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iver consequences of cysteine, glutathione and taurine deficiency in classical homocystinuria

Not Applicable
Recruiting
Conditions
Classical Homocystinuria (CBS deficiency)
E72.1
Registration Number
RBR-9kk7p2
Lead Sponsor
niversidade Federal do Rio Grande do Sul
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Recruiting
Sex
Not specified
Target Recruitment
Not specified
Inclusion Criteria

Age over 18 years; for patients: molecular diagnosis of CBS deficiency

Exclusion Criteria

Patients with gastric, hepatic or kidney disease; smoking; illicit drug users;Acetaminophen or N-acetylcysteine hypersensitivity.

Study & Design

Study Type
Intervention
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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