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Study of REGN4018 Administered Alone or in Combination With Cemiplimab in Adult Patients With Recurrent Ovarian Cancer or Other Recurrent Mucin-16 Expressing (MUC16+) Cancers

Phase 1
Recruiting
Conditions
Recurrent Primary Peritoneal Cancer
Recurrent Endometrial Cancer
Recurrent Ovarian Cancer
Recurrent Fallopian Tube Cancer
Interventions
Registration Number
NCT03564340
Lead Sponsor
Regeneron Pharmaceuticals
Brief Summary

The main purpose of this study is to:

* Learn about the safety of REGN4018 and to find out what dose of REGN4018 can be given alone or with cemiplimab to patients with ovarian cancer or cancer of the uterus

* The study will also look at the levels of REGN4018 and/or cemiplimab in your body and measure how well your body can remove the study drug(s). This is called pharmacokinetics

* The study will also look at any signs that REGN4018 alone or with cemiplimab can treat recurrent advanced ovarian cancer or cancer of the uterus

* To find out how safe and tolerable the sarilumab pretreatment is, in combination with REGN4018 and cemiplimab

Detailed Description

Not available

Recruitment & Eligibility

Status
RECRUITING
Sex
Female
Target Recruitment
690
Inclusion Criteria
  1. Ovarian Cancer Cohorts Only: Patients with histologically or cytologically confirmed diagnosis of advanced, epithelial ovarian cancer (except carcinosarcoma), primary peritoneal, or fallopian tube cancer who have all of the following:

    1. serum CA-125 level ≥2 x upper limit of normal (ULN) (in screening)
    2. has received at least 1 line of platinum-containing therapy or must be platinum-intolerant (applicable for dose escalation and non-randomized dose expansion cohorts)
    3. documented relapse or progression on or after the most recent line of therapy
    4. no standard therapy options likely to convey clinical benefit
  2. Adequate organ and bone marrow function as defined in the protocol

  3. Life expectancy of at least 3 months

  4. Randomized phase 2 expansion cohort (Ovarian Cancer only): Platinum-resistant ovarian cancer patients who have had 1 to 3 lines of platinum-based therapy as defined in the protocol.

  5. Endometrial Cancer Cohorts Only: histologically confirmed endometrial cancer that has progressed or recurrent after prior anti-Programmed Cell Death Ligand 1 (PD-1) therapy and platinum-based chemotherapy:

    1. MUC16 positivity of tumor cells ≥25% by immunohistochemistry (IHC)
    2. 1-2 prior lines of systemic therapy

Key

Exclusion Criteria
  1. Prior treatment with anti-Programmed Cell Death (PD-1)/PD-L1 therapy, as described in the protocol
  2. Ovarian Cancer Expansion cohorts only: More than 4 prior lines of cytotoxic chemotherapy
  3. Prior treatment with a MUC16 - targeted therapy
  4. Untreated or active primary brain tumor, central nervous system (CNS) metastases, or spinal cord compression, as described in the protocol
  5. History and/or current cardiovascular disease, as defined in the protocol
  6. Severe and/or uncontrolled hypertension at screening. Patients taking anti-hypertensive medication must be on a stable anti-hypertensive regimen

Note: Other protocol Inclusion/Exclusion Criteria apply

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
MonotherapyREGN4018REGN4018 administration
Combination TherapyREGN4018REGN4018 and cemiplimab administration
MonotherapySarilumabREGN4018 administration
Combination TherapycemiplimabREGN4018 and cemiplimab administration
Primary Outcome Measures
NameTimeMethod
Number of participants with TEAEs (including imAEs) for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

Concentration of REGN4018 in serum over time for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Number of participants with Treatment-emergent adverse event (TEAE)s (including immune-related adverse events (imAEs)) for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Concentration of REGN4018 in serum over time for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

Objective response rate (ORR) defined by Response Evaluation Criteria in Solid Tumors (RECIST 1.1) for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Number of participants with DLTs for REGN4018 with cemiplimabFrom Cycle 2, Day 1 up to 21 days

Dose Escalation Phase

ORR defined by RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Number of participants with Dose-limiting toxicity (DLTs) for REGN4018 monotherapyFrom Cycle 1, Day 1 up to 35 days

Dose Escalation Phase

Number of participants with serious adverse events (SAEs) for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Number of participants with SAEs for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

