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N-Acetylcysteine and Milk Thistle for Treatment of Diabetic Nephropathy

Phase 2
Completed
Conditions
Proteinuria
Diabetic Nephropathies
Oxidative Stress
Interventions
Dietary Supplement: silibin
Dietary Supplement: N-acetylcysteine
Dietary Supplement: silibin placebo
Dietary Supplement: N-acetylcysteine placebo
Dietary Supplement: high-dose silibin
Registration Number
NCT00915200
Lead Sponsor
The University of Texas Health Science Center at San Antonio
Brief Summary

The study is designed to test if the combination of two potent antioxidant nutritional supplements, N-acetylcysteine and the milk thistle extract silibin, is capable of correcting the shedding of urine protein, the oxidative stress, and the inflammation in patients with type 2 diabetes mellitus and diabetic kidney disease.

Detailed Description

Oxidative stress and GSH imbalance are major contributors to the pathogenesis of diabetic nephropathy. Current options for the treatment of oxidative stress in diabetic nephropathy are limited and only partially effective, thus interest in the development of new strategies is high.

The study intends to test the hypothesis that combined oral supplementation of the antioxidants N-acetylcysteine (NAC) and milk thistle flavonolignan silibin (as silibin-phosphatidylcholine) will reduce proteinuria and urinary and systemic manifestations of oxidative stress and inflammation, which are characteristically observed in patients with type 2 diabetes mellitus and related nephropathy. We expect these effects to be achieved with minimal or no side effects, and with good patient tolerance.

The trial is designed as a two-center, double-blind, placebo-controlled, randomized, modified-factorial dose-ranging design, five-arm pilot study in patients with Type 2 diabetes mellitus and advanced diabetic nephropathy with proteinuria.

Intervention consists of three-month oral administration of NAC, silibin, and/or respective placebos for three months. Subjects are randomized to the following five intervention arms: (A) placebo; (B) NAC; (C) silibin; (D) NAC + silibin; and (E) NAC + double-dose silibin.

The primary outcome measure is urinary excretion of albumin, a marker of glomerular injury. Secondary outcome measures are alpha-1 microglobulin, a marker of tubular injury, and urinary excretion of inflammatory cytokines and C-C chemokines, i.e. markers of renal inflammation. In addition, peripheral blood monocytes from the same patients are analyzed for glutathione (GSH) content and activity of GSH metabolizing enzymes. All outcome measures are monitored in relation to both treatment allocation and prevalent blood and urine levels of the active treatment. Safety and tolerability of this combination treatment are monitored throughout the trial.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
114
Inclusion Criteria
  • Males or females, age 18-70 years old.

  • Type 2 diabetes mellitus

  • Diabetic nephropathy, as defined by:

    • estimated GFR between 60 and 15 ml/min,
    • presence of proteinuria.
  • Current medical treatment with low dose aspirin

  • Treatment of hypertension with (but not limited to) one diuretic, one beta- blocker and one medication from the classes ARBs or ACE inhibitors.

  • Treatment of hyperglycemia with (but not limited to) glipizide and the medication class insulin.

  • Treatment of hypercholesterolemia with (but not limited to) one medication from the class statins.

Exclusion Criteria
  • Type 1 diabetes mellitus.

  • Glycosylated hemoglobin (HbA1C) > 10%

  • >20% variation in estimated GFR, during last 6 months

  • SBP >170 mmHg or DBP >100 mmHg on medications

  • Other secondary forms of hypertension (endocrine, renovascular)

  • History of intolerance to:

    • Both ACE-I and ARBs;
    • The investigational supplements;
    • Iodinated radiologic contrast material.
  • Known non diabetic renal disease, or history of solid organ transplantation.

  • Hepatitis virus or Human Immunodeficiency virus infections

  • Use of one of the following medications within 2 months prior to enrollment in the study:

    • Metformin.
    • Thiazolidinediones (pioglitazone or rosiglitazone);
    • Prescription-grade vitamin E, vitamin C, systemic steroids, and/or non-steroidal anti-inflammatory agents;
    • Over-the-counter vitamin E, vitamin C, and/or non-steroidal anti-inflammatory agents.
    • Over-the-counter antioxidants supplements including: Lipoic acid, Coenzyme Q10, N-acetyl-cysteine (NAC), Glutathione (GSH), Chromium, Fish-oil extracts (omega-3 fatty acids), Soy extracts (isoflavones), Milk thistle extract (silymarin), Green-tea preparations, Pomegranate extracts, Grape extracts, and Prickly pear extract.
  • Active coronary artery disease or cerebral vascular disease within 3 months prior to signing the informed consent.

  • Hepatic dysfunction as defined by abnormal total bilirubin or liver enzymes (ALT, AST) >2 times upper limit of normal range.

  • Active malignancy.

  • History of drug or alcohol dependency.

  • Psychiatric or neurological condition, preventing aware consent to the study and/or adherence to the study protocol

  • Unwillingness to practice birth control throughout the study.

  • Participation to another clinical study within 1 month prior to signing the informed consent form.

  • Planned move to outside the study area, surgery or radiographic studies utilizing iodine-based contrast material within the next one year

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebosilibin placeboN-acetylcysteine placebo + silibin placebo
silibinsilibinN-acetylcysteine placebo + silibin active
silibinsilibin placeboN-acetylcysteine placebo + silibin active
N-acetylcysteinesilibin placeboN-acetylcysteine active + silibin placebo
N-acetycysteine + silibinsilibinN-acetylcysteine active + silibin active
N-acetycysteine + silibinsilibin placeboN-acetylcysteine active + silibin active
silibinN-acetylcysteine placeboN-acetylcysteine placebo + silibin active
PlaceboN-acetylcysteine placeboN-acetylcysteine placebo + silibin placebo
N-acetylcysteineN-acetylcysteineN-acetylcysteine active + silibin placebo
N-acetycysteine + silibinN-acetylcysteineN-acetylcysteine active + silibin active
N-acetylcysteine + high-dose silibinN-acetylcysteineN-acetylcysteine active + high-dose silibin active
N-acetylcysteine + high-dose silibinhigh-dose silibinN-acetylcysteine active + high-dose silibin active
Primary Outcome Measures
NameTimeMethod
Urinary Albumin excretion3-month
Secondary Outcome Measures
NameTimeMethod
urinary alpha-1 microglobulin excretion3-month
urinary C-C-chemokines excretion3-month
peripheral blood monocyte glutathione content3-month
tolerance and safety3-month

Trial Locations

Locations (1)

University of Texas Hlth Sci Ctr San Ant

🇺🇸

San Antonio, Texas, United States

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