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Efficacy and Safety Study of STX209 (Arbaclofen) for Social Withdrawal in Adolescents and Adults With Fragile X Syndrome

Phase 3
Completed
Conditions
Fragile X Syndrome
Interventions
Drug: placebo
Registration Number
NCT01282268
Lead Sponsor
Seaside Therapeutics, Inc.
Brief Summary

To explore the efficacy, safety and tolerability of STX209 (arbaclofen) administered for the treatment of social withdrawal in adolescents and adults with fragile X syndrome (FXS)

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
125
Inclusion Criteria
  • Molecular documentation of the full FMR1 mutation
  • Current pharmacological treatment regimen has been stable for at least 4 weeks prior to Screening.
  • Subjects with a history of seizure disorder must currently be receiving treatment with antiepileptics and must have been seizure free for 6 months, or must be seizure free for 3 years if not currently receiving antiepileptics.
  • If the subject is already receiving stable non-pharmacologic educational, behavioral, and/or dietary interventions, participation in these programs must have been continuous during the 2 months prior to Screening
Exclusion Criteria
  • Subjects with any condition, including alcohol and drug abuse, which might interfere with the conduct of the study, confound interpretation of the study results, or endanger their own well-being.
  • Subjects who plan to initiate or change pharmacologic or non-pharmacologic interventions during the course of the study.
  • Subjects who have taken another investigational drug within the last 30 days.
  • Subjects who are not able to take oral medications.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Arbaclofenarbaclofen-
Placeboplacebo-
Primary Outcome Measures
NameTimeMethod
Aberrant Behavior Checklist - FXS Social Avoidance SubscaleAt 8 weeks of treatment
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (24)

Akron Children's Hospital

🇺🇸

Akron, Ohio, United States

Rush University Medical Center

🇺🇸

Chicago, Illinois, United States

Red Oaks Psychiatry Associates, P.A.

🇺🇸

Houston, Texas, United States

Road Runner Research

🇺🇸

San Antonio, Texas, United States

Lake Mary Pediatrics

🇺🇸

Orange City, Florida, United States

University of Missouri, Thompson Research Center for Autism & Neurodevelpmental Disorders

🇺🇸

Columbia, Missouri, United States

Riley Hospital for Children

🇺🇸

Indianapolis, Indiana, United States

University of Massachusetts

🇺🇸

Worcester, Massachusetts, United States

Seaver Autism Center, Mount Sinai Medical Center

🇺🇸

New York, New York, United States

Miller Children's Hospital Research Administration

🇺🇸

Long Beach, California, United States

Emory University School of Medicine

🇺🇸

Decatur, Georgia, United States

University of Miami, Mailman Center for Child Development

🇺🇸

Miami, Florida, United States

Kennedy Krieger Institute

🇺🇸

Baltimore, Maryland, United States

New York State Institute for Basic Research in Developmental Disabilities

🇺🇸

Staten Island, New York, United States

Seattle Children's Hospital

🇺🇸

Seattle, Washington, United States

Texas Children's Hospital

🇺🇸

Houston, Texas, United States

Suburban Research Associates/Elwyn Genetics

🇺🇸

Media, Pennsylvania, United States

Psychiatric Centers at San Diego

🇺🇸

San Diego, California, United States

Duke University Clinical Research Unit

🇺🇸

Durham, North Carolina, United States

Southwest Autism Research & Resource Center

🇺🇸

Phoenix, Arizona, United States

University of Oklahoma, Physician's Child Study Center

🇺🇸

Oklahoma City, Oklahoma, United States

Vanderbilt Kennedy Center

🇺🇸

Nashville, Tennessee, United States

University of California-Davis, M.I.N.D. Institute

🇺🇸

Sacramento, California, United States

University of Colorado Denver, Children's Hospital

🇺🇸

Aurora, Colorado, United States

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