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Clinical Trials/RBR-9kk7p2
RBR-9kk7p2
Recruiting
未知

Functional consequences and therapeutic intervention in hampered production of cysteine, glutathione and taurine in classical homocystinuria

niversidade Federal do Rio Grande do Sul0 sitesSeptember 16, 2019

Overview

Phase
未知
Intervention
Not specified
Conditions
Classical Homocystinuria (CBS deficiency)
Sponsor
niversidade Federal do Rio Grande do Sul
Status
Recruiting
Last Updated
2 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
September 16, 2019
End Date
TBD
Last Updated
2 years ago
Study Type
Intervention

Investigators

Sponsor
niversidade Federal do Rio Grande do Sul

Eligibility Criteria

Inclusion Criteria

  • Age over 18 years; for patients: molecular diagnosis of CBS deficiency

Exclusion Criteria

  • Patients with gastric, hepatic or kidney disease; smoking; illicit drug users;Acetaminophen or N\-acetylcysteine hypersensitivity.

Outcomes

Primary Outcomes

Not specified

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