Number of deaths for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Number of deaths for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

Number of participants with laboratory abnormalities (grade 3 or higher per Common Terminology Criteria for Adverse Events [CTCAE]) for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Number of participants with laboratory abnormalities (grade 3 or higher per CTCAE) for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

Secondary Outcome Measures
NameTimeMethod
ORR based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation Phase

ORR based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation Phase

Number of participants with TEAEs (including imAEs) for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Number of participants with TEAEs (including imAEs) for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Number of participants with SAEs for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Number of participants with SAEs for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Number of deaths for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Number of deaths for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Number of participants with laboratory abnormalities (grade 3 or higher per CTCAE) for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Number of participants with laboratory abnormalities (grade 3 or higher per CTCAE) for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Concentration of REGN4018 in serum over time for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Concentration of REGN4018 in serum over time for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Change from baseline in quality of life (QoL) as measured by the European Organisation for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire (QLQ)-C30 GHS/QoL score for REGN4018 monotherapyBaseline up to 62 weeks

Dose Expansion Phase

The EORTC-QLQ-C30 is a 30-item subject self-report questionnaire composed of both multi-item and single scales, including global health status/quality of life, functional Scales (physical, role, emotional, cognitive, and social) , symptom scales (fatigue, nausea and vomiting, and pain), and 6 single items (dyspnea, insomnia, appetite loss, constipation, diarrhea, and financial difficulties). Participants rate items on a 4-point scale, with 1 as "not at all" and 4 as "very much."

Change from baseline in quality of life (QoL) as measured by the European Organisation for Research and Treatment of Cancer (EORTC) Quality of Life Questionnaire (QLQ)-C30 GHS/QoL score for REGN4018 with cemiplimabBaseline up to 62 weeks

Dose Expansion Phase

Change from baseline in physical functioning as measured by the EORTC QLQ-C30 physical functioning score for REGN4018 monotherapyBaseline up to 62 weeks

Dose Expansion Phase

Change from baseline in physical functioning as measured by the EORTC QLQ-C30 physical functioning score for REGN4018 with cemiplimabBaseline up to 62 weeks

Dose Expansion Phase

Change from baseline in abdominal symptoms as measured by the Measure of Ovarian Symptoms and Treatment (MOST)-Abdominal index score for REGN4018 monotherapyBaseline up to 62 weeks

Dose Expansion Phase excluding the Endometrial Cancer Cohort

The MOST-24 is a 24-item questionnaire used to measure the impact of chemotherapy on symptoms (21 items) and well-being (3 items). The expected questionnaire completion time is less than 5 minutes.

The prevalence of each MOST item at assessment time points can be summarized by providing the mean, standard deviation and proportions based on the MOST response format, a numeric rating scale with integers from zero to 10, with five verbal anchors: 'No trouble at all' (0), 'Mild' (1-3), 'Moderate' (4-6), 'Severe' (7-10), and 'Worst I can imagine' (10).

Change from baseline in abdominal symptoms as measured by the MOST-Abdominal index score for REGN4018 with cemiplimabBaseline up to 62 weeks

Dose Expansion Phase Not applicable to Endometrial Cancer Cohort

Time to deterioration in GHS/QoL for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Time to deterioration in GHS/QoL for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Time to deterioration in physical functioning for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Time to deterioration in physical functioning for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Time to deterioration in abdominal symptoms for REGN4018 monotherapyUp to 62 weeks

Dose Expansion Phase

Time to deterioration in abdominal symptoms for REGN4018 with cemiplimabUp to 62 weeks

Dose Expansion Phase

Change from baseline in QoL as measured by EQ-5D for REGN4018 monotherapyBaseline up to 62 weeks

Dose Expansion Phase

Change from baseline in QoL as measured by EQ-5D for REGN4018 with cemiplimabBaseline up to 62 weeks

Dose Expansion Phase

ORR based on iRECIST for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

ORR based on iRECIST for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Best overall response (BOR) based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

BOR based on iRECIST for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

BOR based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

BOR based on iRECIST for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Duration of response (DOR) based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

DOR based on iRECIST for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

DOR based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

DOR based on iRECIST for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Disease control rate based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Disease control rate based on iRECIST for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Disease control rate based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Disease control rate based on iRECIST for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Complete response (CR) rate based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

CR rate based on iRECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

CR rate based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

CR rate based on iRECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Progression-free survival (PFS) based on RECIST 1.1 for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

