MedPath

A Phase 1 Dose Escalation Study of VX-708 in Healthy Participants

Phase 1
Completed
Conditions
Pain
Interventions
Registration Number
NCT05518734
Lead Sponsor
Vertex Pharmaceuticals Incorporated
Brief Summary

The purpose of this study is to evaluate the safety, pharmacokinetics, and pharmacodynamics of multiple ascending doses of VX-708 in healthy participants

Detailed Description

This clinical trial information was submitted voluntarily under the applicable law and, therefore, certain submission deadlines may not apply. (That is, clinical trial information for this applicable clinical trial was submitted under section 402(j)(4)(A) of the Public Health Service Act and 42 CFR 11.60 and is not subject to the deadlines established by sections 402(j)(2) and (3) of the Public Health Service Act or 42 CFR 11.24 and 11.44.).

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
64
Inclusion Criteria
  • Male and female of non-childbearing potential are eligible
  • Body mass index (BMI) of 18.0 to 32.0 kilograms per meter square (kg/m^2)
  • A total body weight greater than (>) 50 kg

Key

Exclusion Criteria
  • History of febrile illness or other acute illness within 14 days before the first dose of study drug

  • History of cardiac dysrhythmias

  • Part A Cohorts with Midazolam DDI Evaluation (Cohort A4) Only

    • Hypersensitivity to midazolam or benzodiazepines
  • Part A Cohorts with CSF Sampling (Cohorts A2 and A3) Only

    • Hypersensitivity to local anesthetic for lumbar puncture
    • History of conditions leading to increased intracranial pressure (e.g., brain tumor, idiopathic intracranial hypertension, venous sinus thrombosis)
  • Part B Only

    • Hypersensitivity to itraconazole

Other protocol defined Inclusion/Exclusion criteria may apply.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SEQUENTIAL
Arm && Interventions
GroupInterventionDescription
Part A: VX-708 (Cohort A1-A3)VX-708Participants will receive multiple doses of one of different dose levels of VX-708 under fasting condition.
Part A: PlaceboPlaceboParticipants will receive placebo matched to VX-708.
Part A: Midazolam With or Without VX-708 (Cohort A4)MidazolamParticipants will receive a single dose of Midazolam with or without VX-708 under fasting condition.
Part A: Midazolam With or Without VX-708 (Cohort A4)VX-708Participants will receive a single dose of Midazolam with or without VX-708 under fasting condition.
Part B: VX-708 With ItraconazoleVX-708Participants will receive a single dose of VX-708 in treatment period 1, followed by itraconazole, which will be dosed daily with a single dose of VX-708 administered in treatment period 2 under fasting conditions. A washout period of 6 days will be maintained between the 2 treatment periods.
Part B: VX-708 With ItraconazoleItraconazoleParticipants will receive a single dose of VX-708 in treatment period 1, followed by itraconazole, which will be dosed daily with a single dose of VX-708 administered in treatment period 2 under fasting conditions. A washout period of 6 days will be maintained between the 2 treatment periods.
Primary Outcome Measures
NameTimeMethod
Part A: Safety and Tolerability as Assessed by Number of Participants With Clinically Meaningful Findings in Columbia Suicide Severity Rating Scale (C-SSRS) ResponsesDay 1 up to Day 30
Part A: Continuous Pulse Oximetry Monitoring as assessed by oxygen saturation for Cohort A4Pre-dose up to 6 hours Post-dose
Part A: Infusion Nurses Society (INS) Visual Infusion Phlebitis (VIP) Score MonitoringDay 1 up to Day 30
Part B: Area Under the Plasma Concentration Versus Time Curve from the Time of Dosing Extrapolated to Infinity (AUC0-inf) of VX-708 in the Absence or Presence of ItraconazoleDay 1 up to Day 16
Part A: Safety and Tolerability as Assessed by Number of Participants With Adverse Events (AEs) and Serious Adverse Events (SAEs)Day 1 up to Day 30
Secondary Outcome Measures
NameTimeMethod
Part B: Safety and Tolerability as Assessed by Number of Participants With Adverse Events (AEs) and Serious Adverse Events (SAEs)Day 1 up to Day 32
Part A: Area Under the Concentration Versus Time Curve from the Time of Dosing Extrapolated to Infinity (AUC0-inf) of Midazolam and 1-hydroxy-midazolam in the Absence or Presence of VX-708 (Cohort A4)Day 1 up to Day 14
Part B: Infusion Nurses Society (INS) Visual Infusion Phlebitis (VIP) ScoreDay 1 up to Day 30
Part A: Area Under the Plasma Concentration Versus Time Curve from the Time of Dosing Extrapolated to Infinity (AUC0-inf) of VX-708Day 1 up to Day 14

Trial Locations

Locations (1)

Celerion - Tempe

🇺🇸

Tempe, Arizona, United States

© Copyright 2025. All Rights Reserved by MedPath