MedPath

Phase 3 Study of Sofosbuvir and Ribavirin

Phase 3
Completed
Conditions
Hepatitis C
Interventions
Registration Number
NCT01497366
Lead Sponsor
Gilead Sciences
Brief Summary

This study was to assess the safety and efficacy of sofosbuvir (GS-7977; PSI-7977) in combination with ribavirin (RBV) administered for 12 weeks compared with pegylated interferon (PEG)/RBV administered for 24 weeks in treatment-naive patients with Hepatitis C (HCV) genotype 2 or 3. Efficacy was assessed by the rate of sustained viral response (SVR) 12 weeks after the discontinuation of therapy (SVR12). This was a non-inferiority study, and if non-inferiority was demonstrated, the study was then allowed to test for superiority.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
527
Inclusion Criteria
  • Chronic Genotype 2 or 3 HCV-infection
  • Naive to all HCV antiviral treatment(s)
Exclusion Criteria
  • Positive test at Screening for HBsAg, anti-hepatitis B core immunoglobulin M antibody (anti-HBc IgM Ab), or anti-HIV Ab
  • History of any other clinically significant chronic liver disease
  • A history consistent with decompensated liver disease
  • History or current evidence of psychiatric illness, immunologic disorder, hemoglobinopathy, pulmonary or cardiac disease, seizure disorder or anticonvulsant use, poorly controlled diabetes, cancer, or a history of malignancy, that makes the subject unsuitable for the study.
  • Participation in a clinical study within 3 months prior to first dose

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Sofosbuvir+RBVSofosbuvirParticipants were randomized to receive sofosbuvir+RBV for 12 weeks.
PEG+RBVPEGParticipants were randomized to receive PEG+RBV for 24 weeks.
Sofosbuvir+RBVRBVParticipants were randomized to receive sofosbuvir+RBV for 12 weeks.
PEG+RBVRBVParticipants were randomized to receive PEG+RBV for 24 weeks.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants With Sustained Virologic Response 12 Weeks After Stopping All Study Drugs (SVR12)Post-treatment Week 12

SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ; \< 25 IU/mL) 12 weeks after study drug cessation.

Secondary Outcome Measures
NameTimeMethod
Number of Participants Who Experienced Adverse Events (AEs) and Graded Laboratory AbnormalitiesUp to 24 weeks plus 30 days following the last dose of study drug
Percentage of Participants With Sustained Virologic Response 24 Weeks After Stopping All Study Drugs (SVR24)Post-treatment Week 24

SVR24 was defined as HCV RNA \< LLOQ 24 weeks after study drug cessation.

Percentage of Participants With HCV RNA < LLOQ on TreatmentUp to 12 Weeks
Change From Baseline in HCV RNABaseline to Week 12
Percentage of Participants With Virologic Failure During TreatmentBaseline up to Week 24

Virologic failure was defined as either

* Viral breakthrough: HCV RNA ≥ 25 IU/mL after having previously had HCV RNA \< 25 IU/mL while on treatment, confirmed with 2 consecutive values or last available measurement

* Viral rebound: \> 1 log10 IU/mL increase in HCV RNA from nadir while on treatment, confirmed with 2 consecutive values or last available measurement

* Non-response: HCV RNA persistently ≥ 25 IU/ml while on treatment (through Week 12)

Percentage of Participants With Viral Relapse Following TreatmentUp to Post-treatment Week 24

Viral relapse was defined as HCV RNA ≥ 25 IU/mL in post-treatment after having achieved \< LLOQ at last on-treatment measurement, confirmed with 2 consecutive values or last available measurement.

Trial Locations

Locations (96)

Peter J. Ruane, M.D. Inc.

🇺🇸

Los Angeles, California, United States

AIDS Research Consortium of Atlanta, Inc.

🇺🇸

Atlanta, Georgia, United States

Atlanta Gastroenterology Associates

🇺🇸

Atlanta, Georgia, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

Digestive Disease Associates, P.A.

🇺🇸

Baltimore, Maryland, United States

UPMC Center For Liver Diseases

🇺🇸

Pittsburgh, Pennsylvania, United States

Baylor University Medical Center

🇺🇸

Dallas, Texas, United States

Mount Sinai Hospital

🇨🇦

Toronto, Ontario, Canada

Toronto Liver Centre

🇨🇦

Toronto, Ontario, Canada

Royal Perth Hospital

🇦🇺

Perth, Western Australia, Australia

Fremantle Hospital

🇦🇺

Fremantle, Western Australia, Australia

Sir Charles Gairdner

🇦🇺

Nedlands, Western Australia, Australia

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Nashville Gastrointestinal Specialists Inc.

🇺🇸

Nashville, Tennessee, United States

Kelsey-Seybold Clinic PA

🇺🇸

Houston, Texas, United States

Research Specialists of Texas

🇺🇸

Houston, Texas, United States

Alamo Medical Research

🇺🇸

San Antonio, Texas, United States

Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

University of California San Diego Medical Center

🇺🇸

San Diego, California, United States

Research and Education, Inc.

🇺🇸

San Diego, California, United States

Quest Clinical Research

🇺🇸

San Francisco, California, United States

University of Miami, School of Medicine

🇺🇸

Miami, Florida, United States

Medical Associates Research Group, Inc.

