺🇸

Lansing, Michigan, United States

New York University

🇺🇸

New York, New York, United States

Kaiser Medical Center

🇺🇸

Roseville, California, United States

University Of Missouri Health Care

🇺🇸

Columbia, Missouri, United States

A. I. Dupont Hospital For Children

🇺🇸

Wilmington, Delaware, United States

SUNY Upstate Medical University

🇺🇸

Syracuse, New York, United States

Helen Devos Children'S Hospital

🇺🇸

Grand Rapids, Michigan, United States

Johns Hopkins University

🇺🇸

Baltimore, Maryland, United States

Children'S Hospital Of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

St. Mary'S

🇺🇸

West Palm Beach, Florida, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Geisinger Medical Center

🇺🇸

Danville, Pennsylvania, United States

Ut Southwestern

🇺🇸

Dallas, Texas, United States

Levine Children's Hospital

🇺🇸

Charlotte, North Carolina, United States

St Vincent Hospital

🇺🇸

Green Bay, Wisconsin, United States

Nationwide Children'S Hospital

🇺🇸

Columbus, Ohio, United States

Goryeb Children'S Hospital

🇺🇸

Morristown, New Jersey, United States

The Children'S Medical Center Of Dayton

🇺🇸

Dayton, Ohio, United States

Children's Hospital Of Pittsburgh Of UPMC

🇺🇸

Pittsburgh, Pennsylvania, United States

Scott & White - McLane Children's Specialty Clinic

🇺🇸

Temple, Texas, United States

Alberta Children'S Hospital

🇨🇦

Calgary, Alberta, Canada

Mercy Children's Hospital

🇺🇸

Toledo, Ohio, United States

Cook Children'S Hem/Onc Center

🇺🇸

Fort Worth, Texas, United States

New York Presbyterian/Weill Cornell

🇺🇸

New York, New York, United States

Inova Pediatric Specialty Center Ii

🇺🇸

Fairfax, Virginia, United States

Driscoll Children'S Hospital

🇺🇸

Corpus Christi, Texas, United States

Penn State Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

Children'S Hosp-Kings Daughter

🇺🇸

Norfolk, Virginia, United States

East Tennessee Children'S Hosp

🇺🇸

Knoxville, Tennessee, United States

The Toledo Children'S Hospital

🇺🇸

Toledo, Ohio, United States

The Montreal Children's Hospital of the MUHC

🇨🇦

Montreal, Quebec, Canada

Chu Ste-Justine

🇨🇦

Montreal, Quebec, Canada

Children'S Hospital Of Eastern Ontario

🇨🇦

Ottawa, Ontario, Canada

Local Institution

🇬🇧

Cambridge, United Kingdom

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

James Whitcomb Riley Hospital For Children

🇺🇸

Indianapolis, Indiana, United States

Children'S Center For Cancer And Blood Diseases

🇺🇸

Indianapolis, Indiana, United States

Children'S Specialty Center Of Nevada

🇺🇸

Las Vegas, Nevada, United States

Cincinnati Children'S Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Texas Children'S Cancer Center

🇺🇸

Houston, Texas, United States

Seattle Children'S

🇺🇸

Seattle, Washington, United States

Childrens Hospitals And Clinics Of Minnesota

🇺🇸

Minneapolis, Minnesota, United States

Ucsf - Hematology/Oncology

🇺🇸

San Francisco, California, United States

Vanderbilt University

🇺🇸

Nashville, Tennessee, United States

Primary Children's Medical Center

🇺🇸

Salt Lake City, Utah, United States

University Of Alabama At Birmingham

🇺🇸

Birmingham, Alabama, United States

Children'S Hospital Of Michigan

🇺🇸

Detroit, Michigan, United States

University Of Oklahoma Health Sciences Center

🇺🇸

Oklahoma City, Oklahoma, United States

St. Joseph's Children's Hospital

🇺🇸

Tampa, Florida, United States

Legacy Emanuel Hospital & Health Center

🇺🇸

Portland, Oregon, United States

Oregon Health & Sci Univ

🇺🇸

Portland, Oregon, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Phoenix Children'S Hospital/Ctr. For Cancer & Blood Ctr.

🇺🇸

Phoenix, Arizona, United States

Valley Children's Hospital

🇺🇸

Madera, California, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

Lpch & Sumc

🇺🇸

Palo Alto, California, United States

Nemours Children'S Clinic

🇺🇸

Jacksonville, Florida, United States

Lee Memorial Health System

🇺🇸

Fort Myers, Florida, United States

Children's Healthcare Of Atlanta

🇺🇸

Atlanta, Georgia, United States

Ann & Robert H Lurie Children's Hospital Of Chicago

🇺🇸

Chicago, Illinois, United States

Southern Illinois University School Of Medicine

🇺🇸

Springfield, Illinois, United States

UMass Memorial Medical Center

🇺🇸

Worcester, Massachusetts, United States

Univ Of Mississippi Med Ctr

🇺🇸

Jackson, Mississippi, United States

St. Joseph's Regional Medical Center

🇺🇸

Paterson, New Jersey, United States

Washington University Medical Center

🇺🇸

Saint Louis, Missouri, United States

Children'S Hospital Colorado

🇺🇸

Aurora, Colorado, United States

Hackensack University Medical Center

🇺🇸

Hackensack, New Jersey, United States

Md Anderson Cancer Center Orlando

🇺🇸

Orlando, Florida, United States

Norton Children's Hospital

🇺🇸

Louisville, Kentucky, United States

Nemours Childrens Hospital

🇺🇸

Orlando, Florida, United States

Wake Forest University

🇺🇸

Winston-Salem, North Carolina, United States

Children'S Mercy Hospital And Clinics

🇺🇸

Kansas City, Missouri, United States

Children'S National Medical Center

🇺🇸

Washington, District of Columbia, United States

Sinai Hospital Of Baltimore

🇺🇸

Baltimore, Maryland, United States

New York Medical College

🇺🇸

Valhalla, New York, United States

University Of Florida

🇺🇸

Gainesville, Florida, United States

Kapiolani Medical Center For Women & Children

🇺🇸

Honolulu, Hawaii, United States

University Of Kentucky

🇺🇸

Lexington, Kentucky, United States

University Of New Mexico

🇺🇸

Albuquerque, New Mexico, United States

Dell Children'S Medical Center Of Central Texas

🇺🇸

Austin, Texas, United States

Kenneth Desantes, Md

🇺🇸

Madison, Wisconsin, United States

Stollery Children'S Hospital

🇨🇦

Edmonton, Alberta, Canada

Rhode Island Hospital

🇺🇸

Providence, Rhode Island, United States

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