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Evaluation of PKU UP

Not Applicable
Recruiting
Conditions
PKU
Registration Number
NCT05995717
Lead Sponsor
Vitaflo International, Ltd
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
All
Target Recruitment
15
Inclusion Criteria

Inclusion Criteria:<br><br> - Diagnosis of PKU requiring a low-protein diet and protein substitute.<br><br> - Participants who are adherent with their blood phenylalanine (Phe) testing, in the<br> opinion of the investigator.<br><br> - Participants aged 1-10 years.<br><br> - Participants who in the opinion of the investigator are anticipated to be able to<br> take at least half of their daily protein equivalent requirement from PKU UP (in<br> order to assess this, a taste test (or similar) may be conducted at investigator's<br> discretion as part of the screening process).<br><br> - Willingly given, written, informed consent from the parent(s)/guardian(s).<br><br> - Willingly given, written assent by the participant (if appropriate).<br><br>Exclusion Criteria:<br><br> - Inability to comply with the study protocol, in the opinion of the investigator.<br><br> - Any co-morbidity, which, in the opinion of the investigator, would preclude<br> participation in the study.<br><br> - Diagnosis of persistent hyperphenylalaninemia, or mild PKU not requiring a low<br> protein diet and protein substitute.<br><br> - Allergy or intolerance to milk.<br><br> - Participants who are currently participating in, plan to participate in or have<br> participated in an interventional investigational drug, food or medical device study<br> within 30 days prior to the screening visit.<br><br> - Use of additional micronutrient supplements during the evaluation period, unless<br> clinically indicated and prescribed by the Investigator (must be recorded in both<br> the medical records and case report form).

Exclusion Criteria

Not provided

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Change in phe level between baseline and visit 3;Change in tyrosine level between baseline and visit 3;Change in PI impression of metabolic control;Change in the growth of participants as measured by Height (length in under 2 years of age), Head circumference in under 2 years of age and Weight.;Change in GI tolerance (participant);Change in PI impression of GI tolerance;Change in compliance with study product consumption;Change in PI impression of study product intake;Change in product acceptability;Change in dietary intake;Change in nutritional biochemistry
Secondary Outcome Measures
NameTimeMethod
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