🇺🇸

San Diego, California, United States

Henry Ford Health System

🇺🇸

Detroit, Michigan, United States

Duke University Medical Center

🇺🇸

Durham, North Carolina, United States

South Florida Center of Gastroenterology

🇺🇸

Wellington, Florida, United States

eStudySite

🇺🇸

Oceanside, California, United States

AGA Clinical Research Associates, LLC

🇺🇸

Egg Harbor Township, New Jersey, United States

Indianapolis Gastroenterology Research Foundation

🇺🇸

Indianapolis, Indiana, United States

ID Care

🇺🇸

Hillsborough, New Jersey, United States

Atlantic Research Affiliates, LLC

🇺🇸

Morristown, New Jersey, United States

VAMC & Baylor College

🇺🇸

Houston, Texas, United States

Gallipoli MRF

🇦🇺

Greenslopes, Queensland, Australia

Princess Alexandria

🇦🇺

Woollongabba, Queensland, Australia

Royal Adelaide Hospital

🇦🇺

Adelaide, South Australia, Australia

(G.I.R.I.) Gastrointestinal Research Institute

🇨🇦

Vancouver, British Columbia, Canada

Austin Hospital

🇦🇺

Heidelberg, Victoria, Australia

Franco Felizarta, MD

🇺🇸

Bakersfield, California, United States

eStudy Site

🇺🇸

La Mesa, California, United States

Arrowhead Regional Medical Center

🇺🇸

Colton, California, United States

SCTI Research Foundation

🇺🇸

Coronado, California, United States

Midway Immunology & Research Center, LLC

🇺🇸

Fort Pierce, Florida, United States

Borland-Groover Clinic Baptist

🇺🇸

Jacksonville, Florida, United States

Advanced Research Institute

🇺🇸

Trinity, Florida, United States

Beth Israel Deaconess Medical Center

🇺🇸

Boston, Massachusetts, United States

The Research Institute

🇺🇸

Springfield, Massachusetts, United States

Partners in Internal Medicine, PC

🇺🇸

Worcester, Massachusetts, United States

Veterans Affairs Medical Center

🇺🇸

East Orange, New Jersey, United States

Southwest C.A.R.E. Center

🇺🇸

Santa Fe, New Mexico, United States

Weill Cornell Medical College

🇺🇸

New York, New York, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Mount Sinai School of Medicine

🇺🇸

New York, New York, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Schleinitz Research and Gastroenterology LLC

🇺🇸

Medford, Oregon, United States

Gastro One

🇺🇸

Germantown, Tennessee, United States

Texas Clinical Research Institute, LLC

🇺🇸

Arlington, Texas, United States

Digestive and Liver Disease Specialists

🇺🇸

Norfolk, Virginia, United States

Digestive and Liver Disease Specialist, Ltd.

🇺🇸

Norfolk, Virginia, United States

Metropolitan Research

🇺🇸

Fairfax, Virginia, United States

Canberra Hospital

🇦🇺

Garran, Australian Capital Territory, Australia

Royal Prince Alfred Hospital

🇦🇺

Camperdown, New South Wales, Australia

St. George Hospital

🇦🇺

Kogarah, New South Wales, Australia

Royal Brisbane Hospital Research Foundation

🇦🇺

Herston, Queensland, Australia

Monash Medical Centre

🇦🇺

Clayton, Victoria, Australia

The Alfred

🇦🇺

Melbourne, Victoria, Australia

University Health Network-Toronto Western Hospital

🇨🇦

Toronto, Ontario, Canada

Toronto Digestive Disease Associates, Inc.

🇨🇦

Vaughan, Ontario, Canada

Casa Sollievo della Sofferenza Hospital

🇮🇹

San Giovanni Rotondo, Italy

Academish Medisch Centrum

🇳🇱

Amsterdam, Netherlands

Waikato Hospital (District Health Board)

🇳🇿

Hamilton, Waikato, New Zealand

Mercy Hospital

🇳🇿

Dunedin, OTA, New Zealand

Auckland City Hospital

🇳🇿

Grafton, Auckland, New Zealand

Tauranga Hospital

🇳🇿

Tauranga, BOP, New Zealand

Christchurch Hospital

🇳🇿

Chrischurch, Canterbury, New Zealand

Wellington Hospital

🇳🇿

Newtown, WGN, New Zealand

Fundacion de Investigacion de Diego

🇵🇷

San Juan, Puerto Rico

Karolinska Universitetssjukhuset, Solna

🇸🇪

Stockholm, Sweden

Sahlgrenska Universitetssjukhuset, Östra Sjukhus

🇸🇪

Göteborg, Sweden

University of Massachusetts, Worcester

🇺🇸

Worcester, Massachusetts, United States

Alabama Liver & Digestive Specialist

🇺🇸

Montgomery, Alabama, United States

University of Florida College of Medicine

🇺🇸

Gainesville, Florida, United States

California Liver Institute

🇺🇸

Beverly Hills, California, United States

Concord Repatriation General Hospital

🇦🇺

Concord, New South Wales, Australia

South Denver Gastroenterology, PC

🇺🇸

Englewood, Colorado, United States

Pointe West Infectious Diseases

🇺🇸

Bradenton, Florida, United States

Gastrointestinal Specialists of Georgia, PC

🇺🇸

Marietta, Georgia, United States

Asheville Gastroenterology Associates, P.A.

🇺🇸

Asheville, North Carolina, United States

Regional Gastroenterology Associates of Lancaster, Ltd.

🇺🇸

Lancaster, Pennsylvania, United States

Carolinas Center for Liver Disease

🇺🇸

Statesville, North Carolina, United States

Gastroenterology United of Tulsa

🇺🇸

Tulsa, Oklahoma, United States

University Gastroenterology

🇺🇸

Warwick, Rhode Island, United States

University of California, Davis - Health System

🇺🇸

Sacramento, California, United States

Orlando Immunology Center

🇺🇸

Orlando, Florida, United States

Internal Medicine Specialists

🇺🇸

Orlando, Florida, United States

Digestive Health Specialists, PA

🇺🇸

Winston-Salem, North Carolina, United States

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