Study of longitudinal observation for patient with X-linked hypophosphatemic rickets/osteomalacia in collaboration with Asian partners
Not Applicable
- Conditions
- X-linked hypophosphatemic rickets/osteomalacia
- Registration Number
- JPRN-UMIN000031605
- Lead Sponsor
- Kyowa Kirin Co., Ltd.
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up continuing
- Sex
- All
- Target Recruitment
- 226
Inclusion Criteria
Not provided
Exclusion Criteria
1. Participation in any clinical study (trial) sponsored by Kyowa Kirin at the time of informed consent 2. Any patient whose participation in the study is considered inappropriate by the investigator or the subinvestigator
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Patients aged,<18years:Height,Rickets Severity Score,QOL,and motor function Patients aged >=18years:QOL and motor function
- Secondary Outcome Measures
Name Time Method Patients aged <18 years:Growth velocity, lower limb deformity,biomarkers for phosphorus metabolism and bone metabolism,and fracture Patients aged >=18 years:Biomarkers for phosphorus metabolism and bone metabolism,fracture,spinal ligament ossification,nephrocalcinosis,and renal function