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Study Evaluating The Safety Of AAB-003 (PF-05236812) In Subjects With Alzheimer's Disease

Phase 1
Completed
Conditions
Alzheimer's Disease
Interventions
Drug: AAB-003 (PF-05236812)
Other: Placebo
Registration Number
NCT01193608
Lead Sponsor
Pfizer
Brief Summary

This is a study to evaluate the safety of multiple doses of AAB-003 (PF-05236812) in patients with mild to moderate Alzheimer's Disease. Patients will receive either AAB-003 (PF-05236812) or placebo. Each patient's participation will last approximately 41 weeks.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
88
Inclusion Criteria
  • Diagnosis of probable Alzheimer's Disease with MMSE score of 16-26, and brain MRI consistent with the diagnosis of Alzheimer's Disease
  • Concurrent use of cholinesterase inhibitor or memantine allowed, if stable.
  • Caregiver will participate and be able to attend clinic visits with patient
Exclusion Criteria
  • Significant neurological disease other than Alzheimer's Disease
  • Major psychiatric disorder
  • Contraindication to undergo brain MRI (e.g., pacemaker, CSF shunt, or foreign metal objects in the body)
  • Women of childbearing potential

Study & Design

Study Type
INTERVENTIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
1 mg/kg AAB-003AAB-003 (PF-05236812)-
0.5 mg/kg AAB-003AAB-003 (PF-05236812)-
2 mg/kg AAB-003AAB-003 (PF-05236812)-
4 mg/kg AAB-003AAB-003 (PF-05236812)-
8 mg/kg AAB-003AAB-003 (PF-05236812)-
PlaceboPlacebo-
Primary Outcome Measures
NameTimeMethod
Number of Participants With Laboratory AbnormalitiesBaseline up to 39 Weeks and at Early Withdrawal
Number of Participants With Vital Signs of Potential Clinical ConcernBaseline up to 39 Weeks and at Early Withdrawal

Criteria for potential clinical concern in vital signs included: supine/sitting pulse rate of less than (\<) 40 or more than (\>) 120 beats per minute (bpm), and standing pulse rate of \<40 or \>140 bpm; systolic blood pressure (SBP) of more than or equal to (\>=)30 millimeters of mercury (mm Hg) change from baseline in same posture and \<90 mm Hg; diastolic blood pressure (DBP) \>=20 mm Hg change from baseline in same posture and \<50 mm Hg. Only supine vital signs were planned for this study. Unplanned sitting vital signs were collected only in the 8/mg and placebo groups and also reported.

Time to Reach Maximum Observed Serum Concentration (Tmax) for AAB-003 at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Area Under the Curve From Time Zero to Extrapolated Infinite Time (AUCinf) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Number of Participants With Treatment-Emergent Adverse Events (TEAEs)Baseline up to 39 Weeks and at Early Withdrawal
Number of Participants With Abnormal Neurological Examination FindingsScreening, Day 1 (Baseline) and Weeks 1,6,13,19,26,32, and 39, and at Early Withdrawal

The neurological examination was done to the extent needed to assess the participant for any potential changes in neurological status, as determined by the investigator. The minimum items assessed were level of consciousness, speech, cranial nerves, motor, sensory, coordination, gait, and tendon reflexes.

Maximum Observed Serum Concentration (Cmax) for AAB-003 at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Area Under the Curve From Time Zero to Last Quantifiable Concentration (AUClast) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Serum Decay Half-Life (t1/2) for AAB-003 at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Number of Participants With Categorical Scores on the Columbia Suicide Severity Rating Scale (C-SSRS)Baseline up to Week 39 or Early Withdrawal

The C-SSRS assessed whether the participant experienced the following: completed suicide (1), suicide attempt (2) (response of "Yes" on "actual attempt"), preparatory acts toward imminent suicidal behavior (3)("Yes" on "preparatory acts or behavior"), suicidal ideation (4) ("Yes" on "wish to be dead", "non-specific active suicidal thoughts", "active suicidal ideation with methods without intent to act or some intent to act, without specific plan or with specific plan and intent), any suicidal behavior or ideation, self-injurious behavior (7)("Yes" on "Has participant engaged in non-suicidal self-injurious behavior").

Number of Participants With New Occurrence of Brain Magnetic Resonance Imaging (MRI) FindingBaseline up to Week 32.

Brain MRIs were collected during the course of study to assess for any potential drug-related changes that might have constituted a safety concern for study participants. Findings suggestive of either vasogenic edema (VE) or intracranial hemorrhage represented adverse events of special circumstance and were to be reported immediately.

Number of Participants With Vasogenic Edema of All Severity After Each Infusion VisitDay 1, Week 13, and Week 26

VE of the brain, identified via MRI, was identified as an adverse event of special circumstance.

