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Safety and Efficacy of ALLO-715 BCMA Allogenic CAR T Cells in in Adults With Relapsed or Refractory Multiple Myeloma (UNIVERSAL)

Phase 1
Active, not recruiting
Conditions
Relapsed/Refractory Multiple Myeloma
Interventions
Registration Number
NCT04093596
Lead Sponsor
Allogene Therapeutics
Brief Summary

The purpose of the UNIVERSAL study is to assess the safety, efficacy, cell kinetics, and immunogenicity of ALLO-715 with or without Nirogacestat in adults with relapsed or refractory multiple myeloma after a lymphodepletion regimen of ALLO-647 in combination with fludarabine and/or cyclophosphamide, or ALLO-647 alone.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
132
Inclusion Criteria
  • Documented diagnosis of relapsed/refractory multiple myeloma (MM) with measurable disease (serum, urine, or free light chain [FLC]) per International Myeloma Working Group (IMWG) criteria
  • At least 3 prior lines of MM therapy, including a proteasome inhibitor, immunomodulatory agent, and anti-CD38 antibody (unless contraindicated), and refractory to the last treatment line.
  • Eastern Cooperative Oncology Group (ECOG) 0 or 1
  • Absence of donor (product)-specific anti-HLA antibodies
  • Adequate hematologic, renal, hepatic, pulmonary, and cardiac function
Exclusion Criteria
  • Current or history of Central Nervous System (CNS) involvement of myeloma or plasma cell leukemia
  • Clinically significant CNS disorder
  • Current or history of thyroid disorder
  • Autologous stem cell transplant within the last 6 weeks, or any allogeneic stem cell transplant
  • Prior treatment with anti-BCMA therapy, any gene therapy, any genetically modified cell therapy, or adoptive T cell therapy
  • History of HIV infection or acute or chronic active hepatitis B or C infection
  • Patients unwilling to participate in an extended safety monitoring period

Additional Exclusion Criteria for Nirogacestat plus ALLO-715 Cohorts

  • Inability to swallow tablets
  • Subject has known malabsorption syndrome or preexisting gastrointestinal conditions that may impair absorption of nirogacestat
  • Use of strong/moderate CYP3A4 inhibitors, and strong CYP3A4 inducers within 14 days before starting nirogacestat.
  • Use of concomitant medications that are known to prolong the QT/QTcF interval

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
ALLO-647, ALLO-715, NirogacestatALLO-715-
ALLO-647, ALLO-715, NirogacestatALLO-647-
ALLO-647, ALLO-715, NirogacestatCyclophosphamide-
ALLO-647, ALLO-715, NirogacestatNirogacestat-
ALLO-647, ALLO-715, NirogacestatFludarabine-
Primary Outcome Measures
NameTimeMethod
To assess the overall safety profile and tolerability of ALLO-647 in combination with Fludarabine and/or cyclophosphamide or ALLO-647 alone, prior to ALLO-715 to confirm the dose of ALLO-647.33 days

The proportion of subjects in a dose cohort with DLTs of ALLO-647

Proportion of subjects experiencing Dose Limiting Toxicities at increasing doses of ALLO-71528 Days

Dose limiting toxicities are defined as ALLO-715-related adverse events with onset within 28 days following infusion of ALLO-715.

To assess the overall safety profile and tolerability of nirogacestat given concomitantly with ALLO-715 following lymphodepletion with Flu/ Cy/ ALLO-647.28 days

Dose limiting toxicities are defined as ALLO-715-related adverse events with onset within 28 days following infusion of ALLO-715.

Secondary Outcome Measures
NameTimeMethod
Pharmacokinetics of nirogacestatup to 60 months

Serum concentration levels of nirogacestat

Cellular kinetics of ALLO-715up to 60 months

Levels of anti-BCMA CAR T cells in blood

antitumor activity of ALLO-715 in combination with nirogacestatup to 60 months

overall -response rate (ORR)

Cellular kinetics of ALLO-715 in combination with nirogacestatup to 60 months

Levels of anti-BCMA CAR T cells in blood

Pharmacokinetics of ALLO-647up to 60 months

Serum concentration levels of ALLO-647

Incidence of immunogenicity against ALLO-715 and ALLO-647up to 60 months

detection and levels of anti-drug antibodies

Immune monitoring after lymphodepletion regimenup to 60 months

Detection of the following circulating cells: T cell subset, B lymphocytes, and NK cells

To evaluate the expression of BCMA in bone marrow plasma cells with and without nirogacestatup to 60 months

Overall response rate of ALLO-715 with and without Nirogacestat

Anti-tumor activity of ALLO-715up to 60 months

minimal residual disease

Trial Locations

Locations (11)

Stanford Cancer Institute

🇺🇸

Palo Alto, California, United States

Banner MD Anderson Cancer Center

🇺🇸

Gilbert, Arizona, United States

Mayo Clinic

🇺🇸

Rochester, Minnesota, United States

City of Hope

🇺🇸

Duarte, California, United States

Medical College of Wisconsin

🇺🇸

Milwaukee, Wisconsin, United States

Sarah Cannon/Colorado Blood Cancer Institute

🇺🇸

Denver, Colorado, United States

Cleveland Clinic Taussig Cancer Center

🇺🇸

Cleveland, Ohio, United States

Memorial Sloan Kettering Cancer Center

🇺🇸

New York, New York, United States

Vanderbilt-Ingram Cancer Center

🇺🇸

Nashville, Tennessee, United States

St. David's South Austin Medical Center

🇺🇸

Austin, Texas, United States

Texas Transplant Institute

🇺🇸

San Antonio, Texas, United States

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