MedPath

A Study to Evaluate the Efficacy and Safety of Pemigatinib (INCB054828) in Subjects With Myeloid/Lymphoid Neoplasms With FGFR1 Rearrangement - (FIGHT-203)

Phase 2
Completed
Conditions
MPN (Myeloproliferative Neoplasms)
Interventions
Registration Number
NCT03011372
Lead Sponsor
Incyte Corporation
Brief Summary

The purpose of this study is to evaluate the efficacy and safety of pemigatinib (INCB054828) in subjects with myeloid/lymphoid neoplasms with fibroblast growth factor receptor (FGFR) 1 rearrangement.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
47
Inclusion Criteria
  • Documented lymphoid or myeloid neoplasm with 8p11 rearrangement known to lead to FGFR1 activation, based on standard diagnostic cytogenetic evaluation performed locally, before signing informed consent for this study.

  • Eligible subjects must:

    • Have relapsed after stem cell transplantation or after other disease modifying therapy, OR
    • Not be current candidates for stem cell transplantation or other disease modifying therapies.
  • Note: All relapsed/refractory subjects must have evidence of either cytogenetic or hematological disease and have no evidence of residual toxicity (eg, graft-versus-host disease requiring treatment).

  • Life expectancy ≥ 12 weeks.

  • Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2.

Exclusion Criteria
  • Prior receipt of a selective FGFR inhibitor.
  • History and/or current evidence of ectopic mineralization/calcification, including but not limited to soft tissue, kidneys, intestine, myocardia, or lung, except calcified lymph nodes and asymptomatic arterial or cartilage/tendon calcifications.
  • Current evidence of corneal disorder/keratopathy, including but not limited to bullous/band keratopathy, corneal abrasion, inflammation/ulceration, and keratoconjunctivitis, as confirmed by ophthalmologic examination.
  • Use of any potent cytochrome P450 3A4 inhibitors or inducers within 14 days or 5 half-lives (whichever is shorter) before the first dose of study drug.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
PemigatinibPemigatinib-
Primary Outcome Measures
NameTimeMethod
The proportion of participants who achieve Complete Response (CR) based on response criteria for myeloid/lymphoid neoplasms with FGFR1 rearrangement: Assessed at protocol-defined timepoints through end of study, up to approximately 24 months.
Secondary Outcome Measures
NameTimeMethod
The proportion of subjects who achieve a complete cytogenetic response (CCyR) as assessed by local analysis and investigator evaluationAssessed at protocol-defined timepoints through end of study, up to approximately 24 months.
The proportion of subjects who achieve response, defined as a best response of CR or PR, as determined by investigator assessment according to the response criteriaAssessed at protocol-defined timepoints through end of study, up to approximately 24 months.
The proportion of subjects who achieve a partial cytogenetic response (PCyR) as assessed by local analysis and investigator evaluationAssessed at protocol-defined timepoints through end of study, up to approximately 24 months.
Duration of CR, defined as the time from first assessment of CR to the earlier of disease progression or death due to any causeAssessed at protocol-defined timepoints through end of study, up to approximately 24 months.
Duration of response, defined as the time from first assessment of CR or PR to the earlier of disease progression or death due to any causeAssessed at protocol-defined timepoints through end of study, up to approximately 24 months.
Progression-free survival (PFS)From the date of first study drug dose until the date of disease progression or until death due to any cause, whichever is earlier, assessed up to approximately 24 months.

PFS is defined as the time from the first date of taking study drug until the date of disease progression, as measured by response criteria for myeloid/lymphoid neoplasms with FGFR1 rearrangement, or until death due to any cause, whichever is earlier.

Overall survivalFrom date of first study drug dose until death due to any cause, assessed up to approximately 24 months.

Overall survival is defined as the time from the first day of taking study drug until death due to any cause. Subjects without death observed at the time of the analysis will be censored at last date known to be alive.

Safety and tolerability as assessed by frequency, duration, and severity of adverse eventsFrom baseline through 30-35 days after end of treatment, up to 7 months per individual subject

A treatment-emergent AE was defined as an event occurring after exposure to at least 1 dose of study drug. A treatment-related AE was defined as an event with a definite, probable, or possible causality to study medication. A serious AE is an event resulting in death, hospitalization, persistent or significant disability/incapacity, or is life threatening, a congenital anomaly/birth defect or requires medical or surgical intervention to prevent 1 of the outcomes above. The intensity of an AE was graded according to the National Cancer Institute common terminology criteria for adverse events (NCI-CTCAE) version 4.03: Grade 1 (Mild); Grade 2 (Moderate); Grade 3 (Severe); Grade 4 (life-threatening).

Trial Locations

Locations (33)

Stanford Cancer Institute

🇺🇸

Stanford, California, United States

Chu de Nice - Hospital L Archet

🇫🇷

Nice Cedex 3, France

Universitatsklinikum Jena

🇩🇪

Jena, Germany

Ntt Medical Center Tokyo

🇯🇵

Tokyo, Japan

Hospital Clinico Universitario de Valencia

🇪🇸

Valencia, Spain

Iii Med. Abteilung For Hematologie and Onkologie Hanuscfhkrankenhaus

🇦🇹

Wien, Austria

Universitair Ziekenhuis (Uz) Leuven

🇧🇪

Leuven, Belgium

University of Utah

🇺🇸

Salt Lake City, Utah, United States

Johannes Wesling Klinikum Minden

🇩🇪

Minden, Germany

Kindai University Hospital

🇯🇵

Osaka, Japan

University Medical Center Rwth Aachen

🇩🇪

Aachen, Germany

Guys and St Thomas Nhs Foundation Trust

🇬🇧

London, United Kingdom

Hospital Saint Louis

🇫🇷

Paris Cedex 10, France

Medical University of Vienna

🇦🇹

Wien, Austria

Ospedale Papa Giovanni Xxiii

🇮🇹

Bergamo, Italy

Princess Margaret Cancer Center

🇨🇦

Toronto, Ontario, Canada

Universitaire Du Cancer de Toulouse Institut Claudius Regaud Iuct-Oncopole

🇫🇷

Toulouse Cedex 9, France

Universitatsklinikum Leipzig

🇩🇪

Leipzig, Germany

Azienda Ospedaliero-Universitaria Careggi (Aouc)

🇮🇹

Florence, Italy

Centre Leon Berard

🇫🇷

Lyon, France

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Mayo Clinic Arizona

🇺🇸

Phoenix, Arizona, United States

Emory University - Winship Cancer Institute

🇺🇸

Atlanta, Georgia, United States

Weill Cornell Medical Centers

🇺🇸

New York, New York, United States

Franciscan St. Francis Health

🇺🇸

Indianapolis, Indiana, United States

Md Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Universitatsklinikum Halle (Saale)

🇩🇪

Halle, Germany

University Hospital Mannheim

🇩🇪

Mannheim, Germany

Oxford University Hospitals Nhs Foundation Trust

🇬🇧

Oxford, United Kingdom

City of Hope National Medical Center

🇺🇸

Duarte, California, United States

Inselspital - Universitaetsspital Bern

🇨🇭

Bern, Switzerland

Universitatsspital Zurich

🇨🇭

Zurich, Switzerland

Ordensklinikum Krankenhaus Der Barmherzigen Schwestern Linz

🇦🇹

Linz, Austria

© Copyright 2025. All Rights Reserved by MedPath