Number of Participants With Abnormal Physical Examination FindingsBaseline up to 39 Weeks and at Early Withdrawal
Maximum Observed Serum Concentration (Cmax) for AAB-003 at at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Time to Reach Maximum Observed Serum Concentration (Tmax) for AAB-003 at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Systemic Clearance (CL) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Systemic Clearance (CL) for AAB-003 in Serum at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Volume of Distribution at Steady State (Vss) for AAB-003 in Serum at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Serum Decay Half-Life (t1/2) for AAB-003 at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Average Concentration (Cavg) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Area Under the Curve From Time Zero to End of Dosing Interval (AUCtau) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Area Under the Curve From Time Zero to End of Dosing Interval (AUCtau) for AAB-003 in Serum at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Volume of Distribution at Steady State (Vss) for AAB-003 in Serum at Day 1Pre-dose, 1 hour (end of infusion), 1.5, 2, 4 and 6 hours post start of infusion.
Average Concentration (Cavg) for AAB-003 in Serum at Week 26Pre-dose, 1 hour (end of infusion), 1.5, 2, 4, 6, and 24 hours post start of infusion.
Number of Participants With Change From Baseline and Absolute Values in Electrocardiogram (ECG) Meeting Categorical Summarization CriteriaBaseline, Weeks 1,13,16,26,39 or Early Withdrawal

Criteria for ECG values of potential clinical concern are: interval between the start of the ECG P wave and the start of the QRS complex corresponding to the time between onset of atrial depolarization and onset of ventricular depolarization (PR): \>= 300 milliseconds (msec), and \>=25% increase when baseline \>=200 msec/ \>=50% increase when baseline less than or equal to (\<=) 200 msec; time from ECG Q wave to the end of S wave corresponding to ventricular depolarization (QRS): \>=200 msec, and \>=25% increase when baseline \>100 msec/ \>=50% increase when baseline \<=100 msec; QTc using Fridericia's formula (QTcF) interval: 450 to \<480 msec, \>=480 msec; QTcF change from baseline: 30 to \<60 msec, and \>=60 msec.

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (29)

Atlanta Center for Medical Research

🇺🇸

Atlanta, Georgia, United States

Belmont Center for Comprehensive Treatment

🇺🇸

Philadelphia, Pennsylvania, United States

Foers Medical Arts Pharmacy

🇺🇸

Bethesda, Maryland, United States

CBH Health, LLC

🇺🇸

Rockville, Maryland, United States

Early Phase Investigational Center

🇺🇸

Escondido, California, United States

Franck's Pharmacy

🇺🇸

Ocala, Florida, United States

Munroe Regional Medical Center

🇺🇸

Ocala, Florida, United States

Synergy Clinical Research Center of Escondido

🇺🇸

Escondido, California, United States

Konkuk University Medical Center, Department of Neurology

🇰🇷

Seoul, Korea, Republic of

Renstar Medical Research

🇺🇸

Ocala, Florida, United States

DePaul Health Center

🇺🇸

St. Louis, Missouri, United States

Advanced Imaging of Ocala

🇺🇸

Ocala, Florida, United States

Precise Research Centers

🇺🇸

Flowood, Mississippi, United States

Marty's Pharmacy

🇺🇸

Flowood, Mississippi, United States

Samsung Medical Center, Department of Neurology

🇰🇷

Seoul, Korea, Republic of

Borgess Medical Center

🇺🇸

Kalamazoo, Michigan, United States

Central Jersey Radiology

🇺🇸

Oakhurst, New Jersey, United States

Borgess Research Institute

🇺🇸

Kalamazoo, Michigan, United States

Korea University Anam Hospital

🇰🇷

Seoul, Korea, Republic of

Millennium Psychiatric Associates, LLC

🇺🇸

Creve Coeur, Missouri, United States

KNI/Southwest Michigan Imaging Center, LLC

🇺🇸

Kalamazoo, Michigan, United States

Albert Einstein Medical Center

🇺🇸

Philadelphia, Pennsylvania, United States

Pharmacare USA

🇺🇸

Edison, New Jersey, United States

ASAN Medical Center

🇰🇷

Seoul, Korea, Republic of

Inha University Hospital, Department of Neurology

🇰🇷

Incheon, Korea, Republic of

Memory Enhancement Center of America, Inc.

🇺🇸

Eatontown, New Jersey, United States

MD Clinical

🇺🇸

Hallandale Beach, Florida, United States

Seoul National University Bundang Hospital, Department of Neurology

🇰🇷

Seongnam-si, Gyeonggi-do, Korea, Republic of

Brentwood Behavioral Healthcare

🇺🇸

Flowood, Mississippi, United States

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