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PurIST Classification-Guided Adaptive Neoadjuvant Chemotherapy by RNA Expression Profiling of EUS Aspiration Samples

Phase 2
Recruiting
Conditions
Pancreatic Cancer
Interventions
Drug: Gemcitabine/Nab-paclitaxel Treatment Regimen
Drug: mFOLFIRINOX Treatment Regimen
Radiation: Chemoradiation
Registration Number
NCT04683315
Lead Sponsor
Medical College of Wisconsin
Brief Summary

This is an open-label, phase II study in patients with resectable and borderline resectable pancreatic cancer.

Detailed Description

The study intervention involves molecular profiling Purity Independent Subtyping of Tumors (PurIST) subtyping of pretreatment Endoscopic Ultrasound Fine Needle Aspiration (EUS/FNA) samples to determine pancreatic cancer subtype. Neoadjuvant therapy is directed based on the molecular subtype (classical vs. basal). Patients with classical subtype will receive a standard chemotherapy (mFOLFIRINOX) and patients with basal subtype will receive an alternative standard therapy (gemcitabine/nab-paclitaxel).

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
87
Inclusion Criteria

Not provided

Exclusion Criteria
  1. Has received chemotherapy and/or radiation within three years prior to study enrollment.
  2. Has any previous history of another malignancy (other than cured basal or squamous cell carcinoma of the skin or cured in situ carcinoma of the cervix or localized prostate cancer with normal prostate specific antigen) within three years of study enrollment.
  3. Uncontrolled comorbidities including, but not limited to, ongoing or active serious infection, symptomatic congestive heart failure, unstable angina, unstable cardiac arrhythmias, psychiatric illness, excessive obesity (BMI >55) or situations that would limit compliance with the study requirements or the ability to willingly give written informed consent.
  4. Known HIV, hepatitis B virus (HBV) or hepatitis C virus (HCV) infection.
  5. Pregnant or breastfeeding patients or any patient with childbearing potential not using contraception four weeks prior to treatment.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Subtype diagnosis and classification: BasalGemcitabine/Nab-paclitaxel Treatment RegimenPatients will be classified by (molecular) subtype (using the PurIST classifier) into two groups: basal and classical pancreatic cancer. Upon diagnosis, patients categorized as basal will receive two months of the Gemcitabine/Nab-paclitaxel Treatment Regimen.
Subtype diagnosis and classification: ClassicalmFOLFIRINOX Treatment RegimenPatients will be classified by (molecular) subtype (using the PurIST classifier) into two groups: basal and classical pancreatic cancer. Patients in the classical group will receive two months of the mFOLFIRINOX Treatment Regimen.
Basal Group: Restaging: Response to TreatmentGemcitabine/Nab-paclitaxel Treatment RegimenAfter the first restaging evaluation, further treatment will be based on treatment response. Patients who demonstrate a response \[decline in carbohydrate antigen 19-9 (CA19-9) values\] and radiographic response, along with preserved performance status) will be maintained on the first line chemotherapy for an additional two months.
Classical Group: Restaging: Response to TreatmentmFOLFIRINOX Treatment RegimenAfter the first restaging evaluation, further treatment will be based on treatment response. Patients who demonstrate a response \[decline in carbohydrate antigen 19-9 (CA19-9) values\] and radiographic response, along with preserved performance status) will be maintained on the first line chemotherapy for an additional two months.
Basal Group: Restaging: Patients with Stable DiseasemFOLFIRINOX Treatment RegimenPatients who do not have a significant decline in CA19-9 values will be changed to a second-line therapy for an additional two months.
Classical Group: Restaging: Patients with Stable DiseaseGemcitabine/Nab-paclitaxel Treatment RegimenPatients who do not have a significant decline in CA19-9 values will be changed to a second-line therapy for an additional two months.
Basal Group: Restaging: Local Disease ProgressionChemoradiationFurther treatment will be based on treatment response. If the patient has local disease progression amenable to surgical resection, he or she will receive chemoradiation, rather than continued chemotherapy, so the window of opportunity for surgical resection is not lost.
Classical Group: Restaging: Local Disease ProgressionChemoradiationFurther treatment will be based on treatment response. If the patient has local disease progression amenable to surgical resection, he or she will receive chemoradiation, rather than continued chemotherapy, so the window of opportunity for surgical resection is not lost.
Primary Outcome Measures
NameTimeMethod
Subjects who receive PurIST classification-directed therapy.12 weeks

The number of subjects who receive PurIST classification-directed therapy and have a treatment response following 12 weeks of therapy.

Secondary Outcome Measures
NameTimeMethod
Treatment response for subjects with basal subtype tumors.12 weeks

The number of subjects with basal subtype tumors who have a treatment response.

Treatment response for subjects with classical subtype tumors.12 weeks

The number of subjects with classical subtype tumors who have a treatment response.

Subjects with basal subtype tumors who complete all intended neoadjuvant therapy and surgical therapy.One year

The number of subjects completing all intended neoadjuvant therapy and surgical therapy.

Subjects with classical subtype tumors who complete all intended neoadjuvant therapy and surgical therapy.One year

The number of subjects completing all intended neoadjuvant therapy and surgical therapy.

Trial Locations

Locations (2)

HonorHealth Medical Group

🇺🇸

Scottsdale, Arizona, United States

Froedtert & the Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

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