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Therapeutic Vaccine Plus PD-1 Knockout in Prostate Cancer Treatment

Phase 1
Conditions
Prostate Cancer
Interventions
Biological: Therapeutic vaccine
Biological: PD-1 Knockout T Cells
Registration Number
NCT03525652
Lead Sponsor
The First Affiliated Hospital of Guangdong Pharmaceutical University
Brief Summary

This study is to evaluate the safety and efficacy of a therapeutic vaccine in combination with PD-1 knockout T cells in the treatment of advanced prostate cancer.

Detailed Description

This is a phase 1/2 clinical study investigating the safety and efficacy of a therapeutic vaccine in combination with PD-1 knockout T cells in the treatment of advanced prostate cancer. The therapeutic vaccine is a customized product involving ex vivo treatment of the patient's peripheral blood mononuclear cells with a recombinant fusion protein (PAP-GM-CSF) to activate the expression of the antigen that would activate the immune function to kill cancer cells. The PD-1 knockout engineered T cells are also prepared using patient's T cells in which PD-1 gene will be knocked out using CRISPR Cas9 technology. The therapeutic vaccine and PD-1 knockout T cells will be infused back to the patient in 3 times with a 2-week interval.

Recruitment & Eligibility

Status
UNKNOWN
Sex
Male
Target Recruitment
30
Inclusion Criteria
  • • Histologically confirmed prostate cancer (stage IV, according to NCCN Clinical Practice Guidelines in Oncology: Prostate Cancer, Version 2.2017)

    • Evidence of metastasis in the soft tissue and/or bone.
    • Progressive androgen independent castrate resistant prostate cancer.
    • Serum PSA ≥ 5.0 ng/mL
    • Estimated life expectancy ≥ 6 months.
    • Castrate level of testosterone (< 50 ng/dL) achieved via medical or surgical castration.
    • Adequate hematologic, renal and liver function.
Exclusion Criteria
  • • Presence of known lung, liver, or brain metastases, malignant pleural effusions, or malignant ascites.

    • Presence of moderate to severe pain treating with opioid analgesics within 21 days prior to registration.
    • ECOG score ≥ 2.
    • Any other systemic therapy for prostate cancer (except for medical castration).
    • Participation in previous study using Provenge (Sipuleucel-T) or similar product.
    • Known pathologic long-bone fractures, imminent pathologic long-bone fracture (cortical erosion on radiography > 50%) or spinal cord compression.
    • Known malignancies other than prostate cancer requiring active treatment within 6 months.
    • A requirement for systemic immunosuppressive therapy for any reason.
    • A history of allergic reactions attributed to compounds of similar chemical or biologic composition to this product or granulocyte-macrophage colony-stimulating factor.
    • Any infection requiring parenteral antibiotic therapy or causing fever (temp > 100.5°F or > 38.1°C) within 1 week prior to registration.
    • Any medical intervention or other condition which, in the opinion of the Principal Investigator could compromise adherence with study requirements or otherwise compromise the study's objectives.
    • Treatment with any of the following medications or interventions within 28 days of registration:

Systemic use of corticosteroids, External beam radiation therapy or surgery, Use of non-steroidal antiandrogens Dietary and herbal supplements, as well as alternative treatments that have evidence of hormonal and/or anticancer properties (e.g., prostate cancer (PC) -SPES or PC-SPEC) and saw palmetto, Megestrol acetate (Megace®), diethylstilbesterol (DES), or cyproterone acetate, ++Ketoconazole, 5-alpha-reductase inhibitors, Treatment with any other investigational product Treatment with chemotherapy High dose calcitriol [1,25(OH)2Vitamin D] (i.e., > 0.5 mcg/day). Initiation or discontinuation of bisphosphonate therapy

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Therapeutic vaccineTherapeutic vaccineTherapeutic vaccine will be prepared ex vivo using the peripheral mononuclear cells from the patients and the vaccine (as maturated dendritic cells) will be infused back to the patients in 3 times with a 2-week interval.
PD-1 knockout T cellsPD-1 Knockout T CellsPD-1 knockout T cells will be prepared ex vivo using the white cells from the patients and the maturated PD-1 knockout T cells will be infused back to the patients in 3 times.
Therapeutic vaccine plus PD-1 knockoutTherapeutic vaccineTherapeutic vaccine and PD-1 knockout T cells will be prepared ex vivo using the white cells from the patients and the vaccine (as maturated dendritic cells) and maturated PD-1 knockout T cells will be infused back to the patients in 3 times.
Therapeutic vaccine plus PD-1 knockoutPD-1 Knockout T CellsTherapeutic vaccine and PD-1 knockout T cells will be prepared ex vivo using the white cells from the patients and the vaccine (as maturated dendritic cells) and maturated PD-1 knockout T cells will be infused back to the patients in 3 times.
Primary Outcome Measures
NameTimeMethod
Number of participants with adverse events and dose limiting toxicities as assessed by CTCAE v4.06 months

Safety and tolerability of dose of therapeutic vaccine in combination with PD-1 Knockout T cells will be assessed using CTCAE v4.0

Secondary Outcome Measures
NameTimeMethod
Response Rate6 months

Will be assessed according to the revised RECIST guideline v1.1

Progression free survival - PFSUp to 12 months

Time from treatment to date of first documented progression or date of death

Overall Survival - OSDeath

Measure the time from the commencement of treatment to death

Peripheral blood circulating tumor DNA8 weeks

Circuiting tumor DNA will be measured at baseline and 6 weeks after treatment

Trial Locations

Locations (2)

Professor Size Chen

🇨🇳

Guangzhou, Guangdong, China

First Affiliated Hospital of Guangdong Pharmaceutical University

🇨🇳

Guangzhou, Guangdong, China

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