PFS based on iRECIST for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

PFS based on RECIST 1.1 for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

PFS based on iRECIST for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Cancer antigen-125 (CA-125) response for REGN4018 monotherapyUp to 62 weeks

Dose Escalation and Dose Expansion Phases

CA-125 response for REGN4018 with cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Presence or absence of anti-drug antibodies against REGN4018Up to 62 weeks

Dose Escalation and Dose Expansion Phases

Presence or absence of anti-drug antibodies against cemiplimabUp to 62 weeks

Dose Escalation and Dose Expansion Phases

Trial Locations

Locations (51)

Guys Hospital

🇬🇧

London, United Kingdom

Sharet Institute of Oncology

🇮🇱

Jerusalem, Israel

University of Alabama_6th Ave

🇺🇸

Birmingham, Alabama, United States

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Dana Farber / Harvard Cancer Center

🇺🇸

Boston, Massachusetts, United States

Mayo Clinic - Rochester

🇺🇸

Rochester, Minnesota, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Columbia University Medical Center

🇺🇸

New York, New York, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

The Ohio State University Wexner Medical Center James Comprehensive Cancer Center

🇺🇸

Hilliard, Ohio, United States

Stephenson Cancer Center

🇺🇸

Oklahoma City, Oklahoma, United States

Sarah Cannon Research Institute

🇺🇸

Nashville, Tennessee, United States

University College London Hospitals

🇬🇧

London, United Kingdom

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

Peter MacCallum Cancer Center

🇦🇺

Melbourne, Australia

Prince of Wales Hospital

🇦🇺

Randwick, Australia

Universitair Ziekenhuis Antwerpen

🇧🇪

Edegem, Antwerp, Belgium

Grand Hopital de Charleroi

🇧🇪

Charleroi, Hainaut, Belgium

UZLeuven

🇧🇪

Leuven, Vlaams Brabant, Belgium

Centre Georges Francois Leclerc

🇫🇷

Dijon, Bourgogne, France

Institut Gustave Roussy

🇫🇷

Villejuif, Ile De France, France

Hopital Lyon Sud

🇫🇷

Pierre-Benite, Lyon, France

Centre Francois Baclesse (CFB)

🇫🇷

Caen, Normandy, France

Centre Antoine Lacassagne

🇫🇷

Nice, Provence Alpes Cote dAzur, France

Institut Bergonie

🇫🇷

Bordeaux, France

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Sheba Medical Center

🇮🇱

Tel Hashomer, Israel

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

🇮🇹

Roma, Lazio, Italy

Istituto Europeo di Oncologia

🇮🇹

Milano, Italy

Instituto Nazionale Tumori- Fondazione Pascale

🇮🇹

Naples, Italy

Yonsei University Health System

🇰🇷

Seoul, Korea, Republic of

Asan Medical Center, Univ. of Ulsan

🇰🇷

Seoul, Korea, Republic of

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Korea University Guro Hospital

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Radboudumc

🇳🇱

Nijmegen, Gelderland, Netherlands

Erasmus MC

🇳🇱

Rotterdam, Zuid Holland, Netherlands

University Medical Center Groningen

🇳🇱

Groningen, Netherlands

Clinica Universidad de Navarra

🇪🇸

Pamplona, Navarra, Spain

Institut Catala dOncologia Badalona

🇪🇸

Badalona, Spain

Hospital Universitari Vall d'Hebron

🇪🇸

Barcelona, Spain

Institut Catala d'Oncologia

🇪🇸

Barcelona, Spain

Clinica Universidad Navarra (CUN) Madrid

🇪🇸

Madrid, Spain

Fundacion Jimenez Diaz

🇪🇸

Madrid, Spain

Hospital Universitario San Carlos

🇪🇸

Madrid, Spain

Hospital Clinico Universitatio Santiago de Compostela

🇪🇸

Santiago de Compostela, Spain

University of Oxford

🇬🇧

Oxford, Oxfordshire, United Kingdom

Royal Marsden Hospital - Sutton

🇬🇧

Sutton, Surrey, United Kingdom

The Royal Marsden NHS Foundation Trust

🇬🇧

Sutton, Surrey, United Kingdom

Imperial College Healthcare NHS Trust

🇬🇧

London, United Kingdom

The Christie

🇬🇧

Manchester, United Kingdom

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