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A Study of ABT-414 in Participants With Newly Diagnosed Glioblastoma (GBM) With Epidermal Growth Factor Receptor (EGFR) Amplification

Phase 3
Completed
Conditions
Glioblastoma
Gliosarcoma
Interventions
Radiation: Radiation
Drug: Placebo for ABT-414
Registration Number
NCT02573324
Lead Sponsor
AbbVie
Brief Summary

This study seeks to determine whether the addition of ABT-414 to concomitant radiotherapy and temozolomide (TMZ) followed by combination of ABT-414 with adjuvant TMZ prolongs overall survival (OS) among participants with newly diagnosed glioblastoma (GBM) with epidermal growth factor receptor (EGFR) amplification.

In addition, there is a Phase 1, open-label, multicenter sub-study to assess the pharmacokinetics, safety and tolerability of ABT-414 in participants with newly diagnosed EGFR-amplified GBM who have mild or moderate hepatic impairment.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
691
Inclusion Criteria
  • Must have a clinical diagnosis of glioblastoma (GBM).
  • Must have a confirmed epidermal growth factor receptor amplification in tumor tissue.
  • Must have a Karnofsky Performance Status (KPS) >= 70 at assessment <= 14 days prior to randomization (N/A to the sub-study).
  • Must have recovered from effects of surgery, postoperative infection and other complications of surgery.
  • Must have adequate bone marrow, renal, and hepatic function (For the sub-study, the participant must have adequate bone marrow and renal function and have mild-to-moderate hepatic impairment).
Exclusion Criteria
  • Multifocal, recurrent or metastatic GBM or gliomatosis cerebri (For the sub-study, the participant can have multifocal GBM and glimatosis cerebri but can't have recurrent or metastatic GBM).
  • Prior chemo therapy or radiosensitizer for head and neck cancer.
  • Prior radiotherapy to the head or neck in overlap of radiation fields.
  • Prior therapy for glioblastoma or other invasive malignancy.
  • Prior, concomitant or planned treatment with Novo Tumor Treatment Fields (Novo-TTF), EGFR-targeted therapy, bevacizumab, Gliadel wafers or other intratumoral or intracavity anti-neoplastic therapy.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Open-Label Sub-Study: Depatuxizumab Mafodotin, Radiation and TMZTemozolomideDepatuxizumab mafodotin is given to participants with hepatic impairment on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Placebo, Radiation and TMZRadiationPlacebo is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Placebo is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Open-Label Sub-Study: Depatuxizumab Mafodotin, Radiation and TMZRadiationDepatuxizumab mafodotin is given to participants with hepatic impairment on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Depatuxizumab Mafodotin, Radiation and Temozolomide (TMZ)RadiationDepatuxizumab mafodotin is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Placebo, Radiation and TMZPlacebo for ABT-414Placebo is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Placebo is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Depatuxizumab Mafodotin, Radiation and Temozolomide (TMZ)TemozolomideDepatuxizumab mafodotin is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Placebo, Radiation and TMZTemozolomidePlacebo is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Placebo is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Open-Label Sub-Study: Depatuxizumab Mafodotin, Radiation and TMZDepatuxizumab mafodotinDepatuxizumab mafodotin is given to participants with hepatic impairment on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Depatuxizumab Mafodotin, Radiation and Temozolomide (TMZ)Depatuxizumab mafodotinDepatuxizumab mafodotin is given on Day 1 of Week 1, 3 and 5 along with the standard therapy of TMZ and radiation during the chemoradiation phase. Depatuxizumab mafodotin is given on Day 1 and 15 of each cycle along with TMZ (Days 1-5 of each cycle) per standard of care during the adjuvant phase.
Primary Outcome Measures
NameTimeMethod
Overall Survival (OS)Overall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

Time to OS is defined as the number of days from the date of randomization to the date of death due to any cause.

Secondary Outcome Measures
NameTimeMethod
OS for the Epidermal Growth Factor Receptor (EGFR)vIII-Mutated Tumor SubgroupOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

Time to OS is defined as the number of days from the date of randomization to the date of death due to any cause.

Progression-Free Survival (PFS)Overall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

PFS will be defined as the number of days from the date of randomization to the date of earliest disease progression based on Response Assessment in Neuro-Oncology (RANO) criteria (see Wen et al. J Clin Oncol. 2010 Apr 10;28(11):1963-72) or to the date of death, if disease progression does not occur.

