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Safety Study of Inhaled 552-02 in Cystic Fibrosis Patients

Phase 1
Completed
Conditions
Cystic Fibrosis
Registration Number
NCT00274313
Lead Sponsor
Parion Sciences
Brief Summary

The purpose of this study is to evaluate the safety and tolerability of a new inhaled sodium-channel blocker called 552-02 in teens and adults with cystic fibrosis. 552-02 will be inhaled once a day for 14 days using a nebulizer. A small subgroup of patients will donate blood samples for pharmacokinetic analysis to see how 552-02 is absorbed into the blood and eliminated after 14 days of treatment.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
40
Inclusion Criteria
  1. Male and female patients aged > 14 years.
  2. Patients who are diagnosed with cystic fibrosis.
  3. Patients who have a FEV1 ≥ 50% predicted (post-bronchodilator) at screening.
  4. Patients who are able to perform reproducible spirometry according to ATS guidelines.
  5. Patients who have an oxygen saturation of ≥ 92% on room air as determined by pulse oximetry at screening.
Exclusion Criteria
  1. Patients who have a FEV1 change ≥ 15% after bronchodilator use at screening.
  2. Patients who have unstable lung disease as defined by the requirement for intravenous antibiotics during the four weeks prior to screening, a change in medical regimen within 14 days prior to administration of the first dose of study drug or during the 14 day treatment period, a FEV1 ≥ 15% below recent (within six months) clinical measurements, or significant new findings on chest radiograph (pneumothorax, lobar/segmental collapse) that are not considered a part of the usual, chronic progression of cystic fibrosis lung disease.
  3. Patients on angiotensin converting enzyme (ACE) inhibitors.
  4. Patients with renal insufficiency as evidenced by hyperkalemia (blood potassium levels greater than 5.5 mEq/L) or serum creatinine > 2.0 mg/dL.
  5. Patients who have a history of drug allergies to any medicine chemically related to the study drug (e.g. amiloride, Moduretic, Midamor; triamterene).
  6. Patients who are pregnant, have a positive pregnancy test, or are nursing.
  7. Patients who have had a lung transplant.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Primary Outcome Measures
NameTimeMethod
Safety assessments
Blood and urine laboratory tests
Pulmonary function tests
Electrocardiograms
Vital signs and pulse oximetry
Secondary Outcome Measures
NameTimeMethod
Plasma pharmacokinetics on Day 14 of the study.

Trial Locations

Locations (15)

University of South Florida

🇺🇸

Tampa, Florida, United States

University of Pittsburgh

🇺🇸

Pittsburgh, Pennsylvania, United States

University of California at San Diego

🇺🇸

San Diego, California, United States

University of California at San Francisco Medical Center

🇺🇸

San Francisco, California, United States

The Children's Hospital

🇺🇸

Denver, Colorado, United States

Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

Children's Memorial Hospital

🇺🇸

Chicago, Illinois, United States

University of Nebraska Medical Center

🇺🇸

Omaha, Nebraska, United States

Morristown Memorial Hospital

🇺🇸

Morristown, New Jersey, United States

State University of New York Upstate

🇺🇸

Syracuse, New York, United States

Nemours Children's Clinic

🇺🇸

Orlando, Florida, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

University of Virginia

🇺🇸

Charlottesville, Virginia, United States

Hershey Medical Center

🇺🇸

Hershey, Pennsylvania, United States

University of North Carolina at Chapel Hill

🇺🇸

Chapel Hill, North Carolina, United States

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