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Sarcoma Study of MORAb-004 Utilization: Research and Clinical Evaluation

Phase 2
Completed
Conditions
Metastatic Soft Tissue Sarcoma
Interventions
Registration Number
NCT01574716
Lead Sponsor
Morphotek
Brief Summary

This study is being done to see if MORAb-004 increases the effectiveness of the chemotherapies gemcitabine and docetaxel in people with metastatic Soft Tissue Sarcoma.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
209
Inclusion Criteria
  • Be at least 18 years of age
  • Be surgically sterile or consent to use a medically acceptable method of contraception throughout the study period
  • Have a histologically confirmed diagnosis of mSTS as defined by the 4 specified study subgrouped
  • Have been treated in the metastatic setting with 0 to 2 prior systemic regimens for mSTS (Systemic treatment regimens given in the neoadjuvant setting and maintenance therapies will not be considered as regimens in the metastatic setting for the purposes of this protocol. Prior anthracycline-based regimen is allowable but not required. Subjects with extra-skeletal small round blue cell sarcomas, including rhabdomyosarcomas, must have exhausted or be intolerant of standard first line anthracycline-based chemotherapy.)
  • Have measurable disease, as defined by RECIST v 1.1 assess within 2 weeks of study entry and have radiologically documented disease progression greater than or equal to a 10% increase in the sum of the longest diameters of target lesions present within 6 months prior to randomization
  • Have tumor tissue available for TEM-1 biomarker studies
  • Be willing and able to provide written informed consent
Exclusion Criteria
  • Have received more than 2 prior systemic treatment regimens for mSTS
  • Have received either gemcitabine or docetaxel in any previous treatment for mSTS (regardless of the line of treatment)
  • Have a diagnosis of primary bone sarcoma of any histological type.
  • Have a history of clinically significant heart disease, or clinically significant arrhythmia on ECG within the past 6 months
  • Have a history of allergic reaction to prior monoclonal antibody or biologic agent
  • Have received previous treatment with MORAb-004 (anti-TEM-1)
  • Have a medical condition with a high risk of bleeding (e.g., a known bleeding disorder, a coagulopathy, or a tumor that involves the major vessels) or have a recent (within past 6 months) history of a significant bleeding event
  • Have undergone major surgical procedures or open biopsy, have significant traumatic injury within 30 days prior to the first date of study treatment, or have major surgical procedures anticipated during the study
  • Have a serious non-healing wound, an ulcer (including gastrointestinal), or a bone fracture

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo, gemcitabine, docetaxelPlacebo-
MORAb-004, gemcitabine, docetaxelMORAb-004-
Placebo, gemcitabine, docetaxelGemcitabine-
MORAb-004, gemcitabine, docetaxelGemcitabine-
MORAb-004, gemcitabine, docetaxelDocetaxel-
Placebo, gemcitabine, docetaxelDocetaxel-
Primary Outcome Measures
NameTimeMethod
Part 2: Radiologic Progression-free Survival (PFS)From date of first dose until date of first observation of disease progression, or death due to any cause (up to approximately 3 years)

PFS was defined as the time (in weeks) from the date of randomization to the date of first observation of disease progression according to Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST 1.1) or date of death, regardless of the cause.

Secondary Outcome Measures
NameTimeMethod
Part 2: Overall Response Rate (ORR)From date of first dose until disease progression (up to approximately 3.5 years)

ORR was defined as the percentage of subjects with either a complete response (CR) or a partial response (PR) based on RECIST 1.1. CR was defined as disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to less than (\<) 10 millimeter (mm). PR was defined as at least a 30 percent (%) decrease in sum of diameters of target lesions, taking as reference the baseline sum of diameters.

Part 2: Symptomatic Progression-free SurvivalFrom date of first dose until date of first observation of disease progression, symptomatic progression, or death due to any cause (up to approximately 3 years)

PFS including symptomatic progression was defined as the time (in weeks) from the date of randomization to the date of the first observation of disease progression according to RECIST 1.1, symptomatic progression, or death due to any cause.

Part 2: Radiologic Progression-free Survival Rate (PFR)Weeks 12, 24, 48 and 52

Radiologic progression-free survival rate was defined as the percentage of subjects achieving radiologic PFS at the pre-specified time points.

Part 2: Number of Participants Who Had Relationship Between MORAb-004 Exposures and Biomarker LevelsUp to approximately 3 years
Part 2: Overall Survival (OS)From date of first dose until date of death from any cause (up to approximately 3.5 years)

OS was defined as the time (in months) from the date of randomization to the date of death, regardless of the cause.

Trial Locations

Locations (29)

Sarcoma Oncology Center

🇺🇸

Santa Monica, California, United States

Sidney Kimmel Comprehensive Cancer Center at John Hopkins

🇺🇸

Baltimore, Maryland, United States

Dana-Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Washington University

🇺🇸

Saint Louis, Missouri, United States

Mayo Clinic - Rochester

🇺🇸

Rochester, New York, United States

The University of North Carolina at Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

Northwestern Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Fox Chase Cancer Center

🇺🇸

Philadelphia, Pennsylvania, United States

Mount Sinai Medical Center

🇺🇸

New York, New York, United States

Siouxland Hematology-Oncology

🇺🇸

Sioux City, Iowa, United States

University of Michigan Health System

🇺🇸

Ann Arbor, Michigan, United States

Royal North Shore Hospital

🇦🇺

St. Leonards, New South Wales, Australia

Canberra Hospital

🇦🇺

Garran, Australian Capital Territory, Australia

MD Anderson Cancer Center

🇺🇸

Houston, Texas, United States

Institut Gustave Roussy

🇫🇷

Villejuif, France

UZ Leuven Medical Oncology

🇧🇪

Leuven, Belgium

Seattle Care Alliance

🇺🇸

Seattle, Washington, United States

Istituto Ortopedico Rizzoli

🇮🇹

Bologna, Italy

University of Claude Bernard

🇫🇷

Villeurbanne, France

Mayo Clinic Jacksonville

🇺🇸

Jacksonville, Florida, United States

UCLA

🇺🇸

Santa Monica, California, United States

University of Miami

🇺🇸

Miami, Florida, United States

Moffitt Cancer Center

🇺🇸

Tampa, Florida, United States

Oregon Health and Science University

🇺🇸

Portland, Oregon, United States

Huntsman Cancer Institute at the University of Utah

🇺🇸

Salt Lake City, Utah, United States

Sir Charles Gairdner Hospital

🇦🇺

Perth, Western Australia, Australia

Leiden University Medical Center

🇳🇱

Leiden, Netherlands

Princess Alexandra Hospital

🇦🇺

Woolloongabba, Queensland, Australia

Ashford Cancer Centre Research

🇦🇺

Kurralta Park, South Australia, Australia

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