PFS for EGFRvIII-Mutated Tumor SubgroupOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

PFS will be defined as the number of days from the date of randomization to the date of earliest disease progression based on Response Assessment in Neuro-Oncology (RANO) criteria or to the date of death, if disease progression does not occur.

Deterioration Free Survival in M.D. Anderson Symptom Inventory Brain Tumor Module (MDASI-BT) Symptom Severity ScoreOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

The MDASI-BT assesses the severity of multiple brain tumor-related symptoms and the impact of these symptoms on daily functioning in the last 24 hours. It consists of 22 symptom items and 6 interference items, each rated from 0 to 10. MDASI-BT symptom severity score is defined as average over 13 core symptom items and 9 brain tumor symptom items, with a total score of 0 to 10, with higher score indicating worse symptoms/interference. Changes in symptom severity score were classified into 3 categories: improved (≤ -1), stable (\> -1 and \< 1), and deteriorated (≥ 1). Deterioration is defined as satisfying the deterioration criteria (i.e., increase in symptom severity score by ≥ 1 unit) without further improvement (i.e., failing to satisfy deterioration criteria) within 8 weeks or occurrence of death.

Deterioration Free Survival in MDASI-BT Symptom Interference ScoreOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

The MDASI-BT assesses the severity of multiple brain tumor-related symptoms and the impact of these symptoms on daily functioning in the last 24 hours. It consists of 22 symptom items and 6 interference items, each rated from 0 to 10. MDASI-BT symptom interference score is defined as an average of 6 interference items, with a total score of 0 to 10, where higher scores indicate worse interference. Changes in symptom interference score were classified into 3 categories: improved (≤ -1), stable (\> -1 and \< 1), and deteriorated (≥ 1). Deterioration is defined as satisfying the deterioration criteria (i.e., increase in symptom interference score by ≥ 1 unit) without further improvement (i.e., failing to satisfy deterioration criteria) within 8 weeks or occurrence of death.

Deterioration Free Survival in Neurocognitive Functioning on the Hopkins Verbal Learning Test Revised (HVLT-R) Total Recall ScoreOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

The HVLT-R consists of 3 parts. Free call has a range of 0 to 36, delayed recall has a range from 0 to 12, and delayed recognition has a range of -12 to 12. Higher scores indicating better function in all 3 parts. When scoring the HVLT-R, the 3 learning trials are combined to calculate a total recall score (range -12 to 60). Deterioration is defined as satisfying the deterioration criteria (i.e., decrease in HVLT-R total recall score by 5 units) without further improvement within 8 weeks or occurrence of death.

OS for the MGMT Methylated GroupOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

Time to OS is defined as the number of days from the date of randomization to the date of death due to any cause.

OS for the O6-methylguaninemethlytransferese (MGMT) Unmethylated GroupOverall median duration of follow-up was 15.5 months (range: 0.1, 35.6).

Time to OS is defined as the number of days from the date of randomization to the date of death due to any cause.

Unmethylated MGMT promoter is associated with a worse prognosis in GBM

Trial Locations

Locations (212)

St. Josephs Hospital and Med Center /ID# 144149

🇺🇸

Phoenix, Arizona, United States

Highlands Oncology Group, PA /ID# 142050

🇺🇸

Springdale, Arkansas, United States

University of Southern California /ID# 147543

🇺🇸

Los Angeles, California, United States

University of California, Los Angeles /ID# 149239

🇺🇸

Los Angeles, California, United States

Sharp Memorial Hospital /ID# 148193

🇺🇸

San Diego, California, United States

Univ California, San Francisco /ID# 145889

🇺🇸

San Francisco, California, United States

Duplicate_St. John's Health Center /ID# 148192

🇺🇸

Santa Monica, California, United States

Cedars-Sinai Medical Center-West Hollywood /ID# 148472

🇺🇸

West Hollywood, California, United States

Univ of Colorado Cancer Center /ID# 148194

🇺🇸

Aurora, Colorado, United States

Associated Neurologists of Sou /ID# 147701

🇺🇸

Fairfield, Connecticut, United States

Scroll for more (202 remaining)
St. Josephs Hospital and Med Center /ID# 144149
🇺🇸Phoenix, Arizona, United States

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